- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Proteostasis Deficiencies in United Kingdom
Total 920 results
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Prothena Biosciences Ltd.CompletedPrimary AmyloidosisUnited States
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University of UlsterBelfast Health and Social Care Trust; Sheffield Teaching Hospitals NHS Foundation... and other collaboratorsRecruitingStroke | Paralysis | Motor Neuron Disease | Disorder of Consciousness | Physical DisabilityUnited Kingdom, Ireland
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Alnylam PharmaceuticalsCompletedPolyneuropathy | Hereditary Transthyretin-mediated (ATTRv) AmyloidosisUnited States
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University of ChicagoMassachusetts General Hospital; Washington University School of Medicine; National... and other collaboratorsRecruitingAmyotrophic Lateral SclerosisUnited States
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Ono Pharmaceutical Co. LtdCompletedAmyotrophic Lateral Sclerosis (ALS)Belgium, France, Austria, Germany, Italy, Netherlands, Switzerland, United Kingdom
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Orion Corporation, Orion PharmaCompletedAmyotrophic Lateral SclerosisCanada, United States, Australia, Austria, United Kingdom, Germany, Finland, Spain, France, Italy, Sweden, Netherlands, Belgium, Ireland
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI)CompletedPrimary Systemic AmyloidosisUnited States
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Prothena Biosciences Ltd.Amyloidosis Research Consortium; Amyloidosis Support Groups; Amyloidosis Foundation and other collaboratorsCompletedAL Amyloidosis | AmyloidosisUnited States
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Amylyx Pharmaceuticals Inc.Massachusetts General Hospital Neurology Clinical Research InstituteCompletedAmyotrophic Lateral Sclerosis | ALSUnited States
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Richard Bedlack, M.D., Ph.D.Ultragenyx Pharmaceutical IncCompleted
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Chippewa Valley Eye ClinicTA-SciencesCompleted
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University of Kansas Medical CenterGilead SciencesUnknown
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ProgenaBiomeRecruitingMotor Neuron Disease | Amyotrophic Lateral Sclerosis | ALSUnited States
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Clene NanomedicineMassachusetts General HospitalAvailable
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Mayo ClinicCompletedAmyotrophic Lateral SclerosisUnited States
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Johns Hopkins UniversityPrecision MolecularTerminatedAmyotrophic Lateral SclerosisUnited States
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NeuroSense Therapeutics Ltd.CompletedALS (Amyotrophic Lateral Sclerosis)United States
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VA Office of Research and DevelopmentFlorida Institute for Human and Machine CognitionCompletedAmyotrophic Lateral SclerosisUnited States
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National Institute of Neurological Disorders and...CompletedMotor Neuron Disease | Primary Lateral SclerosisUnited States
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Mayo ClinicCompletedAmyotrophic Lateral SclerosisUnited States
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Massachusetts General HospitalThe Salah Foundation; MGH cure ALS FundCompletedAmyotrophic Lateral SclerosisUnited States
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Drexel University College of MedicineMDA/ALS Center of HopeTerminatedNeurodegenerative Diseases | Amyotrophic Lateral SclerosisUnited States
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Johns Hopkins UniversityCornell University; Nutricia North AmericaTerminatedAmyotrophic Lateral SclerosisUnited States
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TCA Cellular TherapySuspendedAmyotrophic Lateral SclerosisUnited States
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Avid RadiopharmaceuticalsNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedParkinson's DiseaseUnited States
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Novartis PharmaceuticalsCompletedAmyotrophic Lateral SclerosisUnited States
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Stanford UniversityCompletedAmyloidosis | Blood and Marrow Transplant (BMT)United States
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Phoenix Neurological Associates, LTDForest LaboratoriesCompletedAmyotrophic Lateral SclerosisUnited States
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National Center for Research Resources (NCRR)CompletedAmyotrophic Lateral SclerosisUnited States
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University of Southern CaliforniaNational Institute on Aging (NIA); Alzheimer's Therapeutic Research Institute; Alzheimer's AssociationCompletedCognition DisordersUnited States
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PfizerCompletedFamilial Amyloid PolyneuropathyUnited Kingdom, Spain, United States, Argentina, Brazil, France, Germany, Portugal, Sweden
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VA Office of Research and DevelopmentRecruiting
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Richard Bedlack, M.D., Ph.D.CompletedAmyotrophic Lateral SclerosisUnited States
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Dwight Koeberl, M.D., Ph.D.CompletedAmyotrophic Lateral SclerosisUnited States
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Wake Forest University Health SciencesALS Therapy Development InstituteCompletedAmyotrophic Lateral SclerosisUnited States
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Cedars-Sinai Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Completed
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University of MichiganTerminatedAmyotrophic Lateral SclerosisUnited States
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University of MichiganTerminatedAmyotrophic Lateral SclerosisUnited States
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University of MichiganNational Institute of Neurological Disorders and Stroke (NINDS)CompletedAmyotrophic Lateral Sclerosis | ALSUnited States
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BiogenIonis Pharmaceuticals, Inc.CompletedAmyotrophic Lateral SclerosisUnited States, Canada, Belgium, France, Australia, Japan, Denmark, Korea, Republic of, United Kingdom, Germany, Italy, Poland
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National Cancer Institute (NCI)Recruiting
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Cellenkos, Inc.RecruitingAmyotrophic Lateral SclerosisUnited States
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University of MiamiMassachusetts General HospitalCompletedAmyotrophic Lateral SclerosisUnited States
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PathMaker Neurosystems Inc.Spaulding Rehabilitation Hospital; Muscular Dystrophy Association; Sean M. Healey...RecruitingAmyotrophic Lateral SclerosisUnited States
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Mayo ClinicNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingAmyotrophic Lateral SclerosisUnited States
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University of PennsylvaniaNational Institutes of Health (NIH)RecruitingAlzheimer Disease | Frontotemporal Lobar Degeneration | Cognitively NormalUnited States
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University of MiamiALS AssociationRecruitingAmyotrophic Lateral SclerosisUnited States
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n-Lorem FoundationMayo ClinicActive, not recruitingAmyotrophic Lateral SclerosisUnited States
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University of MiamiActive, not recruitingAmyotrophic Lateral SclerosisUnited States