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Clinical Trials on Persistent Developmental Stutter in New Zealand
Total 505 results
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Boston Children's HospitalPhelan-McDermid Syndrome FoundationCompletedIntellectual Disability | Autism Spectrum Disorder | Phelan-McDermid SyndromeUnited States
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Novo Nordisk A/SCompletedGrowth Hormone Deficiency in Children | Growth DisorderUnited States, United Kingdom
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Maria I. NewNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD)Completed21-hydroxylase DeficiencyUnited States, Brazil
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Novartis PharmaceuticalsActive, not recruitingTuberous Sclerosis ComplexUnited States, Spain, Belgium, Taiwan, Turkey, Australia, Korea, Republic of, Thailand, France, Hungary, United Kingdom, Italy, Japan, Canada, Russian Federation, Poland, Mexico, Colombia
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Novo Nordisk A/SCompletedGrowth Hormone Disorder | Growth Hormone Deficiency in ChildrenUnited States
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Marinus PharmaceuticalsActive, not recruitingTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, Israel, Italy, Germany, France, Canada
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Novo Nordisk A/SActive, not recruitingGrowth Hormone Deficiency in ChildrenUnited States, Korea, Republic of, United Kingdom, Canada, Russian Federation, India, Spain, Italy, Algeria, Austria, France, Ireland, Israel, Japan, Latvia, Poland, Serbia, Thailand, Ukraine, Germany, Slovenia, Switzerland
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Rutgers UniversityUnknownAlzheimer Disease | Parkinson | Dementia, Alzheimer Type | Dementia With Lewy Bodies | Asperger Syndrome | Autistic Disorders Spectrum | Adhd | Lewy Body Dementia With Behavioral Disturbance (Disorder) | Dementia Frontal | Tremor EssentialUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIUnited States, Canada
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Jazz PharmaceuticalsCompletedSeizures | Tuberous Sclerosis ComplexUnited States, Spain, Australia, Poland, United Kingdom, Netherlands
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Novartis PharmaceuticalsCompletedTuberous Sclerosis Complex-associated Refractory SeizuresUnited States, Colombia, Belgium, France, Japan, Taiwan, Turkey, Spain, Thailand, Korea, Republic of, Australia, Hungary, United Kingdom, Canada, Norway, Germany, Italy, Russian Federation, Denmark, Argentina, Netherlands, Greece, P... and more
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HedgePath Pharmaceuticals, Inc.CompletedBasal Cell Carcinoma in Basal Cell Nevus SyndromeUnited States
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DePuy OrthopaedicsRecruitingOsteoarthritis | Rheumatoid Arthritis | Congenital Hip Dysplasia | Traumatic Arthritis | Avascular Necrosis of the Femoral Head | Acute Traumatic Fracture of the Femoral Head or Neck | Certain Cases of Ankylosis | Non-union of Femoral Neck Fractures | Certain High Sub-Capital & Femoral Neck Fractures...United States
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AstraZenecaCompletedPuberty, Precocious | McCune-Albright SyndromeItaly, United States, Germany, France, Russian Federation, United Kingdom
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States, Brazil, France
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Sol-Gel Technologies, Ltd.Premier Research Group plcRecruitingGorlin SyndromeUnited States
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Ultragenyx Pharmaceutical IncMereo BioPharmaCompletedOsteogenesis Imperfecta Type III | Osteogenesis Imperfecta Type IV | Osteogenesis Imperfecta, Type IUnited States, Canada, Denmark, France, United Kingdom
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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Marinus PharmaceuticalsEnrolling by invitationTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, China, Italy, France, Israel, Germany, Canada, Australia
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National Tuberous Sclerosis AssociationRecruitingTuberous Sclerosis | LymphangioleiomyomatosisUnited States, Canada
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Longboard PharmaceuticalsActive, not recruitingDravet Syndrome | Lennox-Gastaut Syndrome | Developmental and Epileptic EncephalopathyUnited States, Australia
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Novo Nordisk A/SCompletedGrowth Hormone Disorder | Adult Growth Hormone DeficiencyUnited States, Poland, India, Japan, Russian Federation, United Kingdom, Germany, Sweden, Israel, Malaysia, Turkey, South Africa, Australia, Latvia, Lithuania, Romania, Brazil, Norway, Ukraine
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Novo Nordisk A/SCompletedGrowth Hormone Disorder | Pituitary DwarfismUnited States
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Longboard PharmaceuticalsCompletedDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathyUnited States, Australia
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States
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CHU de Quebec-Universite LavalCanadian Institutes of Health Research (CIHR); Laval UniversityActive, not recruitingChild Development | Bronchopulmonary Dysplasia | Neonatal and Perinatal ConditionsCanada
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AEterna ZentarisNovo Nordisk A/SActive, not recruitingGrowth Hormone DeficiencyUnited States, Italy, Turkey, Georgia, Romania, Poland, Armenia, Germany, Serbia, Slovakia, Slovenia
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Teva Branded Pharmaceutical Products R&D, Inc.TerminatedGrowth Hormone DeficiencyUnited States, Austria, Czechia, Greece, Hungary, Italy, Slovakia, Spain
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Novartis PharmaceuticalsCompletedTuberous Sclerosis | Subependymal Giant Cell AstrocytomaUnited States, Belgium, Canada, Germany, Italy, Russian Federation, Netherlands, Poland, Australia, United Kingdom
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingTurner SyndromeUnited States
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingEndocrine System Diseases | Adult Growth Hormone Deficiency | Hormone DeficiencyUnited States, Armenia, Georgia, Greece, Ukraine, Australia, Canada, France, Israel, Italy, Japan, Malaysia, Poland, Romania, Serbia, Slovakia, Spain, Turkey, United Kingdom, Germany, Korea, Republic of
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Progenity, Inc.CompletedDown Syndrome | Aneuploidy | DiGeorge Syndrome | Turner Syndrome | Klinefelter Syndrome | Chromosome Deletion | Edwards Syndrome | Patau SyndromeUnited States
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Merck Sharp & Dohme LLCActive, not recruitingPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)United States, Australia, Brazil, Italy, United Kingdom
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PellePharm, Inc.CompletedBasal Cell Nevus SyndromeUnited States, Spain, Germany, United Kingdom, Italy, France, Belgium, Canada, Denmark, Netherlands
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); FDA Office of Orphan Products... and other collaboratorsCompletedMarfan SyndromeUnited States, Canada, Belgium
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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Sol-Gel Technologies, Ltd.TerminatedBasal Cell Nevus SyndromeUnited States, France, Belgium, Denmark, Germany, Italy, Netherlands, Spain, United Kingdom
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Clementia Pharmaceuticals Inc.TerminatedExostoses, Multiple HereditaryUnited States, Spain, Canada, Japan, Italy, Portugal, United Kingdom, Turkey, Australia, Belgium, France, Netherlands
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Mount Sinai Hospital, CanadaCanadian Institutes of Health Research (CIHR); Sunnybrook Research InstituteRecruitingDiabetes Mellitus, Type 2 | Child Development | Child Obesity | Pregnancy in DiabeticCanada, Australia
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMedulloblastoma | Nevoid Basal Cell Carcinoma Syndrome | Desmoplastic/Nodular Medulloblastoma | Medulloblastoma With Extensive NodularityUnited States, Canada, Puerto Rico, Australia
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Edgar JaeggiLabatt Family Heart CentreRecruitingAtrial Flutter | Tachycardia, Supraventricular | Tachycardia, Atrioventricular Nodal Reentry | Tachycardia Atrial | Tachycardia, Reciprocating | Tachycardia, Paroxysmal | Fetal Hydrops | Tachycardia, Atrial EctopicUnited States, Hong Kong, Canada, Netherlands, Sweden, Australia, Brazil, Finland, France, Russian Federation, Spain, Czechia, Switzerland, United Kingdom
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Palvella Therapeutics, Inc.RecruitingBCCs in Gorlin Syndrome PatientsUnited States, United Kingdom
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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McMaster UniversityHarvard Medical School (HMS and HSDM); The Hospital for Sick Children; Canadian... and other collaboratorsTerminatedEpilepsy | Cerebral Palsy | Autism Spectrum Disorder | Spina Bifida | Fetal Alcohol Spectrum DisordersCanada
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Novo Nordisk A/SRecruitingSGA, Turner Syndrome, Noonan Syndrome, ISSKorea, Republic of, United States, Ireland, United Kingdom, Finland, France, Netherlands, Japan, Thailand, Belgium, China, Israel, Brazil, India, Portugal, Austria, Bulgaria, Canada, Croatia, Germany, Greece, Malaysia, Poland, Saudi Arabia and more
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Johnson & Johnson Pharmaceutical Research & Development...CompletedSchizophrenia | Bipolar Disorder | Autistic Disorder | Conduct and Other Disruptive Behavior DisordersUnited States, Belgium, Germany, Poland, Greece, Netherlands
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Bellicum PharmaceuticalsActive, not recruitingStudy of Gene Modified Donor T-cells Following TCR Alpha Beta Positive Depleted Stem Cell TransplantLymphoma, Non-Hodgkin | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Anemia, Aplastic | Primary Immune Deficiency Disorder | Cytopenia | Osteopetrosis | Leukemia, Acute Myeloid (AML), Child | Hemoglobinopathy in ChildrenUnited States
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Spruce BiosciencesRecruitingCongenital Adrenal Hyperplasia | 21-OHDUnited States
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Hoffmann-La RocheCompletedBasal Cell CarcinomaUnited States, Spain, France, Germany, Netherlands, Russian Federation, Italy, Mexico, Austria, Canada
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Ottawa Hospital Research InstituteEnrolling by invitationDeath | Asthma | Autism Spectrum Disorder | Pre-Eclampsia | Executive Dysfunction | Emotional Problem | Behavioural ProblemAustralia, United Kingdom, Canada, Jamaica