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Clinical Trials on Pompe's Disease Juvenile Onset
Total 1329 results
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UCB BIOSCIENCES GmbHPRA Health SciencesCompletedPolyarticular-course Juvenile Idiopathic Arthritis (JIA)United States, Argentina, Brazil, Canada, Chile, Mexico, Russian Federation
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Neurocrine BiosciencesTerminatedFocal Onset Seizure | Focal Onset EpilepsySpain, Australia, Belgium, Czechia, France, Hungary, Italy
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Mindful Diagnostics and Therapeutics, LLCCompleted
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Emalex Biosciences Inc.Premier Research Group plc; University of California, RiversideCompletedChildhood-Onset Fluency Disorder (Stuttering)United States
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PfizerActive, not recruitingPolyarticular Juvenile Idiopathic Arthritis | Psoriatic Arthritis, JuvenileKorea, Republic of
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Ohio State UniversityCompletedAlzheimer Disease, Late OnsetUnited States
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NeuroEM Therapeutics, Inc.University of South Florida Health / Byrd Alzheimer's InstituteUnknownAlzheimer Disease | Alzheimer Disease, Late OnsetUnited States
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Universitaire Ziekenhuizen KU LeuvenUnknownAlzheimer Disease, Late OnsetBelgium
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National Institute of Mental Health (NIMH)TerminatedPediatric Acute-onset Neuropsychiatric Syndrome (PANS)United States
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Centocor, Inc.CompletedRheumatoid Arthritis, Juvenile
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Novartis PharmaceuticalsCompletedSystemic Juvenile Idiopathic ArthritisJapan
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Kasr El Aini HospitalActive, not recruiting
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Genzyme, a Sanofi CompanyActive, not recruiting
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Centre Hospitalier de CayenneCompleted
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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Duke UniversityGenzyme, a Sanofi CompanyCompletedNeuropathy | Myopathy | Glycogen Storage Disease Type II (Late-onset Pompe Disease)United States
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Eric B. SuhlerGenentech, Inc.TerminatedJuvenile Idiopathic Arthritis Associated UveitisUnited States
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Neurocrine BiosciencesCompletedFocal Onset Seizure | Focal Onset EpilepsySpain, Belgium, Czechia, France, Italy, Australia, Hungary, United Kingdom
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Mindful Diagnostics and Therapeutics, LLCInfectious Disease Society of AmericaNot yet recruiting
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Eli Lilly and CompanyRecruitingSystemic Juvenile Idiopathic ArthritisBelgium, Spain, India, Italy, Czechia, Japan, Austria, France, United Kingdom, Brazil, Mexico, Israel, Poland, Argentina, Denmark, Turkey
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Children's Hospital Los AngelesCompletedAdolescent Juvenile Idiopathic Arthritis | Yoga TherapyUnited States
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University Hospital, Gentofte, CopenhagenCompletedMaturity-Onset Diabetes of the Young, Type 3Denmark
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Novartis PharmaceuticalsPediatric Rheumatology International Trials OrganizationCompletedSystemic Juvenile Idiopathic ArthritisItaly, United States, Belgium, Germany, Greece, Russian Federation, Turkey, Spain, France, Israel, Canada, Hungary, Switzerland, United Kingdom, Brazil, Austria, Sweden, Netherlands, Argentina, Peru, Poland
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Rigshospitalet, DenmarkDanish Research Center for Magnetic ResonanceRecruitingGlycogen Storage Disease | Pompe Disease (Late-onset) | McArdle DiseaseDenmark
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Taichung Veterans General HospitalNational Health Research Institutes, TaiwanRecruitingDiabetes Complications | Type 2 Diabetes | Maturity-Onset Diabetes of the Young (MODY)Taiwan
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Spark TherapeuticsActive, not recruitingLysosomal Storage Diseases | Glycogen Storage Disease Type II | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Canada, Netherlands, France, Denmark, Germany, Italy, United Kingdom
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Weill Medical College of Cornell UniversityWithdrawnAlzheimer Disease | Alzheimer Disease, Late Onset | Memory Loss | Patient Education as TopicUnited States
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Spark TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Italy, United Kingdom, Netherlands, France, Germany
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Qassim UniversityCairo University; Prince Sattam Bin Abdulaziz UniversityCompletedQuality of Life | Cardiorespiratory Fitness | Juvenile ArthritisSaudi Arabia
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Istanbul University - Cerrahpasa (IUC)RecruitingJuvenile Idiopathic ArthritisTurkey
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Nourhan ElsherifRecruiting
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Centre Hospitalier Universitaire de BesanconRecruiting
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Assiut UniversityNot yet recruitingJuvenile Idiopathic Arthritis
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University of British ColumbiaCanadian Institutes of Health Research (CIHR); The Arthritis Society, CanadaRecruitingJuvenile Idiopathic ArthritisCanada
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Guangzhou Women and Children's Medical CenterRecruitingJuvenile Idiopathic ArthritisChina
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Oslo University HospitalUniversity Hospital of North Norway; The Research Council of Norway; Helse Stavanger... and other collaboratorsActive, not recruitingJuvenile Idiopathic ArthritisNorway
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SanofiRegeneron PharmaceuticalsCompletedJuvenile Idiopathic ArthritisUnited States, Argentina, Canada, Chile, Czechia, Finland, France, Germany, Italy, Mexico, Netherlands, Poland, Russian Federation, Spain, United Kingdom
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Cairo UniversityCompletedJuvenile Idiopathic ArthritisSaudi Arabia
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Centre Hospitalier Universitaire, AmiensCompletedJuvenile Idiopathic ArthritisFrance
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Cairo UniversityCompletedJuvenile Idiopathic ArthritisSaudi Arabia
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Assistance Publique - Hôpitaux de ParisActive, not recruitingJuvenile Idiopathic ArthritisFrance
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University of WashingtonNational Institute of Nursing Research (NINR)CompletedJuvenile Idiopathic ArthritisUnited States
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The Hospital for Sick ChildrenDalhousie University; IWK Health Centre; Provincial Health Services Authority; The... and other collaboratorsCompletedJuvenile Idiopathic ArthritisCanada
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PfizerCompletedJuvenile Idiopathic ArthritisUnited States, Spain, Turkey, Canada, Australia, Israel, United Kingdom, Argentina, Brazil, Poland, Mexico, Belgium, Russian Federation, Ukraine
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Assiut UniversityUnknownJuvenile Idiopathic Arthritis
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Sheffield Children's NHS Foundation TrustSheffield Teaching Hospitals NHS Foundation TrustCompleted
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Benha UniversityCompleted
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Centre Hospitalier Universitaire de BesanconUnknownJuvenile Idiopathic ArthritisFrance
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AbbVieCompletedArthritis, Juvenile Rheumatoid
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University Hospital, MontpellierResearch department, unknowns, Strategic & innovation consulting, Paris (anthropologists) and other collaboratorsCompletedJuvenile Idiopathic ArthritisFrance