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Clinical Trials on Myotonia Dystrophica
Total 1589 results
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CHU de ReimsCompletedMyotonic Dystrophy Type 1 (DM1)France
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McMaster UniversityNot yet recruiting
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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Centre Hospitalier Universitaire de NiceWithdrawn
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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AMO Pharma LimitedCompletedMyotonic Dystrophy 1United Kingdom
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Huashan HospitalEnrolling by invitation
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Centre d'Investigation Clinique et Technologique...Recruiting
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Massachusetts General HospitalRecruiting
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Institut de Myologie, FranceEnrolling by invitationMyotonic Dystrophy Type 1France
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Insmed IncorporatedMuscular Dystrophy AssociationCompleted
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Prof. Dr. Benedikt SchoserCompleted
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IRCCS San Camillo, Venezia, ItalyCompletedMyotonic Dystrophy Type 1 (DM1)
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Assistance Publique - Hôpitaux de ParisNot yet recruitingMyotonic Dystrophy 1 | Steinert's Disease | MetforminFrance
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of... and other collaboratorsCompletedMyotonic Dystrophy Type 1Netherlands, France, Germany, United Kingdom
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Castle Creek Biosciences, LLC.TerminatedEpidermolysis Bullosa Dystrophica, RecessiveUnited States
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Instituto de Investigación Hospital Universitario...Instituto de Salud Carlos III; Universidad Carlos III Madrid (TERMeG); St John... and other collaboratorsUnknownEpidermolysis Bullosa Dystrophica, RecessiveSpain
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Krystal Biotech, Inc.CompletedDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis Bullosa | DEB - Dystrophic Epidermolysis BullosaUnited States
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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National Institute of Respiratory Diseases, MexicoUnknownMyotonic Dystrophy 1 | Steinert DiseaseMexico
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Massachusetts General HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital; University...Recruiting
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Newcastle UniversityRecruiting
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Poitiers University HospitalTerminated
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Myogem Health Company, S.L.CompletedMyotonic Dystrophy 1Spain
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University of Campania "Luigi Vanvitelli"RecruitingSudden Cardiac Death | Myotonic Dystrophy 1Italy
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Lupin Ltd.Recruiting
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Lupin Ltd.Active, not recruitingMyotonic DystrophyFrance, Germany, United Kingdom
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University of NancyCentral Hospital, Nancy, FranceCompleted
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University of VersaillesAssistance Publique - Hôpitaux de Paris; Association Française contre les Myopathies...Completed
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University of RochesterCompletedMyotonic Muscular Dystrophy
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Krystal Biotech, Inc.RecruitingDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis BullosaUnited States
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Fondazione Serena Onlus - Centro Clinico NeMO MilanoAzienda Ospedaliera Città della Salute e della Scienza di Torino; Fondazione... and other collaboratorsActive, not recruiting
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Krystal Biotech, Inc.CompletedDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis BullosaUnited States
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University Hospital, LilleRecruitingDiabetes | Myotonic Dystrophy 1 | Carbohydrate IntoleranceFrance
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University College, LondonNational Institute for Health Research, United Kingdom; Myotonic Dystrophy... and other collaboratorsRecruitingMyotonic Dystrophy 1 | Dysphagia, OropharyngealUnited Kingdom
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Assistance Publique - Hôpitaux de ParisRecherche Clinique Paris Descartes Necker Cochin Sainte Anne; AFM-Téléthon...Recruiting
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Centre d'Investigation Clinique et Technologique...Philips Respironics; Adep AssistanceCompleted
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Institut de Myologie, FranceCompleted
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University Hospital, LilleRecruitingMyotonic Dystrophy, SteinertFrance
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University Hospital, GrenobleCompletedMyotonic DystrophyFrance
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University of Texas Southwestern Medical CenterMassachusetts General HospitalRecruitingDystonia | Dystonia; Idiopathic | Dystonia, Primary | Dystonia, Secondary | Dystonia, Familial | Dystonia Disorder | Dystonias, Sporadic | Dystonia; Orofacial | Dystonia Lenticularis | Dystonia, Paroxysmal | Dystonia 6 | Dystonia 5 | Dystonia 8 | Dystonia 9 | Dystonia 19 | Dystonia 10 | Dystonia 11 | Dystonia 20 | Dystonia 12 | Dystonia... and other conditionsUnited States
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisUnknownRespiratory Insufficiency | Myopathy | Muscular WeaknessFrance
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Abeona Therapeutics, IncNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminatedRecessive Dystrophic Epidermolysis BullosaAustria
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Columbia UniversityTerminatedEpidermolysis BullosaUnited States
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University of Southern CaliforniaCompletedRecessive Dystrophic Epidermolysis Bullosa
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University of Southern CaliforniaCompleted
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King's College LondonUnknownRecessive Dystrophic Epidermolysis BullosaUnited Kingdom