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Clinical Trials on NGLY1 Deficiency in New Zealand
Total 1530 results
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ADMA Biologics, Inc.CompletedPrimary Immune Deficiency DisorderUnited States
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Pamlab, Inc.UnknownThe Nutritional Benefits of Metanx in Patients With Diabetic Peripheral Neuropathy (MEDIAN) (MEDIAN)Diabetic Peripheral Neuropathy | B Vitamin DeficiencyUnited States
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Icahn School of Medicine at Mount SinaiCompletedMetabolic Syndrome | Vitamin D Deficiency | PrediabetesUnited States
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Pharmacosmos A/SCompletedChronic Kidney Disease | Iron Deficiency Anemia | Iron Deficiency AnaemiaUnited States
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Mehrotra, Anita, M.D.American Heart Association; National Kidney FoundationCompletedVitamin D Deficiency | End-stage Renal DiseaseUnited States
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Seth I. Sokol, M.D.Albert Einstein College of Medicine; Yale University; Montefiore Medical Center; American Heart Association and other collaboratorsCompletedCoronary Artery Disease | Inflammation | Vitamin D Deficiency | Endothelial DysfunctionUnited States
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Chiesi Farmaceutici S.p.A.CompletedSevere Combined Immunodeficiency | Adenosine Deaminase DeficiencyUnited States
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New York Presbyterian HospitalCompletedNephrolithiasis | Vitamin D Deficiency | Urolithiasis | Idiopathic Hypercalciuria | Disorder of Vitamin DUnited States
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National Center for Research Resources (NCRR)Completed
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Yale UniversityBristol-Myers Squibb; Merck Sharp & Dohme LLCCompletedHIV Infections | Human Immunodeficiency Virus | AIDS | Acquired Immune Deficiency SyndromeUnited States
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ADMA Biologics, Inc.CompletedPrimary Immune Deficiency Disorders (PIDD)United States
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Columbia UniversityNew York Blood CenterCompleted
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University of New MexicoWithdrawnHypovitaminosis DUnited States
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Maimonides Medical CenterCompletedPolycystic Ovary Syndrome | Vitamin D DeficiencyUnited States
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Leadiant Biosciences, Inc.CompletedSevere Combined Immunodeficiency | ADA-SCID | Adenosine Deaminase DeficiencyUnited States
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MegaPro Biomedical Co. Ltd.TerminatedIron Deficiency AnemiaUnited States
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Columbia UniversityRecruitingImmune Deficiency | Allergic Inflammation | Immune Dysregulation DisorderUnited States
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AMAG Pharmaceuticals, Inc.CompletedIron Deficiency AnemiaUnited States, Canada, Hungary, Latvia, Poland, Lithuania, Puerto Rico
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Columbia UniversityClínica de Familia La Romana, Dominican RepublicRecruitingHIV Infections | Sexually Transmitted Diseases, Viral | Acquired Immune Deficiency SyndromeUnited States, Dominican Republic
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Columbia UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)WithdrawnPrimary Hyperparathyroidism | Vitamin D Deficiency | Osteoporosis | Osteopenia | HypercalcemiaUnited States
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Kirby InstituteGilead Sciences; Melanoma Institute Australia; St Vincent's Hospital, Sydney; Royal... and other collaboratorsActive, not recruitingCOVID-19 | Cancer | Primary Immune Deficiency Disorder | HIV-1-infection | Immunosuppression DisordersAustralia
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PfizerCompletedHIV Infections | CryptosporidiosisUnited States
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Cornell UniversityUniversity of RochesterCompletedIron DeficiencyUnited States
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Memorial Sloan Kettering Cancer CenterMerck Sharp & Dohme LLCRecruitingMetastatic Pancreatic Ductal Adenocarcinoma | Homologous Recombination Deficiency (HRD)United States
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Winthrop University HospitalNational Kidney FoundationCompletedVitamin D Deficiency | End Stage Renal DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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Ascendis Pharma Endocrinology Division A/SCompletedEndocrine System Diseases | Pituitary Diseases | Hormones | Growth Hormone Deficiency, Pediatric | hGH (Human Growth Hormone)United States, Armenia, Australia, Belarus, Bulgaria, Georgia, Greece, Italy, New Zealand, Poland, Romania, Russian Federation, Turkey, Ukraine
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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OctapharmaCompleted
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Lumos PharmaActive, not recruitingGrowth Hormone DeficiencyUnited States, Australia, Israel, New Zealand, Poland, Ukraine
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Yale UniversityNational Institute of Allergy and Infectious Diseases (NIAID); Robert Leet...Active, not recruitingMultiple Sclerosis | Autoimmune Blistering Disease | B-Cell DeficiencyUnited States
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New York Medical CollegeJohns Hopkins University; Children's Hospital of Philadelphia; Medical College... and other collaboratorsRecruitingPrimary Immune Deficiency Disorder | Viral InfectionUnited States
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI)RecruitingGastric Adenocarcinoma | Epstein-Barr Virus Positive | Mismatch Repair Protein Deficiency | Stage IB Gastric Cancer AJCC v7 | Stage II Gastric Cancer AJCC v7 | Stage IIA Gastric Cancer AJCC v7 | Stage IIB Gastric Cancer AJCC v7 | Stage III Gastric Cancer AJCC v7 | Stage IIIA Gastric Cancer AJCC v7 | Stage... and other conditionsUnited States
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Glycomine, Inc.Active, not recruitingPhosphomannomutase 2 DeficiencyUnited States, Spain, Portugal, Belgium, Czechia, France, Italy, Netherlands, Poland
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Bio Products LaboratoryCompletedFactor 10 DeficiencyUnited States
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Columbia UniversityUniversitat Autonoma de Barcelona; Instituto de Salud Carlos III; University... and other collaboratorsActive, not recruitingThymidine Kinase 2 Deficiency | Mitochondrial DNA Depletion Syndrome 2 Myopathic TypeUnited States
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ADMA Biologics, Inc.Active, not recruitingPrimary Immune Deficiency DisorderUnited States
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Inhibrx, Inc.RecruitingEmphysema | Alpha 1-Antitrypsin DeficiencyUnited States, Australia, United Kingdom, New Zealand
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New York Medical CollegeJohns Hopkins University; Children's Hospital of Philadelphia; Washington University... and other collaboratorsRecruitingPrimary Immune Deficiency Disorder | Cytomegalovirus InfectionsUnited States
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Yale UniversityNational Center for Research Resources (NCRR)CompletedVitamin D Deficiency | Polycystic Ovarian SyndromeUnited States
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Altus PharmaceuticalsUnknownGrowth Hormone DeficiencyUnited States
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ONYSuspendedChronic Lung Disease | RDS of Prematurity | Surfactant Protein B DeficiencyUnited States
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The Hospital for Sick ChildrenBristol-Myers SquibbTerminatedRefractory or Recurrent Hypermutated Malignancies | Biallelic Mismatch Repair Deficiency (bMMRD) Positive PatientsUnited States, France, Canada, Australia, Israel
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Yale UniversityNational Center for Advancing Translational Sciences (NCATS)SuspendedRickets | Hypophosphatemia | Hypercalciuria | XLH | HHRHUnited States
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OPKO Health, Inc.Active, not recruitingSafety and Efficacy Phase 3 Study of Long-acting hGH (MOD-4023) in Growth Hormone Deficient ChildrenPediatric Growth Hormone DeficiencyIsrael, United States, India, Korea, Republic of, Australia, Taiwan, Spain, Argentina, Belarus, Bulgaria, Canada, Colombia, Georgia, Greece, Mexico, New Zealand, Poland, Russian Federation, Ukraine, United Kingdom
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University of Colorado, DenverNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsRecruitingCDKL5 | CDKL5 Deficiency Disorder | CDDUnited States, Australia
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Renal Research InstituteUnknownSleep Apnea | ESRD | Oxygen DeficiencyUnited States
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Novo Nordisk A/SRecruitingGrowth Hormone Disorder | Growth Hormone Deficiency in ChildrenUnited States, Japan, Israel, India, Austria, Slovenia, Belgium, Brazil, France, Germany, Sweden, Turkey, Ukraine
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State University of New York - Downstate Medical...CompletedHyperparathyroidism | Congestive Heart Failure | Hypovitaminosis DUnited States