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Clinical Trials on Myotonic Dystrophy 1
Total 7067 results
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Bioblast Pharma Ltd.WithdrawnOculopharyngeal Muscular DystrophyCanada
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National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
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Universitaire Ziekenhuizen KU LeuvenFund for Scientific Research, Flanders, Belgium; Funds for Research in Ophthalmology... and other collaboratorsCompletedFuchs' Endothelial DystrophyBelgium
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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Peter WiedemannInstitut für Angewandte TrainingswissenschaftUnknownPseudophakic Bullous Keratopathy | Fuchs Endothelial Corneal Dystrophy | Chemical Burn of Cornea | Posterior Polymorphous Corneal DystrophyGermany
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Başak Çağla ArslanHacettepe UniversityRecruitingDuchenne Muscular Dystrophy | Occupational Therapy | GamificationTurkey
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Assiut UniversityNot yet recruitingLimb-girdle Muscular Dystrophy
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsCompletedBecker Muscular Dystrophy | Healthy VolunteerUnited States
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Dokuz Eylul UniversityCompletedDuchenne Muscular Dystrophy | Upper Extremity ProblemTurkey
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | Gait | EnergyTurkey
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Rigshospitalet, DenmarkCompleted
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Istituto Ortopedico RizzoliCompletedBethlem Myopathy | Ullrich Congenital Muscular DystrophyItaly
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Upper Limb Function | Respiratory Function Test
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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University of RochesterLivionex IncCompletedCorneal Dystrophy, Band-ShapedUnited States
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University Hospital, RouenCompleted
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Children's Hospital of Eastern OntarioJesse's Journey-The Foundation for Gene and Cell TherapyCompletedDuchenne Muscular DystrophyCanada
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Monica Levy AndersenCompletedOther Diseases or ConditionsBrazil
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PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States
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Centre Hospitalier Universitaire de Saint EtienneKyoto University, Graduate School of MedicineNot yet recruitingCorneal DystrophiesFrance
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Benha UniversityCompletedDuchenne Muscular Dystrophy | Inflammatory MyopathyEgypt
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, France, Germany
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Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
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University of CalgaryMuscular Dystrophy CanadaEnrolling by invitationMuscular Dystrophies | Oculopharyngeal Muscular Dystrophy | Myopathy; HereditaryCanada
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Fondation Ophtalmologique Adolphe de RothschildTerminated
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University Hospital, MontpellierRecruitingPrimary Disease Fascioscapulohumeral Dystrophy (FSHD)France
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Universiteit AntwerpenUniversitaire Ziekenhuizen KU Leuven; KU Leuven; University Hospital, Antwerp; Research...CompletedDravet Syndrome | Severe Myoclonic Epilepsy of InfancyBelgium
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Muscle Strength | Hamstring Contractures | Lower ExtremityTurkey
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Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
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Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
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Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
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Tissue Tech Inc.CompletedCorneal Dystrophy, Epithelial Basement MembraneUnited States
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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CHABiotech CO., LtdCompletedStargardt's Macular DystrophyKorea, Republic of
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Astellas Institute for Regenerative MedicineCompleted
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University of SouthamptonUnknownKeratoconus | Fuchs Dystrophy | Corneal DiseaseUnited Kingdom
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Astellas Institute for Regenerative MedicineCompleted
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Sahra ŞirvanEnrolling by invitationDuchenne Muscular DystrophyTurkey
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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University Hospital, ToulouseUnknownDuchenne Muscular DystrophyFrance
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Hacettepe UniversityCompletedDuchenne Muscular DystrophyTurkey
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Oslo University HospitalUniversity Hospital of North Norway; The Research Council of NorwayCompletedDuchenne Muscular DystrophyNorway
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National Institute of Neurological Disorders and...CompletedHealthy | Dystonic DisorderUnited States
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Hacettepe UniversityCompletedGait Disorders, Neurologic | Body Posture | Balance | Foot PostureTurkey
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Ankara Universitesi TeknokentCompletedRetinitis Pigmentosa | Inherited Retinal DystrophyTurkey