- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Pitt Hopkins Syndrome in United States
Total 14222 results
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Washington University School of MedicineCompletedMyelodysplastic SyndromesUnited States
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Jonsson Comprehensive Cancer CenterNational Cancer Institute (NCI)UnknownMyelodysplastic SyndromesUnited States
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Duke UniversityCelgene CorporationCompletedMyelodysplastic SyndromesUnited States
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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Memorial Sloan Kettering Cancer CenterCompletedAcute Myeloid Leukemia | Advanced Myelodysplastic SyndromesUnited States
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National Institute of Arthritis and Musculoskeletal...Completed
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...CompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Hemophagocytic Lymphohistiocytosis (HLH) | Non Hodgkins Lymphoma | Familial Hemophagocytic Lymphohistiocytosis (FLH) | Viral-associated Hemophagocytic Syndrome (VAHS) | X-linked Lymphoproliferative...United States
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TelikTerminatedMyelodysplastic Syndrome (MDS)United States
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Bausch & Lomb IncorporatedCompletedDry Eye SyndromeUnited States
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H. Lee Moffitt Cancer Center and Research InstituteCelgene CorporationCompletedMyelodysplastic Syndrome | MDSUnited States
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St. Louis UniversityEpharmix, Inc.TerminatedShort Bowel SyndromeUnited States
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Cedars-Sinai Medical CenterAbbottCompletedMyelodysplastic Syndromes | LeukemiaUnited States
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Duke UniversityAgency for Healthcare Research and Quality (AHRQ)CompletedAcute Coronary SyndromesUnited States
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Cook Children's Health Care SystemEncoded TherapeuticsRecruiting
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9 Meters Biopharma, Inc.Unknown
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Catalyst Pharmaceuticals, Inc.No longer availableLambert-Eaton Myasthenic Syndrome | Congenital Myasthenic Syndrome | Nystagmus, AcquiredUnited States
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NYU Langone HealthPerlmutter Cancer CenterCompletedMyelodysplastic SyndromesUnited States
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Kura Oncology, Inc.Terminated
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University of RochesterTerminatedHealthy | Dry Eye SyndromeUnited States
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AllerganCompleted
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Duke UniversityGenzyme, a Sanofi CompanyCompletedMultiple Myeloma | Non-Hodgkins Lymphoma | Hodgkins DiseaseUnited States
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Stanford UniversityNot yet recruitingPTEN Gene Mutation | PTEN Hamartoma Tumor Syndrome | PTEN Hamartoma SyndromeUnited States
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Jonsson Comprehensive Cancer CenterCelgene Corporation; CTI BioPharmaTerminatedMyelodysplastic Syndromes | LeukemiaUnited States
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University of California, Los AngelesAvailableDravet SyndromeUnited States
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Arkansas Children's Hospital Research InstituteBaylor College of Medicine; USDA Grand Forks Human Nutrition Research CenterWithdrawn
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University of NebraskaAstex Pharmaceuticals, Inc.CompletedMyelodysplastic Syndromes | Multiple Myeloma | Chronic Lymphocytic Leukemia | Peripheral T-cell Lymphoma | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Non-Hodgkins Lymphoma | Hodgkins DiseaseUnited States
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Zogenix International Limited, Inc., a subsidiary...CompletedDravet Syndrome | Lennox Gastaut SyndromeUnited States
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H. Lee Moffitt Cancer Center and Research InstituteNovartis PharmaceuticalsRecruitingMyelodysplastic SyndromesUnited States
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National Heart, Lung, and Blood Institute (NHLBI)WithdrawnMyelodysplastic SyndromesUnited States
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Onconova Therapeutics, Inc.CompletedMyelodysplastic SyndromeUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoThrasher Research FundUnknownWest SyndromeUnited States
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Abramson Cancer Center of the University of PennsylvaniaChildren's Hospital of PhiladelphiaRecruiting
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The University of Texas Health Science Center,...Terminated
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Cedars-Sinai Medical CenterNovartisWithdrawn
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John Carroll UniversityUniversity Hospital Southampton NHS Foundation TrustActive, not recruitingPTEN Hamartoma Tumor SyndromeUnited States, United Kingdom
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ShireRecruitingShort Bowel Syndrome (SBS)United States
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Weill Medical College of Cornell UniversityJazz PharmaceuticalsCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, Acute | Leukemia, Relapsed Adult Acute Myeloid | Myelodysplastic Syndromes, Previously TreatedUnited States
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedMyelodysplastic Syndromes | LeukemiaUnited States
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BRIM Biotechnology Inc.Completed
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Emory UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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Washington University School of MedicineCompletedMyelodysplastic SyndromesUnited States
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National Cancer Institute (NCI)CompletedLymphoma, B-Cell | Leukemia, B-cell | Lymphoma, Hodgkins | Lymphoma, Non-hodgkinsUnited States
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Texas Oncology Cancer CenterTerminatedMultiple Myeloma | Chronic Lymphocytic Leukemia | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Aplastic Anemia | Non-Hodgkins Lymphoma | Hodgkins DiseaseUnited States
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Kailea ManningEdward Via Virginia College of Osteopathic MedicineNot yet recruitingMyofascial Pain SyndromeUnited States
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University of NebraskaNational Cancer Institute (NCI)TerminatedMyelodysplastic SyndromesUnited States
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Boston Children's HospitalAlcresta Therapeutics, Inc.Enrolling by invitationMalabsorption | Short Bowel SyndromeUnited States
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Ehab L AtallahCompleted
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NYU Langone HealthCompletedInterstitial Cystitis Bladder Pain SyndromesUnited States
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Mayo ClinicElgene ChemicalCompletedComplex Regional Pain Syndrome, Type 1United States
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University of FloridaCompleted