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Clinical Trials on Myopia; Refractive Error in United Kingdom
Total 2287 results
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National Institute of Dental and Craniofacial Research...CompletedDiabetes Mellitus | Head and Neck Neoplasms | Dental Caries | Sarcoidosis | Cystinosis | Sjorgren's SyndromeUnited States
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Boston Children's HospitalChildren's Hospital Medical Center, CincinnatiRecruitingShwachman-Diamond Syndrome | Shwachman-Diamond Syndrome-LikeUnited States
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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Michio HiranoSanthera PharmaceuticalsCompletedMELAS SyndromeUnited States
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedMELAS Syndrome | Lactic Acidosis | Mitochondrial MyopathyUnited States
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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Amydis Inc.National Institutes of Health (NIH); National Institute on Aging (NIA)Recruiting
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Genelex CorporationCompletedDrug Metabolism, Poor, CYP2D6-RELATED | Drug Metabolism, Poor, CYP2C19-RELATED | Cytochrome P450 CYP2D6 Enzyme Deficiency | Cytochrome P450 CYP2C9 Enzyme Deficiency | Cytochrome P450 CYP2C19 Enzyme Deficiency | Poor Metabolizer Due to Cytochrome P450 CYP2D6 Variant | CYP2D6 Polymorphism | Ultrarapid... and other conditionsUnited States
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Porteus, Matthew, MDRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Fred Hutchinson Cancer CenterNational Heart, Lung, and Blood Institute (NHLBI); Rocket Pharma LimitedTerminated
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Sanguine BiosciencesTerminated
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)Completed
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Unspecified Adult Solid Tumor, Protocol Specific | Fanconi AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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ZevraDenmarkAvailableNiemann-Pick Disease, Type CUnited States
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Auburn UniversityCompletedAlzheimer Disease | Cerebral Amyloid AngiopathyUnited States
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Advicenne PharmaTerminatedDistal Renal Tubular AcidosisUnited States, Canada
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Children's Hospital Medical Center, CincinnatiRecruiting
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Boston Children's HospitalTerminatedFanconi Anemia | Dyskeratosis CongenitaUnited States
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Masonic Cancer Center, University of MinnesotaWithdrawn
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University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)TerminatedAdrenoleukodystrophy | AdrenomyeloneuropathyUnited States
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Masonic Cancer Center, University of MinnesotaRecruiting
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingCerebral Adrenoleukodystrophy | Adrenoleukodystrophy | ALD (Adrenoleukodystrophy)United States
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Hugo W. Moser Research Institute at Kennedy Krieger...TerminatedAdrenoleukodystrophyUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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Michigan Technological UniversityWithdrawnHyper IgD Syndrome | Mevalonate Kinase DeficiencyUnited States, Netherlands
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Stanford UniversityNational Cancer Institute (NCI); Harvard UniversityCompletedCerebral Palsy | Childhood Cancer | Congenital Heart Disease | Chronic Lung Disease | Congenital Metabolic Disorder | GastrostomyUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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Yale UniversityRheumatology Research FoundationRecruitingRheumatic Diseases | Rheumatoid Arthritis | Systemic Lupus Erythematosus | Systemic Sclerosis | Dermatomyositis | Polymyositis | Giant Cell Arteritis | Polymyalgia Rheumatica | Psoriatic Arthritis | Sjogren's Syndrome | Antiphospholipid Syndrome | Sarcoidosis | Lyme Disease | Ankylosing Spondylitis | Scleroderma | Reactive... and other conditionsUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingMyelodysplastic Syndromes | Fanconi Anemia | Severe Aplastic AnemiaUnited States
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The Cleveland ClinicActive, not recruitingAL Amyloidosis | Amyloidosis | Amyloid Neuropathies, Familial | Amyloid | Transthyretin Amyloidosis | Amyloid Cardiomyopathy | Amyloid - PrimaryUnited States
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Bellus Health IncNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Neurologic Diseases, GeneralUnited States
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Thomas S. ScanlanWithdrawnAdrenomyeloneuropathy | X-Linked AdrenoleukodystrophyUnited States
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
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PfizerCompletedTransthyretin Amyloidosis | Transthyretin Gene MutationsUnited States, France, Spain, Taiwan, Israel, Korea, Republic of, Denmark, Canada, Netherlands, Japan, Sweden, Brazil, Mexico, Argentina, Portugal, Belgium, Bulgaria, Cyprus, Germany, Italy, Malaysia, Romania, Saudi Arabia, Turkey, United...
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingFanconi Anemia | Squamous Cell CarcinomaUnited States
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Masonic Cancer Center, University of MinnesotaNational Institutes of Health (NIH)RecruitingFanconi Anemia | Oral Cavity Carcinoma | Alcohol-Related CarcinomaUnited States
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRecruitingRestless Legs Syndrome | AdrenoleukodystrophyUnited States, Netherlands
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Neurogene Inc.TerminatedCharcot-Marie-Tooth Disease | Hereditary Motor and Sensory Neuropathy IVUnited States
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Emory UniversityCompletedSickle Cell Disease | Fanconi Anemia | Hurler Syndrome | Chronic Granulomatous Disease | Severe Congenital Neutropenia | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Thalassemia Major | Leukocyte... and other conditionsUnited States
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NeuroVia, Inc.UnknownX-Linked AdrenoleukodystrophyUnited States
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States