- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Myasthenic+Syndromes%2C+Congenital
Total 2445 results
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University of MinnesotaUnknown
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Ankara City Hospital BilkentCompleted
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Gilead SciencesCompletedLong QT SyndromeUnited States
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Children's Hospital of PhiladelphiaThe Mark H. and Blanche M. Harrington FoundationCompletedTricuspid Atresia | Hypoplastic Left Heart Syndrome
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University of Alabama at BirminghamUltragenyx Pharmaceutical IncCompletedEpidermal Nevus SyndromeUnited States
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Beta-ThalassemiaHungary
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Centre Hospitalier Universitaire de Saint EtienneMinistry of Health, FranceCompleted
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Vanda PharmaceuticalsUnknownSmith Magenis SyndromeUnited States
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Charite University, Berlin, GermanyNeuroCure Clinical Research Center, Charite, Berlin; Prof. Dr. med. Falk Hiepe...TerminatedRheumatoid Arthritis | Systemic Lupus Erythematosus | Myasthenia GravisGermany
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NYU Langone HealthCompletedBrugada Syndrome | Arrhythmogenic Right Ventricular CardiomyopathyUnited States
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer CenterRecruitingFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Severe Marrow FailureUnited States
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Nantes University HospitalInstitut National de la Santé Et de la Recherche Médicale, France; Centre National...RecruitingLong QT SyndromeFrance
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Thryv Therapeutics, Inc.Completed
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IRCCS Policlinico S. DonatoRecruitingPsychology, Social | Marfan Syndrome | Rare DiseasesItaly
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingAcute Myeloid Leukemia | Down Syndrome | Myelodysplastic Syndrome | Myeloproliferative Neoplasm | Myeloid Leukemia Associated With Down SyndromeUnited States, Canada, Saudi Arabia, Puerto Rico, Australia, New Zealand
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QLT Inc.NovartisTerminatedNevoid Basal Cell Carcinoma Syndrome | Basal Cell Carcinoma | Gorlin Syndrome
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Assistance Publique - Hôpitaux de ParisCompletedCongenital Adrenal Hyperplasia (CAH)France
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Sequenom, Inc.Friends Research Institute, Inc.TerminatedDown Syndrome | Turner Syndrome | Edwards Syndrome | Patau SyndromeUnited States
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Shanghai Changzheng HospitalUnknownTethered Cord SyndromeChina
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Oslo University HospitalEnrolling by invitation
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University of AberdeenNHS GrampianCompletedAbdominal Pain | Abdominal Cutaneous Nerve Entrapment SyndromeUnited Kingdom
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SanofiTerminatedRetinitis Pigmentosa | Usher SyndromeUnited States, France
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PellePharm, Inc.CompletedBasal Cell Nevus SyndromeUnited Kingdom
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Okayama UniversityNational Cerebral and Cardiovascular CenterCompletedHeart Failure | Hypoplastic Left Heart Syndrome | Single VentricleJapan
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University of CopenhagenUnknownLong QT Syndrome
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MetroHealth Medical CenterCompletedLong QT Syndrome | Cardiac Repolarization
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IRCCS Policlinico S. DonatoUniversity of MilanRecruitingMarfan Syndrome | Rare Diseases | Ehlers-Danlos SyndromeItaly
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Boston Children's HospitalActive, not recruitingHypoplastic Left Heart Syndrome | Atrioventricular CanalUnited States
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University of MichiganGriese-Hutchinson Champions for Children's Hearts Investigator AwardCompletedTricuspid Atresia | Hypoplastic Left Heart Syndrome | Fontan ProcedureUnited States
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Aevi Genomic Medicine, LLC, a Cerecor companyCompleted22q11.2 Deletion SyndromeUnited States
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University of British ColumbiaUnity Health Toronto; University of Calgary; Queen's University; Ottawa Heart Institute... and other collaboratorsCompletedCardiac Arrest | Early Repolarization Syndrome | Brugada Syndrome | Long QT Syndrome | Arrhythmogenic Right Ventricular Cardiomyopathy | Catecholaminergi Polymorphic Ventricular Tachycardia | Idiopathic VentricularFibrillationCanada
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Assiut UniversityNot yet recruitingTethered Cord Syndrome
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Sol-Gel Technologies, Ltd.Premier Research Group plcRecruitingGorlin SyndromeUnited States
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Radboud University Medical CenterStichting UshersyndroomActive, not recruitingRetinitis Pigmentosa | Usher Syndrome, Type 2A | USH2ANetherlands
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Myelodysplastic/Myeloproliferative NeoplasmsUnited States, Canada, Puerto Rico, Australia, Netherlands, New Zealand, Switzerland
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Queen Silvia Children's Hospital, Gothenburg, SwedenSahlgrenska University Hospital, Sweden; Swedish Heart Lung FoundationRecruitingAortic Valve Stenosis | Congenital Heart Disease | Hypoplastic Left Heart Syndrome | Fetal Cardiac DisorderUnited States, Austria, Canada, Finland, Germany, Poland, Spain, Sweden
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Charles BerulMedtronic; Guidant CorporationTerminatedVentricular Fibrillation | Ventricular Tachycardia | Congenital Heart Disease | Cardiomyopathy | Long QT SyndromeUnited States
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Novartis PharmaceuticalsCompletedNevoid Basal Cell Carcinoma Syndrome | Basal Cell Carcinoma | Gorlin SyndromeBelgium, Austria, Germany, Canada
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Laboratoires VivacyRecruitingAging | Aesthetics | Volume Deficiency in the Mid-FaceFrance
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Narrows Institute for Biomedical ResearchVA New York Harbor Healthcare SystemRecruitingConnective Tissue Diseases | Rheumatoid Arthritis | Long QT SyndromeUnited States
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Assistance Publique - Hôpitaux de ParisCompletedFoetus With Congenital Pulmonary MalformationFrance
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Duke UniversityUniversity of FloridaCompleted
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Washington University School of MedicineCompletedBarth Syndrome
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University of California, San FranciscoCompletedAortic Stenosis | Hypoplastic Left Heart SyndromeUnited States
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Maastricht University Medical CenterUniversity of Bern; University of FreiburgUnknownVentricular Tachycardia | Sudden Cardiac Death | Long QT Syndrome
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Novo Nordisk A/SCompletedNoonan Syndrome | Genetic DisorderSweden
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University of RochesterGilead SciencesCompleted
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Centers for Disease Control and PreventionInternational Centre for Diarrhoeal Disease Research, Bangladesh; Ministry...CompletedMeasles | Rubella | Rubella Syndrome, CongenitalBangladesh
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University of California, Los AngelesCompletedEisenmenger SyndromeUnited States