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Clinical Trials on Myopathic Symptoms
Total 242005 results
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Vastra Gotaland RegionEnrolling by invitationMusculoskeletal Diseases | Neuromuscular Diseases | Centronuclear Myopathy | Nemaline Myopathy | Congenital Myopathy | Myosin Storage MyopathySweden
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Northwestern UniversityTerminated
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Hadassah Medical OrganizationUnknown
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Radboud University Medical CenterUMC UtrechtNot yet recruitingCentronuclear Myopathy | Nemaline Myopathy | Central Core Disease | Multi-Minicore DiseaseNetherlands
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University of ManchesterKing's College Hospital NHS Trust; Northern Care Alliance NHS Foundation Trust and other collaboratorsActive, not recruitingMyositis | Idiopathic Inflammatory MyopathyUnited Kingdom
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Peking University People's HospitalUnknownInflammatory Myopathy
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Clinic for Special ChildrenRecruitingMyopathy | Myopathy; Hereditary | Myopathies, Nemaline | TNNT1-associated Myopathy | Infantile-onset Nemaline Rod Myopathy | Myopathy, Rod | Amish Nemaline Myopathy | Nemaline Myopathy 5 | NEM5 | Genetic Muscle Disease | Recessive Hereditary Disorder (Autosomal) | ANMUnited States
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Peking University People's HospitalUnknown
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Reata, a wholly owned subsidiary of BiogenAbbVieCompletedMItochondrial MyopathiesUnited States, Denmark
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Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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Cristina Domínguez GonzálezRecruiting
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingX-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-LinkedUnited Kingdom
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrCompleted
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DynacureTerminatedCentronuclear MyopathyFrance, Netherlands, United Kingdom, Belgium, Denmark, Germany
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DynacureWithdrawnCentronuclear Myopathy
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Valerion Therapeutics, LLCInstitut de Myologie, France; GenethonCompletedMyotubular MyopathyFrance, Belgium, United States, Canada, Germany, Italy, Spain
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Peking University People's HospitalRecruitingIdiopathic Inflammatory MyopathiesChina
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University Hospital, BrestRecruiting
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Astellas Gene TherapiesCompletedX-linked Myotubular MyopathyUnited States, France, United Kingdom, Canada, Germany
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University of FloridaAudentes TherapeuticsCompletedX-linked Myotubular MyopathyUnited States
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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Institut de Myologie, FranceDynacureCompletedCentronuclear MyopathyFrance, Belgium, Germany, Italy, Spain
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Cure CMDUniversity of Chicago; Boston Children's Hospital; Valerion Therapeutics, LLC; Congenital...Completed
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The First Affiliated Hospital with Nanjing Medical...Not yet recruitingCardiac Disease | Inflammatory Myopathy
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argenxRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory MyopathyUnited States, Germany, Spain, Korea, Republic of, Austria, Turkey, Lithuania, Australia, Thailand, Serbia, Poland, Italy, France, Netherlands, Argentina, United Kingdom, Georgia, Belgium, Bulgaria, Canada, Cyprus, Denmark, Greece, Hu... and more
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Reneo Pharma LtdTerminatedPrimary Mitochondrial MyopathySpain, Australia, Belgium, Denmark, Canada, United Kingdom, France, Germany, Hungary, Italy, Netherlands, New Zealand
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University of ManchesterKarolinska Institutet; Eli Lilly and Company; Clinical Trials Unit, ManchesterCompletedIdiopathic Inflammatory MyopathiesUnited Kingdom
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Yale UniversityCompletedIdiopathic Inflammatory MyopathiesUnited States
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Benha UniversityUnknownIdiopathic Inflammatory MyopathiesEgypt
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DynacureWithdrawnCentronuclear MyopathyGermany, France
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argenxRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory MyopathyKorea, Republic of, Thailand, United States, Bulgaria, Taiwan, Argentina, Belgium, Cyprus, Denmark, France, Georgia, Germany, Greece, Italy, Lithuania, Czechia, Sweden
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University of Sao PauloCompletedPhysical Activity | Idiopathic Inflammatory MyopathiesBrazil
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The Emmes Company, LLCUnited Mitochondrial Disease Foundation; PolG Foundation Mito AustraliaRecruitingPolG, Primary Mitochondrial MyopathyUnited States
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Astellas Pharma IncActive, not recruitingPrimary Mitochondrial MyopathyUnited States
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Astellas Gene TherapiesCompletedMales With X-linked Myotubular Myopathy (XLMTM)United States, United Kingdom
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Reneo Pharma LtdCompletedPrimary Mitochondrial MyopathyUnited States, Spain, Australia, France, United Kingdom, New Zealand, Denmark, Norway, Czechia, Belgium, Canada, Germany, Hungary, Italy, Netherlands
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Stealth BioTherapeutics Inc.TerminatedPrimary Mitochondrial MyopathyUnited States, Germany, Canada, Italy, United Kingdom, Denmark, Hungary
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Reneo Pharma LtdTerminatedPrimary Mitochondrial MyopathyUnited Kingdom
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Eduardo N. ChiniRecruitingMitochondrial MyopathyUnited States
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University of HelsinkiHelsinki University Central Hospital; University of Iowa; Institute for Molecular...CompletedMitochondrial Myopathies
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Cabaletta BioRecruitingIdiopathic Inflammatory Myopathy | Dermatomyositis | Immune-Mediated Necrotizing Myopathy | Anti-Synthetase SyndromeUnited States
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Radboud University Medical CenterCompletedInspiratory Muscle Training | Nemaline MyopathyNetherlands
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Centre Hospitalier Universitaire de NiceRecruitingMitochondrial MyopathiesFrance
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University of HelsinkiHelsinki University Central Hospital; Institute for Molecular MedicineCompletedMitochondrial MyopathiesFinland