Clinical Trials on Myopathy; Primary in France

Total 5543 results

Reneo Pharma Ltd

Terminated

An Open Label, Long Term Safety Study of REN001 in Primary Mitochondrial Myopathy Patients (Stride Ahead)

Primary Mitochondrial Myopathy

Spain, Australia, Belgium, Denmark, Canada, United Kingdom, France, Germany, Hungary, Italy, Netherlands, New Zealand
Reneo Pharma Ltd

Completed

An Efficacy and Safety Study of 24 Week Treatment With Mavodelpar (REN001) in Primary Mitochondrial Myopathy Patients (STRIDE)

Primary Mitochondrial Myopathy

United States, Spain, Australia, France, United Kingdom, New Zealand, Denmark, Norway, Czechia, Belgium, Canada, Germany, Hungary, Italy, Netherlands
Ultragenyx Pharmaceutical Inc

Terminated

Study to Evaluate the Safety and Efficacy of Aceneuramic Acid Extended-Release (Ace-ER) Tablets in Patients With Glucosamine (UDP-N-acetyl)-2-epimerase Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)

Hereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing Myopathy

United States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
Central Hospital, Nancy, France

Unknown

Juvenile Autoimmune Necrotizing Myopathies (MYONECPED)

Immune-Mediated Necrotizing Myopathy

France
Ultragenyx Pharmaceutical Inc

Terminated

A Study to Evaluate the Safety of Aceneuramic Acid Extended Release (Ace-ER; UX001) Tablets in Glucosamine (UDP-N-acetyl)-2-Epimerase (GNE) Myopathy (GNEM) (Also Known as Hereditary Inclusion Body Myopathy [HIBM]) Patients With Severe Ambulatory Impairment

Hereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing Myopathy

Canada, United States, Bulgaria
Dynacure

Withdrawn

Early Phase Human Drug Trial to Investigate DYN101 in Participants 2 to 17 Years With Centronuclear Myopathies (DyNaMic)

Centronuclear Myopathy

Germany, France
Astellas Gene Therapies

Completed

A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects (INCEPTUS)

X-linked Myotubular Myopathy

United States, France, United Kingdom, Canada, Germany
Ra Pharmaceuticals

Terminated

Safety and Efficacy Study of Zilucoplan in Subjects With Immune-Mediated Necrotizing Myopathy

Immune Mediated Necrotizing Myopathy

United States, Netherlands, France, United Kingdom
Astellas Gene Therapies

Active, not recruiting

Gene Transfer Clinical Study in X-Linked Myotubular Myopathy (ASPIRO)

X-Linked Myotubular Myopathy

United States, Canada, France, Germany
Ultragenyx Pharmaceutical Inc
Newcastle University

Completed

GNE-Myopathy Disease Monitoring Program (GNEM-DMP): A Registry and Prospective Observational Natural History Study to Assess GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM)

Hereditary Inclusion Body Myopathy | GNE Myopathy | Nonaka Disease | Quadriceps Sparing Myopathy (QSM) | Distal Myopathy With Rimmed Vacuoles (DMRV)

United States, Bulgaria, Canada, France, United Kingdom
Ultragenyx Pharmaceutical Inc

Completed

Phase 3 Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Sialic Acid in Patients With Glucosamine (UDP-N-acetyl)-2-epimerase Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM) (GNEM)

Hereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type

United States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
Assistance Publique - Hôpitaux de Paris

Terminated

Pharmacological Treatment of a Rare Genetic Disease: N-acetylcysteine in Myopathy Associated Selenoprotein N-related Myopathy (SEPN1-RM) (SelNac)

Selenoprotein N-related Myopathy

France
Centre Hospitalier Universitaire de Nice

Recruiting

Home Based Personalized Training and Video Consultation in Mitochondrial Myopathies: Study of Efficacy and Tolerance. (TELE-MIT)

Mitochondrial Myopathies

France
Dynacure

Terminated

Early Phase Human Drug Trial to Investigate Dynamin 101 (DYN101) in Patients ≥ 16 Years With Centronuclear Myopathies (Unite-CNM)

Centronuclear Myopathy

France, Netherlands, United Kingdom, Belgium, Denmark, Germany
Institut de Myologie, France
Dynacure

Completed

Prospective Natural History Study of Patients With Myotubular Myopathy and Other CentroNuclear Myopathies (NatHis-CNM)

Centronuclear Myopathy

France, Belgium, Germany, Italy, Spain
University Hospital, Montpellier

Completed

Effects of Statins on Pro- and Antioxidant Status : Link With Statin-Associated Myopathy.

Healthy

France
Institut National de la Santé Et de la Recherche...

Completed

IRM Cardiaque en Respiration Libre Pour Des Patients Atteints de Dystrophinopathie sévère

Duchenne or Severe Becker Myopathy

France
Assistance Publique - Hôpitaux de Paris

Recruiting

Feasibility of Magnetic-end Double-J Ureteral Stent Use in Children (EFUJA)

Kidney Transplantation | Uropathy

France
Valerion Therapeutics, LLC
Institut de Myologie, France; Genethon

Completed

Prospective, Longitudinal Study of the Natural History and Functional Status of Patients With Myotubular Myopathy (MTM) (MTM)

Myotubular Myopathy

France, Belgium, United States, Canada, Germany, Italy, Spain
Institut de Myologie, France

Recruiting

Assessment of Safety and Acute Effects of a Knee-hip Powered Soft Exoskeleton in Patients With Neuromuscular Disorders (Exo-NMD1)

Muscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital Myopathy

France
Institut de Myologie, France

Recruiting

Assessment of Safety and Acute Effects of a Lower-limb Powered Dermoskeleton in Patients With Neuromuscular Disorders (Exo-KGO1)

Muscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital Myopathy

France
University Hospital, Brest

Recruiting

Adult Autoimmune Myopathies (MAIA) (MAIA)

Idiopathic Inflammatory Myopathies

France
argenx

Recruiting

A Study to Assess the Long-term Safety and Efficacy of a Subcutaneous Formulation of Efgartigimod in Adults With Active Idiopathic Inflammatory Myopathy (ALKIVIA+)

Myositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory Myopathy

Korea, Republic of, Thailand, United States, Bulgaria, Taiwan, Argentina, Belgium, Cyprus, Denmark, France, Georgia, Germany, Greece, Italy, Lithuania, Czechia, Sweden
University Hospital, Clermont-Ferrand

Recruiting

Metabolomic Approach During Exercise Testing in Myalgia Induced by eXercise (Matmix)

Metabolic Myopathy

France
Cabaletta Bio

Recruiting

RESET-Myositis: An Open-Label Study to Evaluate the Safety and Efficacy of CABA-201 in Subjects With Active Idiopathic Inflammatory Myopathy

Idiopathic Inflammatory Myopathy | Dermatomyositis | Immune-Mediated Necrotizing Myopathy | Anti-Synthetase Syndrome

United States
University Hospital, Montpellier

Recruiting

Improvement of DIAgnostic and Phenotype-genotype Correlation Studies in Patients With MYOpathy Suspected of TITinopathy (DIAMYOTIT)

Genetic Disease | Myopathy | Phenotypic Abnormality

France
Centre Hospitalier Universitaire de Nice

Completed

Arthroplasty Versus Fusion in Anterior Cervical Surgery: Prospective Study of the Impact on the Adjacent Level (PROCERV)

Clinical Radiculopathy | Myelopathy Due to a Cervical Disk Disease

France
argenx

Recruiting

A Study to Investigate the Efficacy and Safety of Efgartigimod PH20 SC in Adult Participants With Active Idiopathic Inflammatory Myopathy. (ALKIVIA)

Myositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory Myopathy

United States, Germany, Spain, Korea, Republic of, Austria, Turkey, Lithuania, Australia, Thailand, Serbia, Poland, Italy, France, Netherlands, Argentina, United Kingdom, Georgia, Belgium, Bulgaria, Canada, Cyprus, Denmark, Greece, Hu... and more
Newcastle-upon-Tyne Hospitals NHS Trust
Jain Foundation

Active, not recruiting

Clinical Outcome Study for Dysferlinopathy (Jain COS)

Dysferlinopathy | LGMD2B Now Classified as LGMDR2 | Miyoshi Myopathy

Korea, Republic of, Chile, Spain, United States, Denmark, France, Italy, Japan, United Kingdom
CHU de Reims

Unknown

FUSION EVALUATION AFTER ANTERIOR CERVICAL DISCECTOMY AND FUSION WITH STAND ALONE LOCKING CAGE WITH BLADE HRCC®

Cervical Radiculopathy | Cervical Myelopathy | Cervical Spinal Fusion

France
University Hospital, Brest

Recruiting

Metabolic Exercise Testing (RANNOU)

Myalgia | Exercise Test | Metabolic Myopathies

France
University Hospital, Montpellier
Centre Hospitalier Universitaire de Nīmes

Completed

Descriptive Study of Acute Spontaneous Spinal Cord Infarction (EDMIAS)

Spinal Cord Infarction | Spinal Cord Stroke | Vascular Myelopathy

France
University Hospital, Montpellier

Completed

ICU Acquired Neuromyopathy and Diaphragm Function

Critical Illness Myopathy | Respiratory Paralysis

France
Hospices Civils de Lyon

Recruiting

Identification of New Markers of Atrial Myopathy in Patients With Embolic Stroke of Undetermined Source (ESUS) From MRI 4D Data (IRM 4D-AVC)

Embolic Stroke of Undetermined Source

France
Bristol-Myers Squibb

Completed

Trial to Evaluate the Efficacy and Safety of Abatacept in Combination With Standard Therapy Compared to Standard Therapy Alone in Improving Disease Activity in Adults With Active Idiopathic Inflammatory Myopathy

Dermatomyositis | Polymyositis | Autoimmune Necrotizing Myopathy | Overlap Myositis | Juvenile Myositis Above the Age of 18

France, United States, Australia, Brazil, Czechia, Germany, Italy, Japan, Korea, Republic of, Mexico, Sweden
Centre d'Investigation Clinique et Technologique...

Unknown

Prognostic Factors , Morbidity and Mortality in Patients With Neuromuscular Disorders Admitted in ICU

Muscular Dystrophies | Intensive Care (ICU) Myopathy

France
University Hospital, Strasbourg, France

Recruiting

Search for Diagnostic and Prognostic Biomarkers in Systemic Sclerosis and Inflammatory Myopathies (SCLEROMYOMICS)

Systemic Sclerosis | Inflammatory Myopathies

France
Centre d'Investigation Clinique et Technologique...
Philips Respironics; Adep Assistance

Completed

Efficacy and Tolerance of AVAPS Mode in Myotonic Dystrophy

Myopathy

France
Hopital Foch

Completed

Management of Giant Thoracic Disc Hernias by Thoracoscopy: Experience of 52 Cases (GHTT)

Myelopathy | Giant Thoracic Herniation

France
Juno Therapeutics, Inc., a Bristol-Myers Squibb...
Bristol-Myers Squibb Services Unlimited Company

Recruiting

A Study of CC-97540, CD-19-Targeted Nex-T CAR T Cells, in Participants With Severe, Refractory Autoimmune Diseases

Systemic Lupus Erythematosus | Systemic Sclerosis | Idiopathic Inflammatory Myopathy

United States, Belgium, France, Spain, Germany, Italy
Assistance Publique - Hôpitaux de Paris
Association Française contre les Myopathies (AFM), Paris

Unknown

Efficacy and Tolerance of Early Launching of Nocturnal Non Invasive (DYVINE)

Respiratory Insufficiency | Myopathy | Muscular Weakness

France
Nantes University Hospital
Ministry of Health, France; University Hospital, Tours

Completed

Impact of Early Low-Calorie Low-Protein Versus Standard Feeding on Outcomes of Ventilated Adults With Shock (NUTRIREA3)

Shock | Critical Illness | Critical Illness Myopathy | Mechanical Ventilation | Nosocomial Infection

France, Guadeloupe
Centre Hospitalier Universitaire de Besancon

Unknown

Access to Maternity and Risk Factors in a Non-consultant Population (PROXIMA)

Post Partum Depression

France
Ferring Pharmaceuticals

Completed

A 6-week Open Label Cross-over Study With 2 Different Daily Doses of Minirin® Oral Lyophilisate in Children and Adolescents With Primary Nocturnal Enuresis (PNE) (PALAT)

Primary Nocturnal Enuresis

France
University Hospital, Bordeaux

Completed

Impact of Local Biopsy to the Endometrium Prior to Controlled Ovarian Stimulation on Clinical Pregnancy (NIDABRECHE)

Primary or Secondary Infertility

France
Centre Hospitalier Universitaire de Besancon

Terminated

Transfer and Ultrafiltration In Peritoneal Dialysis (TULIPE)

End-stage Renal Disease

France
Stallergenes Greer

Completed

Safety and Efficacy on Phase III Study on 300 IR SLIT to Patients Suffering From Grass Pollen Rhinoconjunctivitis

Primary Disease

France, Italy, Spain
Biocodex

Completed

Evaluation of the Efficacy of Stiripentol (Diacomit) as Monotherapy for the Treatment of Primary Hyperoxaluria

Primary Hyperoxaluria

France
Hopital Jean Minjoz

Unknown

NGAL Predictive Value of Acute Kidney Failure After Cardiac Surgery in Patients With Preoperative Chronic Kidney Failure (NGAL-CKF)

Cardiac Surgical Procedures | Preoperative KIDNEY FAILURE, CHRONIC | Postoperative KIDNEY FAILURE, ACUTE

France
University Hospital, Strasbourg, France

Recruiting

Phenotyping of Primary Hyperoxaluria (PHENO-HOPLA)

Primary Hyperoxaluria

France

Clinical Trials on Myopathy; Primary in France

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