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Clinical Trials on Proteostasis Deficiencies
Total 1831 results
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Duke UniversityUCB PharmaCompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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University of California, Los AngelesNational Institute on Aging (NIA)UnknownFrontotemporal Degeneration | Frontotemporal Dementia | Alzheimer's Disease | Social BehaviorUnited States
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Region ÖstergötlandActive, not recruitingObesity | Bariatric Surgery | Micronutrient DeficienciesSweden
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Leiden University Medical CenterThe Dutch Brain Foundation (funding)Not yet recruitingCerebral Amyloid Angiopathy
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University of Sao Paulo General HospitalPfizerRecruiting
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Johns Hopkins UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingAmyotrophic Lateral Sclerosis | Tetraplegia | Locked-in Syndrome | Brainstem StrokeUnited States
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CENTOGENE GmbH RostockAlnylam PharmaceuticalsRecruitingCardiomyopathies | Polyneuropathies | Transthyretin Amyloidosis | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid PolyneuropathyGermany, Austria, Switzerland
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Montreal Heart InstituteActive, not recruitingNeurodegenerative Diseases | Primary Progressive Aphasia | Semantic Dementia | Logopenic Progressive Aphasia | Non-fluent AphasiaCanada
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Istituto Clinico HumanitasFondazione I.R.C.C.S. Istituto Neurologico Carlo Besta; Fondazione Salvatore...CompletedAmyotrophic Lateral Sclerosis | Postural Orthostatic Tachycardia Syndrome | Pure Autonomic Failure | Anti-Cholinergic Receptors AntibodiesItaly
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Beth Israel Deaconess Medical CenterMerz PharmaceuticalsWithdrawnParkinson Disease | Amyotrophic Lateral SclerosisUnited States
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National Institute of Allergy and Infectious Diseases...CompletedInherited Immune DeficienciesUnited States
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Inonu UniversityCompletedSmoking | Oxygen Deficiencies
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Universidade do PortoCentro Hospitalar Universitário São João, E.P.E. (CHUSJ); Centro de Investigação... and other collaboratorsRecruitingCarpal Tunnel Syndrome | Transthyretin AmyloidosisPortugal
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Mayo ClinicRecruitingPrimary Progressive Aphasia | Behavioral Variant of Frontotemporal Dementia | Frontotemporal Dementia, Behavioral VariantUnited States
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Northwestern UniversityEmory UniversityCompletedPrimary Progressive Aphasia | Caregiver BurnoutUnited States
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National Institute of Neurological Disorders and...CompletedAmyotrophic Lateral Sclerosis | Frontotemporal Lobar DegenerationUnited States
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Wave Life Sciences Ltd.TerminatedALS | FTDNetherlands, United Kingdom
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Transposon Therapeutics, Inc.Active, not recruitingAmyotrophic Lateral Sclerosis | Frontotemporal DementiaSpain, United States, Belgium, France, Germany
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CENTOGENE GmbH RostockCompletedNeuropathic Pain | Orthostatic Hypotension | Cardiac Failure | Gastrointestinal Disorders | Polyneuropathy, AmyloidSpain, Austria, Hungary, North Macedonia, Poland, Serbia
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University of Missouri-ColumbiaNational Institute on Deafness and Other Communication Disorders (NIDCD)CompletedParkinson Disease | Amyotrophic Lateral SclerosisUnited States
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Centre Hospitalier Universitaire de NīmesWithdrawnAlzheimer Disease | Amyloid Cerebral AngiopathyFrance
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Hill-RomCompletedMotor Neuron Disease | Cystic Fibrosis | Airway Clearance ImpairmentUnited States
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Neuronetrix, Inc.CompletedCognitive Impairment | Dementia | Alzheimer Disease | Frontotemporal Dementia | Memory DisordersUnited States
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Assistance Publique - Hôpitaux de ParisTerminatedAmyotrophic Lateral Sclerosis | Frontotemporal DementiaFrance
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Bellus Health IncFDA Office of Orphan Products DevelopmentCompletedGastrointestinal Diseases | Kidney Diseases | Rheumatoid Arthritis | Nephrotic Syndrome | Secondary (AA) Amyloidosis | Familial Mediterranean SyndromeUnited States, Israel, Finland, France, Italy, Lithuania, Netherlands, Poland, Russian Federation, Spain, Turkey, United Kingdom
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Steen Hvitfeldt PoulsenNovo Nordisk A/SRecruitingQuality of Life | Transthyretin Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Wild-Type Transthyretin-Related (ATTR)AmyloidosisDenmark
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Synaptrix Labs Inc.Not yet recruitingParalysis | Amyotrophic Lateral Sclerosis | Spinal Cord Injuries | Neurologic Disorder | Cervical Spinal Cord Injury | Paralysis; Stroke | Tetraplegic; Paralysis | Quadriplegia/TetraplegiaUnited States
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Nova Scotia Health AuthorityRecruitingInsomnia | Dementia | Frontotemporal DementiaCanada
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Capital Medical UniversityRecruitingCerebral Amyloid AngiopathyChina
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Wave Life Sciences Ltd.TerminatedALS | FTDCanada, Belgium, New Zealand, Netherlands, Australia, Sweden, United Kingdom, Ireland
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Wake Forest University Health SciencesCompletedCovid19 | Amyotrophic Lateral SclerosisUnited States
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Massachusetts General HospitalCompletedMultiple Myeloma | AmyloidosisUnited States
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University of British ColumbiaTerminatedPrimary Progressive Nonfluent AphasiaCanada
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Axon Neuroscience SEUnknownPrimary Progressive Nonfluent AphasiaGermany
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Southwest Oncology GroupNational Cancer Institute (NCI)CompletedMultiple Myeloma | Amyloidosis | Waldenstrom's Macroglobulinemia | Monoclonal Gammopathy of Undetermined Significance | Smoldering MyelomaUnited States
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China Medical University HospitalUnknownParkinson's Disease | Amyotrophic Lateral Sclerosis | Alzheimer Disease
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University Hospital, LilleTakeda; Laboratoire français de Fractionnement et de Biotechnologies; VitalAire; French Healthcare network for rare immune and hematological disorders (MARIH)Not yet recruitingSpecific Antibody Deficiency | Predominantly Antibody Deficiencies
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RwHealthNorthern Care Alliance NHS Foundation Trust; Alnylam PharmaceuticalsNot yet recruitingHereditary Amyloidosis | Guillain-Barre Syndrome | Chronic Inflammatory Demyelinating PolyneuropathyUnited Kingdom
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Daniel Serrani AzcurraZarebski Graciela, Kabanchik Alicia, Marconi AraceliRecruitingDepression | Dementia of Alzheimer Type | Dementia Frontotemporal | Narcissistic Personality Disorder | Personality ChangeArgentina
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Johns Hopkins UniversityNational Institute on Aging (NIA)RecruitingPrimary Progressive Aphasia | Logopenic Progressive Aphasia | Non-Fluent Primary Progressive AphasiaUnited States, Canada
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
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Bellus Health IncNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Neurologic Diseases, GeneralUnited States
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University of LausanneCompletedObesity | Nutritional DeficienciesSwitzerland
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Institut National de Recherche pour l'Agriculture...CompletedMitochondrial Respiratory Chain DeficienciesFrance
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Diego MorettiNot yet recruiting
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Columbia UniversityCompleted
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University of Maryland, BaltimoreIndian Council of Medical Research; Micronutrient Initiative; The Mathile Institute...CompletedDevelopmental Delay | Nutritional DeficienciesIndia
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University of EdinburghNHS LothianNot yet recruitingMultiple Sclerosis | Parkinson Disease | Motor Neuron Disease | Dementia
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University of ArizonaRecruitingLanguage Disorders | Primary Progressive Aphasia | Aphasia, Acquired | Stroke, CerebrovascularUnited States
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University of California, San FranciscoCompletedDementia | Frontotemporal Dementia | Frontotemporal Lobar Degeneration | Caregiver Stress Syndrome | Caregiver Burnout | Dementia Frontal | Mindfulness Based Stress ReductionUnited States