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Clinical Trials on Neurodegenerative Disease, Hereditary
Total 377723 results
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | Prophylaxis | HAEAustria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Switzerland, United Kingdom, United States, Australia, Hong Kong, Korea, Republic of, New Zealand, Serbia, Slovakia, South Africa, Spain
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Pharming Technologies B.V.CompletedHereditary Angioedema | Genetic DisordersNetherlands, Romania
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Pharming Technologies B.V.CompletedGenetic DisordersNetherlands
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Pharming Technologies B.V.CompletedHereditary Angioedema | Angioneurotic EdemaNetherlands
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Pharming Technologies B.V.CompletedHereditary Angioedema | Genetic Disorders | Angioneurotic EdemaNetherlands, Romania
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Massachusetts Eye and Ear InfirmaryRecruitingFuchs' Endothelial Corneal DystrophyUnited States
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Aspa TherapeuticsRecruiting
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Radboud University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentUnknownColorectal Neoplasms | Hereditary Nonpolyposis Colorectal CancerNetherlands
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Michigan State UniversityRecruitingHereditary DiseasesUnited States
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Okuvision GmbHCompletedPrimary Open Angle Glaucoma | Retinal Vein Occlusion | Retinitis Pigmentosa | Retinal Artery Occlusion | Dry Age Related Macular Degeneration | Hereditary Macular Degeneration | Macula Off | Treated Retina Detachment | Non-Arthritic-Anterior-Ischemic Optic-Neuropathy | Hereditary Autosomal Dominant Optic... and other conditions
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London North West Healthcare NHS TrustCompletedColorectal Neoplasms, Hereditary NonpolyposisUnited Kingdom
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Oslo University HospitalUnknownCorneal Dystrophies, Hereditary | Fuchs' Endothelial Dystrophy | Corneal Transplantation | Descemet Stripping Automated Endothelial KeratoplastyNorway
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Sun Yat-sen UniversityCompletedImmune System Diseases | Autoimmune Diseases | Eye Diseases | Endocrine System Diseases | Thyroid Diseases | Eye Diseases, Hereditary | Graves Ophthalmopathy | Graves Disease | HyperthyroidismChina
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Istituto Ortopedico RizzoliCompletedExostoses, Multiple HereditaryItaly
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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Christine M. Kleinert Institute for Hand and MicrosurgeryUnknownMedian Nerve CompressionUnited States
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Aalborg University HospitalAarhus University Hospital; ARCEDI BiotechCompletedHereditary DiseasesDenmark
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Pacira CryoTech, Inc., a wholly owned subsidiary...CompletedEntrapment NeuropathyUnited States
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Chinese University of Hong KongRecruitingREM Sleep Behavior Disorder | NeurodegenerationHong Kong
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University of Texas Southwestern Medical CenterTerminatedHereditary Spherocytosis
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The Cleveland ClinicNational Eye Institute (NEI)CompletedRetinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...RecruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic ParaplegiaUnited States, South Africa
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Hereditary Breast Carcinoma | Hereditary Ovarian CarcinomaUnited States
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University College, LondonUnknownMitochondrial Diseases | Dystonia, Familial | Sporadic Dystonia | Parkinson Disease, Juvenile | Neurodegeneration With Brain Iron Accumulation 5
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BioCryst PharmaceuticalsApproved for marketingHereditary Angioedema | Prophylaxis | HAE
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University Hospital, GrenobleTerminatedHealthy Volunteers | Hereditary AngioedemaFrance
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Pharming Technologies B.V.CompletedGenetic DisordersNetherlands
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Massachusetts General HospitalHarvard Medical School (HMS and HSDM)RecruitingKeratoconus | Ectasia | Fuchs' Endothelial Dystrophy | CrosslinkingUnited States
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State Scientific Centre of Coloproctology, Russian...The Loginov MCSC MHD; Pirogov National Medical and Surgical Center; Moscow City... and other collaboratorsRecruitingColorectal Cancer | Lynch Syndrome | Hereditary Colorectal Cancer | MSIRussian Federation
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Singapore Eye Research InstituteUnknownFuchs' Endothelial Dystrophy | Bullous Keratopathy | Mild to Moderate Corneal Endothelial Decompensation | Post-surgical Corneal Decompensation (Irreversible)Singapore
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Murdoch Childrens Research InstituteMelbourne Health; Austin Health; Royal Brisbane and Women's Hospital; The University... and other collaboratorsCompletedHereditary HaemochromatosisAustralia
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University Hospital, AntwerpBelgium Health Care Knowledge CentreRecruitingCorneal Edema | Fuchs' Endothelial Dystrophy | Bullous Keratopathy | Pseudophakic Bullous Keratopathy | Corneal Endothelial DisorderBelgium
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University of California, San FranciscoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedAcute Intermittent Porphyria (AIP) | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP)United States
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The Third Xiangya Hospital of Central South UniversityNot yet recruitingCharcot-Marie-Tooth Disease (CMT)
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ENCellCompletedCharcot-Marie-Tooth Disease, Type IAKorea, Republic of
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University Medical Center GoettingenUniversity Hospital Muenster; Ludwig-Maximilians - University of MunichCompletedCharcot-Marie-Tooth Disease, Type IAGermany
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Genomic Prediction Inc.Active, not recruiting
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University of British ColumbiaChildren's & Women's Health Centre of British Columbia; Vancouver Foundation; Circle of CareTerminatedExostoses, Multiple HereditaryCanada
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St George's, University of LondonTerminatedEndometrial Cancer | Hereditary Non-polyposis Colon Cancer (hmsh2, hmlh1, hpms1, hpms2)United Kingdom
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University Medicine GreifswaldCompleted
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National Human Genome Research Institute (NHGRI)CompletedHereditary DiseasesUnited States
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Charite University, Berlin, GermanyShire International GmbHActive, not recruitingHereditary Autoinflammatory DiseaseGermany
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Penn State UniversityWithdrawn
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University College London HospitalsKingston University; Charcot Marie Tooth United KingdomCompletedCharcot-Marie-Tooth Disease, Type IAUnited Kingdom
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University of IowaNational Institute of Neurological Disorders and Stroke (NINDS); Muscular Dystrophy...CompletedCharcot Marie Tooth DiseaseUnited States
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University Hospital, GrenobleCompletedHereditary AngioedemaFrance
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The Cleveland ClinicNational Eye Institute (NEI)RecruitingRetinal Diseases | Retinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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VA Office of Research and DevelopmentNot yet recruitingParkinson Disease | Movement Disorders | NeurodegenerationUnited States
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Chang Gung Memorial HospitalNational Science Council, TaiwanCompleted
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Rhythm Pharmaceuticals, Inc.CompletedBardet Biedl Syndrome (BBS) | Alström Syndrome (AS)United States, United Kingdom, France, Canada, Puerto Rico, Spain