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Clinical Trials on Neuroaxonal Dystrophy, Atypical
Total 1639 results
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ProQR TherapeuticsWithdrawnCorneal Diseases | Fuchs Endothelial Corneal Dystrophy | FECD3 | LRS | Descemet's Membrane DisorderUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Spain, United Kingdom, Netherlands
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aTyr Pharma, Inc.CompletedLimb-Girdle Muscular Dystrophies | Facioscapulohumeral Muscular DystrophyUnited States, Denmark, France
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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Centre Hospitalier Régional Metz-ThionvilleCompletedPseudophakic Bullous Keratopathy | Fuchs' Endothelial Corneal Dystrophy | Descemet Membrane Endothelial Keratoplasty | Graft DetachmentFrance
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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Children's Healthcare of AtlantaWithdrawnScoliosis | Duchenne's Muscular DystrophyUnited States
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Nationwide Children's HospitalMyonexus TherapeuticsRecruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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Aerie PharmaceuticalsCompleted
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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InCor Heart InstituteUniversity of Sao Paulo; Federal University of Minas GeraisCompletedMyocardial Fibrosis | Muscular Dystrophies
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Peking University People's HospitalHangzhou Newhorizon Health Technology Co., Ltd.; Hangzhou Mingze Medical Research... and other collaboratorsRecruitingCervical Cancer | Cervical Adenocarcinoma | Cervical Squamous Cell Carcinoma | Human Papillomavirus Infection | Human Papilloma Virus | Adenocarcinoma in Situ | High-Grade Squamous Intraepithelial Lesions | Cervical Intraepithelial Neoplasia Grade II | Cervical Intraepithelial Neoplasia, Grade III | Atypical... and other conditionsChina
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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University Health Network, TorontoRecruiting
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Rennes University HospitalCompletedAtypical Cognitive DisordersFrance
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Cassella-med GmbH & Co. KGCompletedAtypical Depression
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University of MonsRecruitingFacioscapulohumeral Muscular DystrophyBelgium
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular DystrophyFrance
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Newcastle UniversityRecruitingFacioscapulohumeral Muscular DystrophyUnited Kingdom
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Hillel Yaffe Medical CenterRecruiting
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Centre Hospitalier Universitaire de NiceCompletedFacio-Scapulo-Humeral DystrophyFrance
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University of Kansas Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Robert Jones and Agnes Hunt Orthopaedic and District...CompletedFacioscapulohumeral Muscular Dystrophy
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationCompletedFacioscapulohumeral Muscular DystrophyUnited States, Australia
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Bioblast Pharma Ltd.CompletedMuscular Dystrophy, Oculopharyngeal (OPMD)Canada
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Rigshospitalet, DenmarkUnknownOculopharyngeal Muscular DystrophyDenmark
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Centre Hospitalier Universitaire de NiceCompletedFacioscapulohumeral Muscular DystrophyFrance
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Trefoil Therapeutics, Inc.CompletedCorneal Endothelial DystrophyUnited States
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University Health Network, TorontoRecruitingAtypical Femur Fracture | Atypical Subtrochanteric Fracture | Osteoporosis With AFfCanada
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Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedCardiomyopathy | Duchenne Muscular Dystrophy (DMD)United States
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Maastricht UniversityZonMw: The Netherlands Organisation for Health Research and Development; Utrecht... and other collaboratorsRecruitingAnorexia Nervosa | Bulimia Nervosa | Atypical Anorexia Nervosa (Other Specified Eating Disorder) | Atypical Bulimia Nervosa (Other Specified Eating Disorder)Netherlands
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Columbia UniversityNational Eye Institute (NEI); Centre Hospitalier National d'Ophtalmologie des... and other collaboratorsRecruitingRetinitis Pigmentosa | Best Vitelliform Macular DystrophyUnited States, Germany, France
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University Hospital, AngersFederico II University; University of Modena and Reggio EmiliaNot yet recruitingFacioscapulohumeral Muscular Dystrophy
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PYC TherapeuticsRecruitingRetinitis Pigmentosa | Eye Diseases, Hereditary | Retinal Dystrophies | Retinal Dystrophy Rod | Retinal Dystrophy Rod ProgressiveUnited States, Australia
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Centre Hospitalier Universitaire de NiceCompletedMuscular DystrophiesFrance
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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University of UtahCompletedMacular Dystrophy, CornealUnited States
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National Eye Institute (NEI)Bausch & Lomb Incorporated; Eye Bank Association of America; Midwest Eye Banks; Tissue Banks International and other collaboratorsCompletedCorneal Disease | Fuch's Dystrophy | Pseudophakic Corneal EdemaUnited States
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University of Kansas Medical CenterNational Institutes of Health (NIH)CompletedFacioscapulohumeral Muscular DystrophyUnited States
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
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Istanbul University - Cerrahpasa (IUC)CompletedFacioscapulohumeral Muscular DystrophyTurkey
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedFacioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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University of New MexicoUniversity of FloridaWithdrawnOculopharyngeal Muscular Dystrophy
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Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
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University Health Network, TorontoEli Lilly and Company; The Physicians' Services Incorporated FoundationCompletedNon Displaced Atypical Femoral FracturesCanada
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New York State Psychiatric InstituteEli Lilly and CompanyCompletedAtypical DepressionUnited States