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Clinical Trials on Primary Disease Facioscapulohumeral Dystrophy (FSHD)
Total 54764 results
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LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany
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Centre for Human Drug Research, NetherlandsFacio TherapeuticsCompleted
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Centre Hospitalier Universitaire de Saint EtienneAssociation Française contre les Myopathies (AFM), ParisCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Grete Andersen, MDAP Moeller Foundation; The Danish Rheumatism Association; Aase and Ejnar Danielsens... and other collaboratorsCompletedFacioscapulohumeral Muscle DystrophyDenmark
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Nationwide Children's HospitalRecruiting
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Istanbul University - Cerrahpasa (IUC)CompletedFacio-Scapulo-Humeral DystrophyTurkey
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Radboud University Medical CenterSolve FSHDRecruitingMuscular Dystrophy, FacioscapulohumeralNetherlands
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de Saint EtienneÖrebro University, Sweden; Association Française contre les Myopathies (AFM)...CompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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Ohio State UniversityCompletedMuscular Dystrophy, Facioscapulohumeral
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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Centre Hospitalier Universitaire de Saint EtienneMinistry of Health, France; Association Française contre les Myopathies (AFM)...CompletedMuscular Dystrophy | FacioscapulohumeralFrance
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AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
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Swiss Federal Institute of TechnologyCompletedMuscle Weakness | Muscular Dystrophies | Muscular Dystrophy | Muscular Dystrophy, Facioscapulohumeral | Scapular Dyskinesis | Muscular WeaknessGermany, Switzerland
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Centre Hospitalier Universitaire de NiceActive, not recruitingMuscular Dystrophy | FacioscapulohumeralFrance
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University of LiverpoolBournemouth University; Robert Jones and Agnes Hunt Orthopaedic and District... and other collaboratorsRecruitingNeuromuscular Diseases | Shoulder Injuries | Shoulder Pain | Upper Extremity Problem | Facio-Scapulo-Humeral DystrophyUnited Kingdom
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University Hospital, MontpellierUnknownDuchenne Muscular Distrophy (DMD)France
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Gangnam Severance HospitalCompletedInherited Retinal Dystrophy Primarily Involving Sensory Retina | Inherited Retinal Dystrophy Primarily Involving Retinal Pigment EpitheliumKorea, Republic of
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Shahid Beheshti University of Medical SciencesUnknownInherited Retinal Dystrophy Primarily Involving Sensory Retina | Inherited Retinal Dystrophy Primarily Involving Retinal Pigment EpitheliumIran, Islamic Republic of
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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Manhattan Eye, Ear & Throat HospitalNorthwell HealthWithdrawnPattern Dystrophy of MaculaUnited States
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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Legacy Health SystemDevers Eye Institute; Lions Eye Bank of Oregon Vision Research Laboratory; Fischer...UnknownFuchs' Corneal Endothelial DystrophyUnited States
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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Avidity Biosciences, Inc.Not yet recruitingMyotonic Dystrophy | Myotonic Disorders | Myotonia | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert Disease | Steinert
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University of North Carolina, Chapel HillNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb-Girdle Muscular DystrophyUnited States
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State University of New York at BuffaloActive, not recruitingFuchs DystrophyUnited States
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University Hospital, LilleRecruitingMacular Degeneration | Cone Dystrophy | Cone Rod Dystrophy | Retinal Dystrophy, Cone-RodFrance
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Retrotope, Inc.CompletedNeuroaxonal Dystrophy, InfantileEgypt, China, Saudi Arabia, India, Tunisia
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Centre Hospitalier Universitaire de Saint EtienneKyoto University, Graduate School of MedicineCompletedFuchs Endothelial Corneal DystrophyFrance
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Kowa Research Institute, Inc.CompletedFuchs' Endothelial Corneal DystrophyUnited States, Australia, Germany, Spain, Denmark
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Medical College of WisconsinCompletedCataract | Fuchs' Corneal DystrophyUnited States
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Boston Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingLimb-girdle Muscular Dystrophy | Neuromuscular; Disorder, Hereditary | Duchenne/Becker Muscular DystrophyUnited States
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Virginia Commonwealth UniversityEdgewise Therapeutics, Inc.RecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Muscular Dystrophy in Children | Muscular Dystrophy, BeckerUnited States, New Zealand, United Kingdom
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Massachusetts General HospitalCompletedDuchenne Muscular Dystrophy | Dystrophinopathy | Becker's Muscular DystrophyUnited States
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Cornea Research Foundation of AmericaCompletedBullous Keratopathy | Fuchs' Endothelial Corneal Dystrophy | Iridocorneal Endothelial Syndrome | Posterior Polymorphous DystrophyUnited States
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Rigshospitalet, DenmarkCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy Type 2IDenmark
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Trefoil Therapeutics, Inc.CompletedEndothelial Dysfunction | Corneal Endothelial Dystrophy | Pseudophakic Bullous Keratopathy | Fuchs Endothelial Corneal DystrophyUnited States
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Retina Implant AGTerminatedRetinal Degeneration | Inherited Retinal Dystrophy Primarily Involving Sensory RetinaFrance
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University Hospital of North NorwayUniversity of Tromso; Norwegian Muscle Disease Association (FFM); Norwegian National... and other collaboratorsActive, not recruitingMuscular Dystrophies | Limb Girdle Muscular Dystrophy | Limb Girdle Muscular Dystrophy, Type 2I | Limb Girdle Muscular Dystrophy R9 FKRP-relatedNorway
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Massachusetts Eye and Ear InfirmaryRecruitingFuchs' Endothelial Corneal DystrophyUnited States
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Innostellar Biotherapeutics Co.,LtdRecruitingInherited Retinal DystrophyChina
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Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
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Charite University, Berlin, GermanyUnknownEndothelial Dysfunction | Bullous Keratopathy | Fuchs' Endothelial Corneal Dystrophy | Iridocorneal Endothelial Syndrome | Posterior Polymorphous DystrophyGermany
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)CompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States
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Institut National de la Santé Et de la Recherche...RecruitingLaminopathies | Emery Dreifuss Muscular Dystrophy 2 | LMNA-Related Congenital Muscular Dystrophy | Dilated Cardiomyopathy-1AFrance