Kliniske forsøg med Mucopolysaccharidosis VII

I alt 13 resultater

    • NCT03604835
      Rekruttering
      Betingelser: Mucopolysaccharidosis VII; MPS VII; MPS 7; Sly Syndrome
    • NCT02432144
      Afsluttet
      Betingelser: Sly Syndrome; MPS VII; Mucopolysaccharidosis; Mucopolysaccharidosis VII
    • NCT02418455
      Afsluttet
      Betingelser: Sly Syndrome; MPS VII; Mucopolysaccharidosis; Mucopolysaccharidosis VII
    • NCT02230566
      Afsluttet
      Betingelser: MPS 7; Sly Syndrome; Mucopolysaccharidosis; MPS VII
    • NCT03775174
      Available
      Betingelser: MPS VII; Mucopolysaccharidosis VII; Sly Syndrome
    • NCT02298699
      Aktiv, ikke rekruttering
      Betingelser: Developmental Delay; Skeletal Abnormalities; Hepatomegaly; Splenomegaly
    • NCT01856218
      Afsluttet
      Betingelser: Mucopolysaccharidosis Type 7
    • NCT02097251
      No longer available
      Betingelser: Mucopolysaccharidosis Type 7
    • NCT01870375
      Afsluttet
      Betingelser: Mucopolysaccharidosis Type I; Mucopolysaccharidosis Type II; Mucopolysaccharidosis Type VI; Mucopolysaccharidosis Type IV; Mucopolysaccharidosis Type VII
    • NCT02171104
      Rekruttering
      Betingelser: Mucopolysaccharidosis Disorders; Hurler Syndrome; Hunter Syndrome; Maroteaux Lamy Syndrome; Sly Syndrome; Alpha-Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Glycoprotein Metabolic Disorders; Sphingolipidoses; Recessive Leukodystrophies; Globoid Cell Leukodystrophy; Metachromatic Leukodystrophy; Niemann-Pick B; Niemann-Pick C Subtype 2; Sphingomyelin Deficiency; Peroxisomal Disorders; Adrenoleukodystrophy With Cerebral Involvement; Zellweger Syndrome; Neonatal Adrenoleukodystrophy; Infantile Refsum Disease; Acyl-CoA Oxidase Deficiency; D-Bifunctional Enzyme Deficiency; Multifunctional Enzyme Deficiency; Alpha-methylacyl-CoA Racmase Deficiency; Mitochondrial Neurogastrointestingal Encephalopathy; Severe Osteopetrosis; Hereditary Leukoencephalopathy With Axonal Spheroids (HDLS; CSF1R Mutation); Inherited Metabolic Disorders
    • NCT00668564
      Afsluttet
      Betingelser: Hurler's Syndrome; Maroteaux-Lamy Syndrome; Sly Syndrome; Alpha Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Sphingolipidoses; Krabbe Disease; Wolman's Disease; Niemann-Pick Disease Type B; Niemann-Pick Disease, Type C
    • NCT01043640
      Afsluttet
      Betingelser: Mucopolysaccharidosis; Hurler Syndrome; Hunter Syndrome; Maroteaux-Lamy Syndrome; Sly Syndrome; Alpha Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Adrenoleukodystrophy (ALD); Krabbe Disease; Metachromatic Leukodystrophy (MLD); Sphingolipidoses; Peroxisomal Disorders
    • NCT04532047
      Ikke rekrutteret endnu
      Betingelser: MPS I; MPS II; MPS IVA; MPS VI; Mps VII; Gaucher Disease, Type 2; Gaucher Disease, Type 3; Pompe Disease Infantile-Onset; Wolman Disease