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Clinical Trials on Nonsene Mutation Duchenne Muscular Dystrophy
Total 856 results
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
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Children's Hospital of Eastern OntarioJesse's Journey-The Foundation for Gene and Cell TherapyCompletedDuchenne Muscular DystrophyCanada
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Monica Levy AndersenCompletedOther Diseases or ConditionsBrazil
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PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Sahra ŞirvanEnrolling by invitationDuchenne Muscular DystrophyTurkey
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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University Hospital, ToulouseUnknownDuchenne Muscular DystrophyFrance
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Hacettepe UniversityCompletedDuchenne Muscular DystrophyTurkey
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Oslo University HospitalUniversity Hospital of North Norway; The Research Council of NorwayCompletedDuchenne Muscular DystrophyNorway
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Muscle Strength | Hamstring Contractures | Lower ExtremityTurkey
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Hacettepe UniversityCompletedGait Disorders, Neurologic | Body Posture | Balance | Foot PostureTurkey
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PTC TherapeuticsEnrolling by invitationDuchenne Muscular DystrophyUnited States, Canada
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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Suzuka HospitalNagoya UniversityUnknownCardiomyopathies | Duchenne Muscular DystrophyJapan
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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Istituto Auxologico ItalianoCompletedOsteoporosis | Duchenne Muscular Dystrophy
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisCompletedHeart Failure | Duchenne Muscular Dystrophy | CardiomyopathyFrance
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Wyeth is now a wholly owned subsidiary of PfizerCompletedBecker Muscular Dystrophy | Facioscapulohumeral Muscular Dystrophy | Limb-Girdle Muscular DystrophyUnited States
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Capricor Inc.CompletedDuchenne Muscular Dystrophy | CardiomyopathyUnited States
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Subha RamanBallou SkiesCompletedDuchenne Muscular DystrophyUnited States
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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IRCCS Eugenio MedeaRecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Limb Girdle Muscular Dystrophy | Facio-Scapulo-Humeral DystrophyItaly
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Gokce Yagmur Gunes GencerHacettepe UniversityCompletedMuscular Dystrophy, Duchenne | Upper Extremity | Respiratory FunctionsTurkey
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Peking Union Medical College HospitalNational Natural Science Foundation of China; Cancer Institute and Hospital...Recruiting
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Ambulation Disorder, NeurologicTurkey
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Gait Disorders, Neurologic | Gait Disorders in ChildrenTurkey
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedDuchenne Muscular DystrophyUnited Kingdom
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Jett Foundation, Inc.Pfizer; Hoffmann-La Roche; Italfarmaco; Nationwide Children's Hospital; Capricor... and other collaboratorsCompletedDuchenne Muscular Dystrophy | Rare Diseases | Disability Physical | Burden, Dependency | Impairment | Disease ManagementUnited States
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Virginia Commonwealth UniversityEdgewise Therapeutics, Inc.RecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Muscular Dystrophy in Children | Muscular Dystrophy, BeckerUnited States, New Zealand, United Kingdom
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University of PittsburghRespirtech, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Laurent ServaisSYSNAVRecruitingDuchenne Muscular Dystrophy | Myotonic Dystrophy 1 | Congenital Muscular Dystrophy | Centronuclear Myopathy | Charcot-Marie-Tooth | Fascioscapulohumeral Muscular DystrophyBelgium
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University Hospital, Basel, SwitzerlandCompletedBecker's Muscular Dystrophy (BMD)Switzerland
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Hacettepe UniversitySuleyman Demirel UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Posture Disorders in Children | Ambulation Disorder, NeurologicTurkey
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Politecnico di MilanoIRCCS Eugenio Medea; Villa Beretta Rehabilitation CenterCompletedMuscular Dystrophies | Muscular Dystrophy, Duchenne | Muscular Dystrophy, Becker | Muscular Dystrophy, Limb-Girdle Type 2Italy
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Rigshospitalet, DenmarkCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy Type 2IDenmark
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Seoul National University HospitalRecruitingDuchenne Muscular Dystrophy | Scoliosis Neuromuscular | Lordosis LumbarKorea, Republic of
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Northwestern UniversityCompletedBecker Muscular Dystrophy | Limb-girdle Muscular DystrophyUnited States
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ItalfarmacoCompletedBecker Muscular DystrophyNetherlands, Italy
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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Cedars-Sinai Medical CenterCompleted
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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Sardocor Corp.Not yet recruitingDMD-Associated Dilated Cardiomyopathy
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Edgewise Therapeutics, Inc.Medpace, Inc.Enrolling by invitationBecker Muscular DystrophyUnited States, Netherlands, United Kingdom
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Cedars-Sinai Medical CenterCompletedBecker Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterTerminatedMuscular DystrophyUnited States
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Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
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National Human Genome Research Institute (NHGRI)Completed