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Clinical Trials on Niemann-Pick Disease, Type C
Total 56840 results
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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Eline C. B. EskesRecruiting
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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Children's Hospital Los AngelesCompletedGranuloma | Anemia | Thrombocytopenia | Neutropenia | Sickle Cell Disease | Thalassemia | Niemann-Pick Disease | Wiskott-Aldrich Syndrome | Osteopetrosis | Fucosidosis | Chediak Higashi Syndrome | Hurler DiseaseUnited States
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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Novartis PharmaceuticalsTerminatedc-MET Inhibitor; PI3K Inhibitor, PTEN Mutations, Homozygous Del. of PTEN or PTEN Neg. by IHC, c-Met Ampli. by FISH, INC280, BKM120, Buparlisib; Recurrent GBMSpain, Switzerland, Germany, United States, Netherlands
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Meshalkin Research Institute of Pathology of CirculationUnknownAorta-iliac Segment Lesion (C,D Type by TASC II)Russian Federation
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University of British ColumbiaCanadian Institutes of Health Research (CIHR)CompletedMeningococcal Sero-type C InfectionCanada
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IRCCS Sacro Cuore Don Calabria di NegrarRecruitingTick-Borne DiseasesItaly
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National Institute of Allergy and Infectious Diseases...WithdrawnLyme Disease | Tick-Borne DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...National Institutes of Health (NIH)TerminatedTick-Borne Disease | Encephalitis, Tick-Borne | Tick-Borne Encephalitis | Glycoprotein E, Flavivirus | NSI Protein, FlavivirusUnited States
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University Hospital, Strasbourg, FranceUnknown
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Hadassah Medical OrganizationXTL BiopharmaceuticalsWithdrawnChronic Hepatitis C Virus InfectionIsrael
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Hadassah Medical OrganizationUnknownChronic Hepatitis C Virus InfectionIsrael
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PharmaEssentiaCompletedChronic Hepatitis C Virus InfectionKorea, Republic of, Taiwan, China
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National Institute of Allergy and Infectious Diseases...RecruitingLyme Disease | Tick-borne Diseases | Tick ResistanceUnited States
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Beni-Suef UniversityCompletedChronic Hepatitis C Virus InfectionEgypt
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Humanity and Health Research CentreBeijing 302 HospitalCompletedChronic Hepatitis C InfectionChina
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Trek Therapeutics, PBCCompletedChronic Hepatitis C | Hepatitis C Genotype 1 | Hepatitis C (HCV) | Hepatitis C Viral InfectionUnited States, New Zealand
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Trek Therapeutics, PBCCompletedChronic Hepatitis C | Hepatitis C (HCV) | Hepatitis C Genotype 4 | Hepatitis C Viral InfectionUnited States
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Tripep ABInovio PharmaceuticalsUnknownChronic Hepatitis C Virus InfectionSweden
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University of North Carolina, Chapel HillNational Institute for Occupational Safety and Health (NIOSH/CDC); East Carolina... and other collaboratorsCompletedTick Bites | Tick-borne DiseasesUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Recruiting
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Sinaloa Pediatric HospitalCompleted
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Göteborg UniversityVastra Gotaland Region; Sahlgrenska University Hospital, SwedenUnknownTick-Borne Diseases | Encephalitis, Tick-Borne | Tick Bites | Tick-Bite; Fever | Tick FeverSweden
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AbbVieCompletedChronic Hepatitis C | Hepatitis C (HCV) | Hepatitis C Genotype 1a
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AbbVie (prior sponsor, Abbott)CompletedChronic Hepatitis C | Hepatitis C Genotype 1 | Hepatitis C (HCV)United States, Australia, Canada, France, Germany, New Zealand, Puerto Rico, Spain, United Kingdom
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Sunshine Lake Pharma Co., Ltd.CompletedChronic Hepatitis cChina
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Alios Biopharma Inc.Janssen PharmaceuticaTerminatedChronic Hepatitits CGeorgia, Moldova, Republic of, France
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AbbVieCompletedChronic Hepatitis C | Hepatitis C (HCV) | Hepatitis C Genotype 1a
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Sunshine Lake Pharma Co., Ltd.CompletedChronic Hepatitis cChina
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Hospices Civils de LyonCompleted
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University Health Network, TorontoCompletedChronic Hepatitis C InfectionCanada
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AbbVie (prior sponsor, Abbott)CompletedHepatitis C | Chronic Hepatitis C Infection | HCV | Hepatitis C Genotype 1United States, Puerto Rico
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University Medical Centre LjubljanaUniversity of Ljubljana School of Medicine, SloveniaRecruiting
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University of SurreyCompletedTick-Borne EncephalitisUnited Kingdom
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Elisabethinen HospitalBaxter Healthcare Corporation; ASOKLIFUnknownTick Borne EncephalitisAustria, Czech Republic
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Humanity and Health Research CentreEmory University; Beijing 302 HospitalCompleted
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Merck Sharp & Dohme LLCCompleted
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Sunshine Lake Pharma Co., Ltd.CompletedChronic Hepatitis cChina
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Ascletis Pharmaceuticals Co., Ltd.CompletedChronic Hepatitis cChina
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AbbVieCompletedChronic Hepatitis C | Hepatitis C Virus | Genotype 3 Hepatitis C Virus
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AbbVie (prior sponsor, Abbott)CompletedHepatitis C | Hepatitis C Virus | Chronic Hepatitis C InfectionUnited States
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University Health Network, TorontoCompletedChronic Hepatitis C Virus InfectionCanada