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Clinical Trials on Myasthenic Syndromes, Congenital
Total 40721 results
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Oregon Health and Science UniversityJacobus PharmaceuticalNo longer availableLambert-Eaton Myasthenic Syndrome (LEMS) | Congenital Myasthenia (CM)United States
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisCompletedMyasthenia Gravis | Lambert-Eaton Myasthenic Syndrome | Congenital Myasthenic Syndrome | Autoimmune Myasthenia GravisFrance
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Ricardo MaselliCatalyst Pharmaceuticals, Inc.No longer availableCongenital Myasthenic SyndromeUnited States
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argenxNot yet recruiting
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argenxRecruitingCongenital Myasthenic SyndromeSpain, Italy, France, United States, Canada
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Catalyst Pharmaceuticals, Inc.CompletedMyasthenic Syndromes, CongenitalUnited States
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Mayo ClinicCompletedCongenital Myasthenic SyndromeUnited States
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Institut de Myologie, FranceAssistance Publique - Hôpitaux de ParisCompletedCongenital Myasthenic Syndrome
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Lahey ClinicApproved for marketingLambert-Eaton Myasthenic Syndrome | Congenital Myasthenic SyndromeUnited States
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Vern C. Juel, M.D.No longer available
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Catalyst Pharmaceuticals, Inc.No longer availableLambert-Eaton Myasthenic Syndrome | Congenital Myasthenic Syndrome | Nystagmus, AcquiredUnited States
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Hadassah Medical OrganizationUnknown
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Heinrich-Heine University, DuesseldorfRecruitingMyasthenia Gravis | Lambert-Eaton Myasthenic Syndrome | Myasthenic SyndromeGermany
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University of Colorado, DenverApproved for marketingLambert Eaton Myasthenic SyndromeUnited States
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Jacobus PharmaceuticalCompletedLambert-Eaton Myasthenic Syndrome | Eaton-Lambert Myasthenic SyndromeUnited States
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David P. Richman, MDJacobus PharmaceuticalNo longer available
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Catalyst Pharmaceuticals, Inc.CompletedA Phase 3 Study of Amifampridine Phosphate in Patients With Lambert Eaton Myasthenic Syndrome (LEMS)Lambert Eaton Myasthenic SyndromeUnited States, Spain, Serbia, Russian Federation, Hungary, France, Germany, Poland
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Louis H. Weimer, MDNo longer availableLambert Eaton Myasthenic Syndrome (LEMS)United States
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David Lacomis, MDJacobus PharmaceuticalNo longer availableLambert-Eaton Myasthenic Syndrome
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Catalyst Pharmaceuticals, Inc.CompletedLambert-Eaton Myasthenic SyndromeUnited States
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The Cleveland ClinicNo longer availableLambert-Eaton Myasthenic SyndromeUnited States
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FDA Office of Orphan Products DevelopmentDuke UniversityCompletedLambert-Eaton Myasthenic Syndrome
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University Hospital, BordeauxCompletedMyasthenia GravisFrance
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Ain Shams UniversityUnknownMuscular Dystrophy | Polyneuropathies | Spinal Muscular Atrophy | Muscle Diseases | Myasthenic SyndromesEgypt
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Huashan HospitalRecruiting
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Fred Hutchinson Cancer CenterActive, not recruitingMyasthenia Gravis | Neuromyelitis Optica | Autoimmune Disease | Chronic Inflammatory Demyelinating Polyneuropathy | Lambert Eaton Myasthenic Syndrome | Cerebellar Degeneration | Stiff Person Syndrome | Opsoclonus Myoclonus Syndrome | Neurologic Autoimmune Disease | Autologous Transplant Autoimmune | Multiple... and other conditionsUnited States
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GlaxoSmithKlineCompletedMyasthaenia GravisUnited States, Canada, Germany, Italy
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Assiut UniversityRecruitingNervous System Diseases | Autoimmune Diseases of the Nervous System | Thymoma | Myasthenia Gravis | Neuromuscular Junction Diseases | Myasthenia Gravis, Generalized | Myasthenia Gravis Crisis | Myasthenia Gravis, Ocular | Myasthenia Gravis, Juvenile Form | Thymus Hyperplasia | Myasthenia Gravis With Exacerbation... and other conditionsEgypt
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Catalyst Pharmaceuticals, Inc.TerminatedMyasthenia Gravis, MuSK | AChR Myasthenia GravisUnited States, Italy
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COUR Pharmaceutical Development Company, Inc.RecruitingMyasthenia Gravis | Generalized Myasthenia | AChR Myasthenia Gravis | MuSK MGUnited States
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Alexion Pharmaceuticals, Inc.CompletedMyasthenia Gravis | Myasthenia Gravis, Generalized | Myasthenia Gravis, Juvenile FormUnited States, Japan, Netherlands
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University of AlbertaWithdrawnHypoplastic Left Heart Syndrome | Congenital Heart Defect | TGA - Transposition of Great Arteries | Congential Absence of Heart Structure | Congenital Malformation of Heart, Unspecified | Hypoplastic Right Heart Syndrome | Congential Malformations of Aortic Valve | Congential Malformations of Great...Canada
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University Health Network, TorontoGrifols Therapeutics LLCCompleted
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argenxNot yet recruitingGeneralized Myasthenia Gravis
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Cabaletta BioRecruitingGeneralized Myasthenia Gravis (gMG)United States
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Fondation Ophtalmologique Adolphe de RothschildNot yet recruiting
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argenxRecruiting
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Myasthenia Gravis Rare Disease NetworkRecruitingMyasthenia Gravis | MuSK Myasthenia Gravis | MuSK MGUnited States
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Kyverna TherapeuticsNot yet recruitingGeneralized Myasthenia Gravis | Myasthenia Gravis
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UCB Biopharma SRLNot yet recruitingGeneralized Myasthenia Gravis
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Tang-Du HospitalRecruitingMyasthenia Gravis, GeneralizedChina
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Alexion Pharmaceuticals, Inc.RecruitingGeneralized Myasthenia Gravis | gMGSpain, Italy, United States, France, Switzerland, Serbia, Japan, Netherlands
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argenxRecruitingGeneralized Myasthenia GravisUnited States, Netherlands, Belgium, Poland, United Kingdom
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Regeneron PharmaceuticalsRecruitingGeneralized Myasthenia GravisUnited States, Japan, Spain, Taiwan, Germany, Italy, Canada, Turkey, Georgia, Belgium, India, Poland, Australia, Denmark, France, United Kingdom, Korea, Republic of, Serbia, Czechia
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Tang-Du HospitalRecruitingMyasthenia Gravis, GeneralizedChina
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Huashan HospitalRecruitingMyasthenia Gravis, GeneralizedChina
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Alexion Pharmaceuticals, Inc.RecruitingGeneralized Myasthenia GravisUnited States
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Tang-Du HospitalRecruitingOcular Myasthenia GravisChina
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Cartesian TherapeuticsRecruitingMyasthenia Gravis, GeneralizedUnited States, Canada
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UCB Biopharma SRLCompletedGeneralized Myasthenia GravisUnited States, Canada, Georgia, Germany, Italy, Japan, Poland, Serbia, Spain, United Kingdom