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Clinical Trials on Myotonic Dystrophy in Canada
Total 147 results
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Laval UniversityCompleted
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McMaster UniversityCompletedMuscular Dystrophies | Myotonic Dystrophy 1Canada
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Élise DuchesneFondation du Grand défi Pierre LavoieCompletedMyotonic Dystrophy 1Canada
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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Cynthia GagnonFondation du Grand défi Pierre LavoieCompletedEffects of a Multiple Component Training Program on Muscles in Adults With Myotonic Dystrophy Type 1Myotonic Dystrophy 1Canada
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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McMaster UniversityNot yet recruiting
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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Richard Barohn, MDCompletedNon-Dystrophic Myotonia | MyotoniaUnited States, Canada, Italy, United Kingdom
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Université de SherbrookeCentre de recherche du Centre hospitalier universitaire de Sherbrooke; Interdisciplinary... and other collaboratorsEnrolling by invitationUrinary Incontinence | Myotonic Dystrophy Type 1Canada
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ItalfarmacoCompletedDuchenne and Becker Muscular Dystrophy | Polycytemia VeraCanada
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy 1France, Canada
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Bioblast Pharma Ltd.CompletedMuscular Dystrophy, Oculopharyngeal (OPMD)Canada
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University of British ColumbiaTerminatedJuvenile Myoclonic Epilepsy | Childhood Absence Epilepsy | Juvenile Absence EpilepsyCanada
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Children's Hospital of Eastern OntarioCompletedDuchenne Muscular DystrophyCanada
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CHU de Quebec-Universite LavalRecruitingDuchenne Muscular DystrophyCanada
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Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
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University of CalgaryMuscular Dystrophy CanadaEnrolling by invitationMuscular Dystrophies | Oculopharyngeal Muscular Dystrophy | Myopathy; HereditaryCanada
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedDuchenne Muscular DystrophyCanada
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University Health Network, TorontoUnknownFuch's Endothelial Dystrophy | Bullous Keratopathy, Unspecified EyeCanada
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Bioblast Pharma Ltd.WithdrawnOculopharyngeal Muscular DystrophyCanada
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Queen's UniversityWithdrawnCataracts | Fuch's Endothelial DystrophyCanada
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Cooperative International Neuromuscular Research...United States Department of DefenseCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Japan, Canada
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Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
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PepGen IncRecruitingDuchenne Muscular DystrophyCanada
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Santhera PharmaceuticalsSanthera PharmaceuticalsRecruitingDuchenne Muscular DystrophyCanada
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Acceleron Pharma Inc. (a wholly owned subsidiary...Terminated
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King's College LondonKing's College Hospital NHS Trust; Charles University, Czech Republic; Hopital... and other collaboratorsRecruitingJuvenile Myoclonic EpilepsyUnited States, Canada, Czechia, Denmark, Estonia, France, Italy, Norway, United Kingdom
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NS Pharma, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Canada
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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Fulcrum TherapeuticsCompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States, Canada
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Children's Hospital of Eastern OntarioJesse's Journey-The Foundation for Gene and Cell TherapyCompletedDuchenne Muscular DystrophyCanada
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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University Health Network, TorontoDystonia Medical Research FoundationUnknownFocal Hand Dystonia | Writer's Cramp | Musician's Dystonia | Dystonic CrampCanada
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Sarepta Therapeutics, Inc.TerminatedMuscular Dystrophy, DuchenneUnited States, Canada
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Wave Life Sciences Ltd.CompletedDuchenne Muscular DystrophyBelgium, United Kingdom, France, United States, Italy, Canada, Netherlands
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Spain, Italy, Denmark, Canada, Germany, France, Netherlands, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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Centre integre universitaire de sante et de services...Active, not recruitingMotoric Cognitive Risk Syndrome | Aging DisorderCanada
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel