- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Myotonic Dystrophy, Type 1 (DM1)
Total 4345 results
-
Astellas Pharma IncTerminatedDuchenne Muscular Dystrophy (DMD)United States
-
Nippon Shinyaku Co., Ltd.Active, not recruiting
-
PfizerTerminatedA Low Interventional Study to Monitor Activity Using Wearable Sensors in Duchenne Muscular DystrophyDuchenne Muscular Dystrophy (DMD)United States
-
Sarepta Therapeutics, Inc.Completed
-
University Hospital, Basel, SwitzerlandCompletedDuchenne's Muscular Dystrophy (DMD)Switzerland
-
Santhera PharmaceuticalsCompletedDuchenne Muscular Dystrophy (DMD)Belgium
-
Peking Union Medical College HospitalNot yet recruitingDuchenne Muscular Dystrophy (DMD)
-
University of FloridaU.S. Army Medical Research and Development CommandRecruitingDuchenne Muscular Dystrophy (DMD)United States
-
Ondokuz Mayıs UniversityCompletedDuchenne Muscular Dystrophy (DMD)Turkey
-
Sarepta Therapeutics, Inc.CompletedDuchenne Muscular Dystrophy (DMD)United States
-
Parent Project, ItalyCompletedDuchenne Muscular Dystrophy (DMD)Italy
-
GenethonInstitute of MyologyCompletedDuchenne Muscular Dystrophy (DMD)France
-
Ann & Robert H Lurie Children's Hospital of ChicagoChildren's National Research InstituteWithdrawnDuchenne Muscular Dystrophy (DMD)United States
-
Centre d'Investigation Clinique et Technologique...Philips Respironics; Adep AssistanceCompleted
-
Institut de Myologie, FranceCompleted
-
University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Not yet recruitingMuscular Dystrophy | Exercise | Duchenne Muscular Dystrophy | Vasodilation | DMD | Muscular Dystrophy in Children | Duchenne Disease
-
LMU KlinikumRecruitingMyasthenia Gravis | Myotonic Dystrophy | Inclusion Body Myositis | Facioscapulohumeral Muscular Dystrophies | The Falls Efficacy Scale International | The Morse Fall ScaleGermany
-
Grete Andersen, MDRegion Capital Denmark; GCP-Copenhagen; Danish Region; Lupin Atlantis Holdings... and other collaboratorsRecruiting
-
University Hospital, GrenobleCompletedMyotonic DystrophyFrance
-
NS Pharma, Inc.Approved for marketingMuscular Dystrophy, Duchenne | DMD
-
Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy 1France, Canada
-
Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedCardiomyopathy | Duchenne Muscular Dystrophy (DMD)United States
-
Hoffmann-La RocheTerminatedMuscular Dystrophy (DMD)United States, Canada
-
Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy 1Netherlands
-
Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
-
Institute of Molecular and Clinical Ophthalmology...RecruitingStargardt Disease | Stargardt Disease 1 | Fundus Flavimaculatus | Macular Degeneration, Stargardt | Macular Dystrophy With Flecks, Type 1Switzerland
-
Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
-
University of BernUniversity Hospital Inselspital, Berne; University of Lausanne Hospitals; University... and other collaboratorsRecruitingCongenital Muscular Dystrophy | SMA | DMD | BMD | IMDSwitzerland
-
University Hospital of North NorwayUniversity of Tromso; Norwegian Muscle Disease Association (FFM); Norwegian National... and other collaboratorsActive, not recruitingMuscular Dystrophies | Limb Girdle Muscular Dystrophy | Limb Girdle Muscular Dystrophy, Type 2I | Limb Girdle Muscular Dystrophy R9 FKRP-relatedNorway
-
University of FloridaBrain and Spinal Cord Injury Research Trust FundCompletedDystonia | DYT-1 | DYT1 | DYT 1United States
-
ML Bio Solutions, Inc.RecruitingLimb-Girdle Muscular Dystrophy Type 2I (LGMD2I)United States, Netherlands, United Kingdom, Denmark, Australia, Italy, Norway
-
Linda Pax LowesRecruitingLimb-Girdle Muscular Dystrophy Type 2A | Limb-Girdle Muscular Dystrophy, Type 2EUnited States
-
Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)United States
-
Rigshospitalet, DenmarkCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy Type 2IDenmark
-
Virginia Commonwealth UniversityUniversity of Colorado, Denver; Washington University School of Medicine; University... and other collaboratorsRecruitingLimb Girdle Muscular Dystrophy | Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A | Limb Girdle Muscular Dystrophy Type R1 | LGMD2AUnited States, Netherlands, United Kingdom
-
Catholic University of the Sacred HeartFondazione TelethonUnknownMyotonic Dystrophy | Sudden Cardiac DeathItaly
-
Nationwide Children's HospitalMyonexus TherapeuticsRecruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
-
Sardocor Corp.Not yet recruitingDMD-Associated Dilated Cardiomyopathy
-
Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationHypertrophic Cardiomyopathy (HCM) | Long QT Syndrome (LQTS) | Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT) | Inherited Cardiac Arrythmias | Brugada Syndrome (BrS) | Early Repolarization Syndrome (ERS) | Arrhythmogenic Cardiomyopathy (AC, ARVD/C) | Dilated Cardiomyopathy (DCM) | Muscular... and other conditionsUnited States
-
Mads Peter Godtfeldt StemmerikEdgewise Therapeutics, Inc.CompletedBecker Muscular Dystrophy | McArdle Disease | Limb-Girdle Muscular Dystrophy Type 2Denmark
-
Barcelona Macula FoundationRecruitingRetinitis Pigmentosa | Choroideremia | Stargardt Disease 1 | Best Disease | Pattern Dystrophy of MaculaSpain
-
Northern Care Alliance NHS Foundation TrustBrighter ABCompletedDiabetes type1 | Diabetes type2United Kingdom
-
IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
-
Politecnico di MilanoIRCCS Eugenio Medea; Villa Beretta Rehabilitation CenterCompletedMuscular Dystrophies | Muscular Dystrophy, Duchenne | Muscular Dystrophy, Becker | Muscular Dystrophy, Limb-Girdle Type 2Italy
-
Cairo UniversityCompletedMuscular Dystrophy, Duchenne TypeEgypt
-
University of FloridaTyler's Hope for a Dystonia Cure, IncCompleted
-
Hanmi Pharmaceutical Company LimitedUnknownType2 Diabetes Mellitus | Type1 Diabetes MellitusUnited States
-
Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy Type 2France, Italy, Spain
-
ResMedClinical Trial Center North Hamburg Germany; CRI-The Clinical Research Institute...TerminatedPulmonary Disease, Chronic Obstructive | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Duchenne Muscular Dystrophy | Myotonic Dystrophy | Spinal Cord Injury | Obesity Hypoventilation Syndrome | Kyphoscoliosis | Congenital Central Hypoventilation Syndrome | MyopathiesGermany
-
McGill University Health Centre/Research Institute...CHU de Quebec-Universite LavalUnknownType2 Diabetes | Islet Cell Transplantation | Type1 Diabetes MellitusCanada