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Clinical Trials on Myotonic Dystrophy Type 1
Total 4214 results
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Oslo University HospitalUniversity Hospital, AkerCompletedDiabetes Mellitus, Type 1 | Coronary Heart Disease | ComplicationsNorway
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsTerminatedFollicular Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular LymphomaUnited States
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ShireCompletedGaucher DiseaseUnited States, Spain, United Kingdom, Israel
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
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ISU Abxis Co., Ltd.CompletedGaucher Disease, Type 1
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, United Kingdom, Bulgaria, Canada, Colombia, India, Israel, Lebanon, Mexico, Russian Federation, Serbia, Tunisia
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
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AstraZenecaWithdrawnCore: Relapsed or Refractory Diffuse Large B-Cell Lymphoma | Module 1: Non-GCB Diffuse Large B-Cell Lymphoma
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Genzyme, a Sanofi CompanyWithdrawnGaucher Disease, Type 1United States, India
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ISU Abxis Co., Ltd.Completed
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Recurrent Primary Central Nervous System Neoplasm | Refractory Primary Central Nervous System Neoplasm | Recurrent Childhood Brain Stem Glioma | Recurrent Childhood Visual Pathway GliomaUnited States
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National Cancer Institute (NCI)CompletedParents of Children With Cancer | Parents of Children With NF1 | Parents of Children With Neurofibromatosis Type IUnited States, Canada
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The VA Western New York Healthcare SystemNot yet recruiting
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Novo Nordisk A/SWithdrawnDiabetes Mellitus, Type 2 | Diabetes | Diabetes Mellitus, Type 1 | Chronic Kidney Disease
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Integra LifeSciences CorporationTerminatedDiabetes Mellitus, Type 2 | Diabetes | Diabetic Foot | Diabetes Mellitus, Type 1United States
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Pharnext SACompletedCharcot-Marie-Tooth Disease | Hereditary Neuropathy With Liability to Pressure Palsies | Genetic DisordersFrance
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain
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Shaare Zedek Medical CenterRecruiting
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Alnylam PharmaceuticalsRecruitingPrimary Hyperoxaluria Type 1France, Spain, United States, Israel, Belgium, Switzerland, Germany, United Kingdom, Italy, Canada
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Second Affiliated Hospital, School of Medicine,...RecruitingOvarian Cancer | Neoadjuvant Chemotherapy | Anti-PD-1 | Neoadjuvant ImmunotherapyChina
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AVROBIOTerminatedGaucher DiseaseUnited States, Canada
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Hadassah Medical OrganizationCompleted
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AVROBIOTerminatedType 1 Gaucher DiseaseUnited States, Canada
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Shaare Zedek Medical CenterCompletedGaucher Disease, Type 1Israel
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The Methodist Hospital Research InstituteJohns Hopkins University; University of Colorado, Denver; University of Pennsylvania and other collaboratorsActive, not recruitingSpinocerebellar Ataxia 3 | Spinocerebellar Ataxia Type 1United States
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CEN BiotechTakeda; BioClinica, Inc.Completed
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ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
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ShireCompletedGaucher DiseaseUnited States, Israel, United Kingdom, Poland, Spain
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ShireApproved for marketingGaucher Disease, Type 1United States
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Roberto Léo da SilvaCompletedDiabetes Mellitus, Type 1 | Diabetic Cardiomyopathies | Autonomic Neuropathy, DiabeticBrazil
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University Research Foundation for Lysosomal Storage...University of PittsburghCompletedGaucher DiseaseUnited States
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Shaare Zedek Medical CenterCompletedGaucher Disease Type 1Israel
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National Cancer Institute (NCI)Canadian Cancer Trials GroupActive, not recruitingUnresectable Renal Cell Carcinoma | Stage III Renal Cell Cancer AJCC v7 | Stage IV Renal Cell Cancer AJCC v7 | Type 1 Papillary Renal Cell Carcinoma | Type 2 Papillary Renal Cell Carcinoma | Metastatic Papillary Renal Cell Carcinoma | Locally Advanced Papillary Renal Cell CarcinomaUnited States, Canada
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Sahlgrenska University Hospital, SwedenVastra Gotaland RegionRecruitingDiabetes Mellitus, Type 2 | Diabetes Mellitus | Diabetes | Diabetic Foot | Diabetes Complications | Diabetes Mellitus, Type 1Sweden
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Fondazione TelethonUnknownUsher Syndrome, Type 1BItaly, Netherlands, Spain
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QIAGEN Gaithersburg, IncCompletedRespiratory Syncytial Virus Infections | Influenza A | Rhinovirus | Influenza B | QIAGEN ResPlex II Advanced Panel | Infection Due to Human Parainfluenza Virus 1 | Parainfluenza Type 2 | Parainfluenza Type 3 | Parainfluenza Type 4 | Human Metapneumovirus A/B | Coxsackie Virus/Echovirus | Adenovirus Types B/C/E | Coronavirus Subtypes 229E and other conditionsUnited States
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National Cancer Institute (NCI)Active, not recruitingNeurofibroma | Neurofibromatosis Type 1 | Malignant Peripheral Nerve Sheath Tumor | Optic Glioma | Plexiform NeurofibromaUnited States
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Hereditary Neuropathy FoundationRecruitingCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease, Type IA | Charcot-Marie-Tooth Disease Type 2A | Charcot-Marie-Tooth | Charcot-Marie-Tooth Disease, Type IB | Charcot-Marie-Tooth Disease Type 2 | Charcot-Marie-Tooth Disease, Type 2C | Charcot-Marie-Tooth Disease Type 2A2B | Charcot-Marie-Tooth... and other conditionsUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingNeuroendocrine Neoplasm | Multiple Endocrine Neoplasia Type 1 | Advanced Carcinoid Tumor | Digestive System Neuroendocrine Neoplasm | Unresectable Carcinoid TumorUnited States
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Stanford UniversityJohns Hopkins University; University of California, San FranciscoRecruitingNeurofibromatosis 1United States
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Tianjin Medical University Cancer Institute and...Not yet recruitingEsophageal Squamous Cell Carcinoma | Progression to PD-1 AntibodyChina
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1United States
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Children's Hospital Medical Center, CincinnatiUnited States Department of DefenseRecruitingNeurofibromatosis 1United States
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NobelpharmaTerminated
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Harry T Whelan, MDCompletedNeurofibromatosesUnited States
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Shaare Zedek Medical CenterCompleted
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Changlin MeiThe First Affiliated Hospital with Nanjing Medical University; The First Affiliated... and other collaboratorsCompletedPolycystic Kidney, Type 1 Autosomal Dominant DiseaseChina
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher Disease Type 1United States
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University of ManchesterCompletedNeurofibromatosis 1United Kingdom