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Clinical Trials on Non Dystrophic Myotonia in United States
Total 8663 results
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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Ohio State UniversityGilead SciencesCompletedMyotonic Dystrophy 1 | Myotonia Congenita | Paramyotonia CongenitaUnited States
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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Richard Barohn, MDCompletedNon-Dystrophic Myotonia | MyotoniaUnited States, Canada, Italy, United Kingdom
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National Institute of Neurological Disorders and...TerminatedMyotonic Dystrophy Type-1 | Myotonic Dystrophy Type-2United States
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University College, LondonRecruitingNon-Dystrophic MyotoniaUnited Kingdom
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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Virginia Commonwealth UniversityRecruitingCongenital Myotonic Dystrophy | Childhood Myotonic Dystrophy | CDM | CHDMUnited States, Italy
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Stanford UniversityUnknownMyotonic Dystrophy Type 1United States
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University of RochesterCompletedMyotonic DystrophyUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed IncorporatedCompleted
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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Massachusetts General HospitalRecruiting
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
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Massachusetts General HospitalUniversity of Pittsburgh; Boston Children's Hospital; Brigham and Women's Hospital and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Myotonic Dystrophy | Facioscapulohumeral Muscular DystrophyUnited States
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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Wake Forest University Health SciencesRecruitingMyotonic Dystrophy Type 2United States
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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AMO Pharma LimitedCompletedMyotonic Dystrophy 1United Kingdom
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedMyotonic Dystrophy Type 1United Kingdom
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Insmed IncorporatedMuscular Dystrophy AssociationCompleted
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of... and other collaboratorsCompletedMyotonic Dystrophy Type 1Netherlands, France, Germany, United Kingdom
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Indiana University School of MedicineMuscular Dystrophy AssociationCompletedMuscular Dystrophy | Arrhythmia | Sudden Cardiac DeathUnited States
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Massachusetts General HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital; University...Recruiting
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Newcastle UniversityRecruiting
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Lupin Ltd.Active, not recruitingMyotonic DystrophyFrance, Germany, United Kingdom
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aTyr Pharma, Inc.CompletedLimb-Girdle Muscular Dystrophies | Facioscapulohumeral Muscular DystrophyUnited States, Denmark, France
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University of North Carolina, Chapel HillNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb-Girdle Muscular DystrophyUnited States
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Wake Forest University Health SciencesMuscular Dystrophy AssociationCompletedMuscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)United States
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Boston Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingLimb-girdle Muscular Dystrophy | Neuromuscular; Disorder, Hereditary | Duchenne/Becker Muscular DystrophyUnited States
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Northwestern UniversityCompletedBecker Muscular Dystrophy | Limb-girdle Muscular DystrophyUnited States
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Duke UniversityRecruitingRetinal DystrophiesUnited States
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Castle Creek Biosciences, LLC.TerminatedEpidermolysis Bullosa Dystrophica, RecessiveUnited States
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Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationHypertrophic Cardiomyopathy (HCM) | Long QT Syndrome (LQTS) | Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT) | Inherited Cardiac Arrythmias | Brugada Syndrome (BrS) | Early Repolarization Syndrome (ERS) | Arrhythmogenic Cardiomyopathy (AC, ARVD/C) | Dilated Cardiomyopathy (DCM) | Muscular... and other conditionsUnited States
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)CompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States
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Retrotope, Inc.Active, not recruitingInfantile Neuroaxonal DystrophyUnited States
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Retrotope, Inc.CompletedInfantile Neuroaxonal Dystrophy | INADUnited States
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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State University of New York at BuffaloActive, not recruitingFuchs DystrophyUnited States
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Linda Pax LowesRecruitingLimb-Girdle Muscular Dystrophy Type 2A | Limb-Girdle Muscular Dystrophy, Type 2EUnited States
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedLimb-Girdle Muscular DystrophyUnited States