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Clinical Trials on Mucopolysaccharidosis VII
Total 13 results
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NCT03604835RecruitingConditions: Mucopolysaccharidosis VII; MPS VII; MPS 7; Sly Syndrome
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NCT02432144CompletedConditions: Sly Syndrome; MPS VII; Mucopolysaccharidosis; Mucopolysaccharidosis VII
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NCT02418455CompletedConditions: Sly Syndrome; MPS VII; Mucopolysaccharidosis; Mucopolysaccharidosis VII
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NCT02230566CompletedConditions: MPS 7; Sly Syndrome; Mucopolysaccharidosis; MPS VII
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NCT03775174AvailableConditions: MPS VII; Mucopolysaccharidosis VII; Sly Syndrome
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NCT02298699Active, not recruitingConditions: Developmental Delay; Skeletal Abnormalities; Hepatomegaly; Splenomegaly
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NCT01856218CompletedConditions: Mucopolysaccharidosis Type 7
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NCT02097251No longer availableConditions: Mucopolysaccharidosis Type 7
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NCT01870375CompletedConditions: Mucopolysaccharidosis Type I; Mucopolysaccharidosis Type II; Mucopolysaccharidosis Type VI; Mucopolysaccharidosis Type IV; Mucopolysaccharidosis Type VII
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NCT02171104RecruitingConditions: Mucopolysaccharidosis Disorders; Hurler Syndrome; Hunter Syndrome; Maroteaux Lamy Syndrome; Sly Syndrome; Alpha-Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Glycoprotein Metabolic Disorders; Sphingolipidoses; Recessive Leukodystrophies; Globoid Cell Leukodystrophy; Metachromatic Leukodystrophy; Niemann-Pick B; Niemann-Pick C Subtype 2; Sphingomyelin Deficiency; Peroxisomal Disorders; Adrenoleukodystrophy With Cerebral Involvement; Zellweger Syndrome; Neonatal Adrenoleukodystrophy; Infantile Refsum Disease; Acyl-CoA Oxidase Deficiency; D-Bifunctional Enzyme Deficiency; Multifunctional Enzyme Deficiency; Alpha-methylacyl-CoA Racmase Deficiency; Mitochondrial Neurogastrointestingal Encephalopathy; Severe Osteopetrosis; Hereditary Leukoencephalopathy With Axonal Spheroids (HDLS; CSF1R Mutation); Inherited Metabolic Disorders
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NCT00668564TerminatedConditions: Hurler's Syndrome; Maroteaux-Lamy Syndrome; Sly Syndrome; Alpha Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Sphingolipidoses; Krabbe Disease; Wolman's Disease; Niemann-Pick Disease Type B; Niemann-Pick Disease, Type C
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NCT01043640CompletedConditions: Mucopolysaccharidosis; Hurler Syndrome; Hunter Syndrome; Maroteaux-Lamy Syndrome; Sly Syndrome; Alpha Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Adrenoleukodystrophy (ALD); Krabbe Disease; Metachromatic Leukodystrophy (MLD); Sphingolipidoses; Peroxisomal Disorders
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NCT04532047Not yet recruitingConditions: MPS I; MPS II; MPS IVA; MPS VI; Mps VII; Gaucher Disease, Type 2; Gaucher Disease, Type 3; Pompe Disease Infantile-Onset; Wolman Disease