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Clinical Trials on Pompe Disease Infantile-Onset
Total 905 results
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Amicus TherapeuticsCompletedVariant Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Zagazig UniversityActive, not recruiting
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Eisai Inc.CompletedPartial Onset EpilepsyUnited Kingdom
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Eisai Inc.CompletedPartial Onset EpilepsyUnited Kingdom
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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United Arab Emirates UniversityNot yet recruitingMaturity-onset Diabetes of the Young | MODY | Monogenic Diabetes
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Eisai Inc.CompletedPartial Onset SeizuresGermany, Sweden, Norway, Austria, Denmark
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PiLeJeClinact; ClinfileTerminatedNosocomial Infection | Diarrhea, InfantileFrance
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University of IowaAfrican Population and Health Research CenterCompletedWasting | Stunting | Diarrhea, Infantile | Exposure | Infection GastrointestinalKenya
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University of SevilleCompletedFamily | Infantile Hemiplegia | Constraint Induced Movement Therapy | Bimanual Intensive TherapySpain
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Equilibre Biopharmaceuticals B.V.Terminated
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University of MinhoHospital de Braga; Fundação para a Ciência e a Tecnologia; Centro Hospitalar...Active, not recruitingEating Behavior | Obesity Adult OnsetPortugal
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Eisai Co., Ltd.CompletedPartial Onset SeizuresJapan, Korea, Republic of
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Eisai Co., Ltd.CompletedPartial-onset SeizuresKorea, Republic of, Japan, Australia, China, Malaysia, Taiwan, Thailand
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Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedPartial Onset SeizuresKorea, Republic of, Taiwan, Lebanon, United States, Malaysia, China, Spain, Turkey, Israel, Russian Federation, France, Belarus, Bulgaria, Germany, Hungary, Philippines, Romania, Serbia, Ukraine, Greece, Bosnia and Herzegovina, Be... and more
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NovartisCompletedPartial Onset SeizuresUnited States, Italy, Germany, Taiwan, Hungary, Switzerland, Bulgaria, Korea, Republic of, Slovakia, Poland
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Eisai Inc.No longer availablePartial Onset SeizuresItaly, Spain, Belgium, Israel, Poland, Taiwan, Czechia, Finland, Thailand, Malaysia, Argentina, Chile, Canada, Hungary, Australia, Lithuania, Latvia, Estonia, Netherlands, Greece, Hong Kong
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky DiseaseUnited States, Italy, Germany, United Kingdom
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Xenon Pharmaceuticals Inc.Worldwide Clinical TrialsRecruitingFocal Onset SeizuresUnited States, Spain, Italy, Croatia, Portugal, Poland, Chile, Argentina, Austria, Czechia
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Xenon Pharmaceuticals Inc.Worldwide Clinical TrialsRecruitingFocal Onset SeizuresUnited States, Spain, Australia, Poland, Canada, Bulgaria, Italy, United Kingdom
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NobelpharmaCompleted
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NovartisWithdrawnPartial Onset SeizuresUnited States, Austria, Spain, Estonia, Bulgaria, Latvia, Canada, India, Belgium, Lithuania, Romania
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BioMarin PharmaceuticalActive, not recruitingLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2United States
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Eunice Kennedy Shriver National Institute of Child...CompletedInfantile Neronal Ceroid LipofuscinosisUnited States
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University of Colorado, DenverMassachusetts General Hospital; Beta Bionics, Inc.CompletedDiabetes Mellitus, Type 1 | Type 1 Diabetes | Diabetes type1 | Type 1 Diabetes Mellitus | Autoimmune Diabetes | Diabetes Mellitus, Insulin-Dependent | Juvenile-Onset Diabetes | Diabetes, Autoimmune | Insulin-Dependent Diabetes Mellitus 1 | Diabetes Mellitus, Insulin-Dependent, 1 | Diabetes Mellitus, Brittle | Diabetes Mellitus, Juvenile-Onset and other conditionsUnited States
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Seoul National University HospitalRecruitingNew Onset Diabetes After TransplantationKorea, Republic of
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Ain Shams UniversityCompletedLabor Onset and Length AbnormalitiesEgypt
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Dilafor ABCompletedLabor Onset and Length AbnormalitiesFinland, Sweden
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University of California, San FranciscoWithdrawnLabor Onset and Length AbnormalitiesUnited States
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH)CompletedBatten Disease | Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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IMMUNOe Research CentersOctapharmaUnknownPediatric Autoimmune Neuropsychiatric Disorders Associated With Streptococcal Infections | Pediatric Acute-Onset Neuropsychiatric SyndromeUnited States
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NICHD Neonatal Research NetworkEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedInfant, Newborn, Diseases | Early Onset Neonatal Sepsis | Early-Onset MeningitisUnited States
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University of California, Los AngelesNational Institute on Aging (NIA); University of Southern CaliforniaUnknownAlzheimer Disease | Corticobasal Degeneration | Primary Progressive Aphasia | Alzheimer Disease, Early Onset | Alzheimer Disease, Late Onset | Dementia, Alzheimer Type | Logopenic Progressive Aphasia | Visuospatial/Perceptual Abilities | Posterior Cortical Atrophy | Executive Dysfunction | Ideomotor ApraxiaUnited States
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Cognito Therapeutics, Inc.RecruitingCognitive Impairment | Dementia | Alzheimer Disease | Mild Cognitive Impairment | Cognitive Decline | Alzheimer Disease, Early Onset | Alzheimer Disease, Late Onset | MCI | Dementia Alzheimers | Mild Dementia | Dementia of Alzheimer Type | Cognitive Impairment, Mild | Alzheimer Disease 1 | Dementia, Mild | Alzheimer... and other conditionsUnited States
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Stanford UniversityRecruitingPANDAS | PANS | Pediatric Autoimmune Neuropsychiatric Disorders Associated With Streptococcal Infections | Pediatric Acute-Onset Neuropsychiatric SyndromeUnited States
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Assiut UniversityUnknownDiarrhea, InfantileEgypt
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Eisai Inc.TerminatedRefractory Partial Onset SeizuresUnited States
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Eisai Inc.CompletedPartial Onset SeizuresFrance, United Kingdom, Germany, Denmark, Czech Republic, Norway, Sweden, Ireland
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Imperial College London Diabetes CentreUnknownDiabetes Mellitus, Type 2 | Diabetes Mellitus, Type 1 | Maturity-onset Diabetes of the YoungUnited Arab Emirates
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Sanguine BiosciencesHoffmann-La RocheRecruitingHuntington Disease | Huntington's Dementia | Huntington Disease, Late Onset | Huntington; Dementia (Etiology)United States
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Akron Children's HospitalCompletedInfantile Nystagmus SyndromeUnited States
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Royal Devon and Exeter NHS Foundation TrustUniversity of ExeterCompletedType 1 Diabetes | Type 1 Diabetes Mellitus Maturity OnsetUnited Kingdom
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Wolfson Medical CenterUnknownLabor Onset and Length Abnormalities
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Mahidol UniversityMinistry of Health, ThailandUnknown
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Halic UniversityIstanbul University - Cerrahpasa (IUC)CompletedInfantile Colic | Microbial Colonization | CryingTurkey
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Marinus PharmaceuticalsTerminatedDrug Resistant Partial Onset SeizureUnited States
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Stanford UniversityTerminated
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Marinus PharmaceuticalsCompletedDrug Resistant Partial Onset SeizureUnited States, Australia, Russian Federation, Bulgaria, Germany, Poland
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LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany