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Clinical Trials on Neuronal Ceroid Lipofuscinosis in United States
Total 1487 results
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University of RochesterRecruitingBatten Disease | Neuronal Ceroid Lipofuscinosis | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3 | Neuronal Ceroid Lipofuscinosis CLN5 | Neuronal Ceroid Lipofuscinosis CLN1 | Neuronal Ceroid Lipofuscinosis CLN2 | Neuronal Ceroid Lipofuscinosis CLN7 | Neuronal Ceroid Lipofuscinosis... and other conditionsUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingBatten Disease | Juvenile Neuronal Ceroid Lipofuscinosis (CLN3)United States
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Amicus TherapeuticsCompletedVariant Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Amicus TherapeuticsTerminatedBatten Disease | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3United States
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Weill Medical College of Cornell UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityTerminatedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedInfantile Neronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH)CompletedBatten Disease | Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky DiseaseUnited States, Italy, Germany, United Kingdom
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BioMarin PharmaceuticalActive, not recruitingLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2United States
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StemCells, Inc.CompletedNeuronal Ceroid LipofuscinosisUnited States
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Neurogene Inc.RecruitingNeuronal Ceroid Lipofuscinosis CLN5United States, United Kingdom
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University of RochesterBatten Disease Support and Research Assocation (BDSRA)CompletedJuvenile Neuronal Ceroid LipofuscinosisUnited States
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky Disease | CLN2 DisorderUnited States, Germany, Italy, United Kingdom
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky Disease | CLN2 DisorderUnited States, Germany, Italy, United Kingdom
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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Neurogene Inc.RecruitingCeroid Lipofuscinosis, Neuronal 5United States
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David L Rogers, MDActive, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United States
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Jessica ScherrBioMarin PharmaceuticalEnrolling by invitationBatten Disease | Neuronal Ceroid-Lipofuscinoses | CLN2United States
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StemCells, Inc.WithdrawnNeuronal Ceroid LipofuscinosisUnited States
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Nationwide Children's HospitalMassachusetts General HospitalCompletedNeuronal Ceroid Lipofuscinosis | Batten's DiseaseUnited States
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Children's Hospital of Orange CountyActive, not recruitingNeuronal Ceroid-Lipofuscinoses | Neuronal Ceroid Lipofuscinosis CLN2 | Spinocerebellar Ataxia, Autosomal Recessive 7United States
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Emily de los ReyesRecruitingBatten Disease | CLN6United States
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Eunice Kennedy Shriver National Institute of Child...RecruitingNiemann-Pick Disease Type C1 | Juvenile Neuronal Ceroid Lipofuscinosis | Smith-Lemli-Opitz Syndrome | Creatine Transporter DeficiencyUnited States
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Beyond Batten Disease FoundationTheranexusActive, not recruitingBatten DiseaseUnited States
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Amicus TherapeuticsActive, not recruiting
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Amicus TherapeuticsActive, not recruitingBatten Disease | CLN6United States
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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National Human Genome Research Institute (NHGRI)RecruitingDiabetes | Undiagnosed Diseases | Inherited Metabolic Disorders | Batten's Disease | Tay SachsUnited States
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University of Massachusetts, WorcesterCompleted
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Henry Ford Health SystemCompletedTo Assess the Changes in Markers of Bone Turnover Over a Six Month Period After Epidural Steroid Inject | To Assess the Changes in Bone Mineral DensityUnited States
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Augusta UniversityRecruitingSpinal Cord Stimulator Trial Period, Neuromodulation Trial Period, SCS Trial PeriodUnited States
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Northwell HealthCompletedImaging of the Brain and Antipsychotics | Neuronal Network ChangesUnited States
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Northwestern UniversityAmerican Society for Surgery of the HandEnrolling by invitationNeuroma Amputation | Neuroma | Neuroma of Upper Limb | Neuroma of Lower LimbUnited States
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University of PennsylvaniaActive, not recruiting
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University of California, DavisCompletedEndarterectomy, CarotidUnited States
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University of LouisvilleWithdrawn
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Washington University School of MedicineSociety of Family PlanningCompletedPostpartum PeriodUnited States
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Washington University School of MedicineTerminatedCarotid EndarterectomyUnited States
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Thomas Jefferson UniversityCompletedAnesthesia | Preoperative PeriodUnited States
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Baylor Research InstituteAdmedus Regen Pty Ltd.Completed
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Woebot HealthScripps Translational Science InstituteTerminated
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Arizona Heart InstituteVolcano CorporationCompletedCarotid Artery DiseaseUnited States
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Baylor College of MedicineCompletedCarotid Artery Occlusive DiseaseUnited States
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Washington University School of MedicineNational Heart, Lung, and Blood Institute (NHLBI); Cedars-Sinai Medical Center and other collaboratorsRecruitingCarotid Atherosclerosis | Asymptomatic Carotid Artery Stenosis | Carotid Artery AtheromaUnited States
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Lahey ClinicAmerican Association of Neurological SurgeonsWithdrawn
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United States Naval Medical Center, PortsmouthUnknownContraception | Postpartum PeriodUnited States
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Mayo ClinicCompletedCarotid Artery Intima Media ThicknessUnited States