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Clinical Trials on Myotonic Dystrophy 1
Total 7077 results
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University of Sao Paulo General HospitalUnknownHeart Failure | Chest Pain | Syncope | Pulmonary Embolism | Pulmonary Edema | Acute Coronary Syndromes | Aortic Aneurysm, Familial Thoracic 1Brazil
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Pharnext SACompletedCharcot-Marie-Tooth Disease | Hereditary Neuropathy With Liability to Pressure Palsies | Genetic DisordersFrance
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Jersey Shore University Medical CenterRutgers University; Rutgers Cancer Institute of New JerseyCompletedPancreatic Cancer | Parathyroid Disease | Thymic Cancer | MEN1 SyndromeUnited States
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI); GlaxoSmithKline; Millennium Pharmaceuticals,...TerminatedRecurrent Adult Diffuse Large Cell Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular Lymphoma | Recurrent Mantle Cell LymphomaUnited States
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National Cancer Institute (NCI)CompletedParents of Children With Cancer | Parents of Children With NF1 | Parents of Children With Neurofibromatosis Type IUnited States, Canada
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Centre Hospitalier Universitaire Saint PierreCompletedPertussis | Pregnancy | HIV-1-infection | Immunization; InfectionBelgium
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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Cwm Taf University Health Board (NHS)Cardiff University; Imperial College London; University of OxfordCompletedDiabetes Mellitus, Type 1 | SARS-CoV2 InfectionUnited Kingdom
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University of Alabama at BirminghamMedtronic; The Children's Tumor FoundationTerminatedNF1 | Congenital Pseudarthrosis of TibiaUnited States, Australia
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University Hospital ErlangenCompletedHypohidrotic Ectodermal DysplasiaGermany
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Vanderbilt University Medical CenterCompletedCognitive Impairment | Memory Impairment | HIV-1-infection | Aging, Premature | HIV-Associated Cognitive Motor ComplexUnited States
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Northwestern UniversityCompletedNeurofibromatosis Type 1 | Neurofibromatosis Type 2 | Adult Ependymoma | Recurrent Adult Brain Tumor | Acoustic Schwannoma | Adult Anaplastic Meningioma | Adult Grade I Meningioma | Adult Grade II Meningioma | Adult Meningeal Hemangiopericytoma | Adult Papillary MeningiomaUnited States
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Jazz PharmaceuticalsRecruitingSeizure in Participants With Tuberous Sclerosis Complex | Seizure in Participants With Dravet Syndrome | Seizure in Participants With Lennox-Gastaut SyndromeUnited States
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Sahlgrenska University Hospital, SwedenVastra Gotaland RegionRecruitingDiabetes Mellitus, Type 2 | Diabetes Mellitus | Diabetes | Diabetic Foot | Diabetes Complications | Diabetes Mellitus, Type 1Sweden
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Qi ZhouNot yet recruiting1. Relapsed Ovarian Cancer 2. Metastatic Ovarian Cancer 3. Endometrial Cancer 4. Cervical CancerChina
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University of ChicagoPfizer; Biogen; APDM Wearable TechnologiesActive, not recruitingSpinocerebellar Ataxia Type 3 | Friedreich Ataxia | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6United States
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Biohaven Pharmaceuticals, Inc.Active, not recruitingSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxias | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 10 | Spinocerebellar Ataxia Type 7 | Spinocerebellar Ataxia Type 8United States, China
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Children's National Research InstituteActive, not recruitingNeurofibromatosis 1 | Neurofibroma | Plexiform Neurofibroma | Atypical Neurofibroma | Atypical Neurofibromatosis | Von Recklinghausen DiseaseUnited States
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University of HawaiiTobira Therapeutics, Inc.CompletedAIDS Dementia Complex | Human Immunodeficiency Virus | HIV-1-Associated Cognitive Motor ComplexUnited States
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Fondazione TelethonUnknownUsher Syndrome, Type 1BItaly, Netherlands, Spain
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NovoCure Ltd.Unknown1-5 Brain Metastases From Non-Small Cell Lung CancerPoland, Czech Republic, Italy, France, Spain
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National Cancer Institute (NCI)CompletedCervical Cancer | Human Papilloma Virus Infection | Cervical Intraepithelial Neoplasia Grade 1United States
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Leigh R. Hochberg, MD, PhD.National Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Dysarthria | Brain Stem Infarctions | Locked in Syndrome | AnarthriaUnited States
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University of ZurichBalgrist University HospitalRecruitingComplex Regional Pain Syndrome I (CRPS I) | Complex Regional Pain Syndromes | Osteoarthritis Hand | Complex Regional Pain Syndrome Type II | Complex Regional Pain Syndrome Type I of the Upper Limb | Complex Regional Pain Syndrome I of Upper Limb | Complex Regional Pain Syndrome II of Upper Limb | Peripheral Nerve Injury Upper Limb and other conditionsSwitzerland
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Children's Hospital Medical Center, CincinnatiRecruitingLow Back Pain | Chronic Widespread Pain | Fibromyalgia | Complex Regional Pain Syndrome (CRPS) | Ehlers-Danlos Syndrome (EDS) | Amplified Musculoskeletal Pain Syndrome (AMPS)United States
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Steno Diabetes Center CopenhagenRigshospitalet, DenmarkRecruitingDiabetes Mellitus, Type 2 | Diabetes Mellitus, Type 1 | Hemodialysis | Peritoneal Dialysis | Chronic Kidney Disease | DialysisDenmark
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Lei LiRecruitingEpithelial Ovarian Cancer | Microsatellite Instability | PD-L1 | Nucleotide Variant | Copy Number Variation | Insertion-deletion Variation | Genomic Structural Variation | Total Mutation Burden | PD-1China
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Biohaven Pharmaceuticals, Inc.Active, not recruitingSpinocerebellar Ataxias | Spinocerebellar Ataxia Genotype Type 1 | Spinocerebellar Ataxia Genotype Type 2 | Spinocerebellar Ataxia Genotype Type 3 | Spinocerebellar Ataxia Genotype Type 6 | Spinocerebellar Ataxia Genotype Type 7 | Spinocerebellar Ataxia Genotype Type 8 | Spinocerebellar Ataxia Genotype...United States
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University Hospital, Clermont-FerrandCompletedCharcot-Marie-Tooth Type 1A NeuropathyFrance
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M.D. Anderson Cancer CenterActive, not recruitingGenetic Mutation | MEN1United States
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National Cancer Institute (NCI)WithdrawnNeoplasms, Nerve Tissue | Peripheral Nervous System Diseases | Heredodegenerative Disorders, Nervous System | Neurofibromatosis 1
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Alcon ResearchCompletedKeratoconjunctivitis | Corneal Edema | Corneal Ulcer | Bullous Keratopathy | Bell Palsy | Corneal Dystrophy | Entropion | Filamentary Keratitis | Corneal Erosion | Foreign Body in Cornea | Sicca Syndrome; Keratoconjunctivitis (Etiology)United States
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University College, LondonWashington University School of Medicine; University of Washington; Alzheimer... and other collaboratorsNot yet recruitingAlzheimer Disease | Autosomal Dominant Alzheimer Disease Due to Mutation of Presenilin 1 (Disorder) | Autosomal Dominant Alzheimer Disease Due to Mutation of Presenilin 2 (Disorder) | Autosomal Dominant Alzheimer Disease Due to Mutation of Amyloid Precursor Protein (Disorder)
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Therapeutic Advances in Childhood Leukemia ConsortiumRecruitingNeurofibromatosis 1 | JMML | Leukemia, Juvenile Myelomonocytic | JCML | CBL SyndromeUnited States
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Silesian Centre for Heart DiseasesMedical Research Agency, PolandNot yet recruitingHeart Failure | Breast Cancer | Breast Diseases | Cardiotoxicity | Molecular Mechanisms of Pharmacological Action | Angiotensin Receptor Antagonists | Neoplasm, Breast | Cardiac Toxicity | Angiotensin II Type 1 Receptor Blockers | Cancer, Therapy-Related | Antihypertensive Agents | Sacubitril/Valsartan | Cancer...Poland
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingNeuroendocrine Neoplasm | Multiple Endocrine Neoplasia Type 1 | Advanced Carcinoid Tumor | Digestive System Neuroendocrine Neoplasm | Unresectable Carcinoid TumorUnited States
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Weill Medical College of Cornell UniversityNational Cancer Institute (NCI); Merck Sharp & Dohme LLC; University of Sao Paulo and other collaboratorsActive, not recruitingHPV Infection | HIV-1-infection | HPV Positive Oropharyngeal Squamous Cell CarcinomaBrazil, Mexico, Puerto Rico
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University Hospital, Clermont-FerrandActive, not recruitingCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyEnrolling by invitationKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2) | Primary Hyperoxaluria Type 3 (PH3)United States, France, Germany, Japan, Lebanon, Spain, United Kingdom, Australia, Canada, Italy, Netherlands, Norway, Turkey
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J.M. de LaatRadboud University Medical Center; University Medical Center Groningen; Maastricht... and other collaboratorsRecruitingPrecision Radiotherapy Using MR-linac for Pancreatic Neuroendocrine Tumours in MEN1 Patients (PRIME)Multiple Endocrine Neoplasia Type 1 | Neuroendocrine Tumor of PancreasNetherlands
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Baylor College of MedicineChildren's Hospital of Philadelphia; Children's Hospital Colorado; Seattle Children... and other collaboratorsRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS DeficiencyUnited States
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyRecruitingEnd Stage Renal Disease | Primary Hyperoxaluria Type 2 | Primary Hyperoxaluria Type 1Germany, Spain, United States, United Kingdom, Italy, United Arab Emirates, Lebanon, Morocco, France, Romania
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Renalytix AI, Inc.Active, not recruitingDiabetic Kidney Disease | Chronic Kidney Disease, Stage 3 (Moderate) | Chronic Kidney Disease Stage 2 | Chronic Kidney Disease Stage 1United States
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University of CoimbraCompletedAutism Spectrum Disorder | Neurofibromatosis 1Portugal
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Janssen R&D IrelandCompletedHepatitis C Virus Genotype-1United States, France, United Kingdom, Germany, Spain, Portugal, Canada, Puerto Rico
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St. Marianna University School of MedicineUnknownHTLV-I-Associated MyelopathyJapan
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Wake Forest University Health SciencesNational Cancer Institute (NCI)CompletedAnatomic Stage I Breast Cancer AJCC v8 | Anatomic Stage IA Breast Cancer AJCC v8 | Anatomic Stage IB Breast Cancer AJCC v8 | Anatomic Stage II Breast Cancer AJCC v8 | Anatomic Stage IIA Breast Cancer AJCC v8 | Anatomic Stage IIB Breast Cancer AJCC v8 | Anatomic Stage III Breast Cancer AJCC v8 | Anatomic... and other conditionsUnited States
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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Steno Diabetes Center CopenhagenKing's College London; Juvenile Diabetes Research Foundation; Glostrup University...Not yet recruitingHypoxia | Diabetes Mellitus, Type 1 | Diabetic Nephropathies | Albuminuria | Nephropathy | Diabetic Complications Renal | Diabetic Complications CardiovascularDenmark
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Five Liters, Inc.RecruitingHeavy Menstrual Bleeding | Von Willebrand Disease, Type 1United States