- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Proteostasis Deficiencies
Total 1775 results
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Ramsay Générale de SantéEuropean Clinical Trial Experts NetworkRecruitingAmyloid | Systemic AmyloidosisFrance
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The Christ HospitalThe Cleveland Clinic; Ohio State UniversityRecruitingTransthyretin AmyloidosisUnited States
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Mathew S. MaurerNational Heart, Lung, and Blood Institute (NHLBI); Yale University; Boston Medical... and other collaboratorsRecruitingAmyloid Cardiomyopathy, Transthyretin-RelatedUnited States
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PfizerActive, not recruitingTransthyretin Amyloid CardiomyopathyKorea, Republic of
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PfizerCompletedTransthyretin Amyloid CardiomyopathyChina
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Nanjing University School of MedicineRecruiting
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Oregon Health and Science UniversityIonis Pharmaceuticals, Inc.RecruitingAmyloidosis | Transthyretin Amyloid CardiomyopathyUnited States
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Second Affiliated Hospital, School of Medicine,...Recruiting
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University of TriestePfizerUnknownAmyloid CardiomyopathyItaly
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Steen Hvitfeldt PoulsenRecruitingATTR Amyloidosis Wild TypeDenmark
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Alexion Pharmaceuticals, Inc.RecruitingTransthyretin Amyloid CardiomyopathyUnited States, Spain, United Kingdom, Norway, Israel, Korea, Republic of, Belgium, France, Germany, Italy, Japan, China, Australia, Argentina, Austria, Taiwan, Switzerland, Canada, Sweden, Poland, Denmark, Turkey, Brazil, Netherlands, G... and more
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Ospedale C & G MazzoniRecruitingHeart Failure | Amyloidosis CardiacItaly
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Cedars-Sinai Medical CenterRecruitingCardiac AmyloidosisUnited States
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Neurimmune AGCompletedAmyloid Transthyretin CardiomyopathyGermany, France, Netherlands, Spain
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Oncology Institute of Southern SwitzerlandUniversity of Kiel; Ente Ospedaliero Cantonale, BellinzonaCompleted
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Brigham and Women's HospitalRecruitingTransthyretin Cardiac Amyloidosis | Amyloid CardiomyopathyUnited States
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AstraZenecaRecruiting
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PfizerRecruitingTransthyretin Amyloid CardiomyopathyIndia
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Brigham and Women's HospitalNot yet recruitingTransthyretin Amyloid CardiopathyUnited States
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Columbia UniversityCompletedTransthyretin Amyloid CardiomyopathyUnited States
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AZ Sint-Jan AVActive, not recruiting
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Alnylam PharmaceuticalsCompletedFamilial Amyloidotic Cardiomyopathy (FAC)United States, France, Spain, United Kingdom, Belgium, Brazil
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Alexion Pharmaceuticals, Inc.Eidos Therapeutics, a BridgeBio companyActive, not recruitingSymptomatic Transthyretin Amyloid CardiomyopathyJapan
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Eidos Therapeutics, a BridgeBio companyActive, not recruitingAmyloid Cardiomyopathy, Transthyretin-RelatedUnited States, Spain, Australia, Canada, Italy, Netherlands, Ireland, New Zealand, Belgium, Israel, Greece, Korea, Republic of, Czechia, Brazil, Denmark, Portugal, United Kingdom
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Aarhus University Hospital SkejbyActive, not recruitingHeart Failure | Transthyretin Amyloid CardiomyopathyDenmark
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Paolo MilaniRecruitingAmyloidosis | Amyloidosis Cardiac | ATTR Amyloidosis Wild TypeItaly
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Akcea TherapeuticsRecruitingPregnancy | Hereditary Transthyretin-mediated Amyloidosis With PolyneropathyUnited States
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University Hospital, EssenRecruitingDetection of Occult Cardiac AmyloidosisGermany
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PfizerRecruiting
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Mahidol UniversityPfizerNot yet recruiting
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University Hospital Center of MartiniqueRecruiting
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Montefiore Medical CenterActive, not recruitingTransthyretin Cardiac Amyloidosis | Transthyretin Amyloid CardiomyopathyUnited States
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Mayo ClinicPfizerCompletedHeart Failure With Preserved Ejection FractionUnited States
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Medical University of GrazMedical University InnsbruckRecruitingAmyloid Cardiomyopathy | Wild Type ATTR AmyloidosisAustria
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Virginia Commonwealth UniversityNot yet recruitingAmyloidosis, HereditaryUnited States
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Boston UniversityCompleted
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PfizerRecruitingATTR-CM (Transthyretin Amyloid Cardiomyopathy)Korea, Republic of
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Novo Nordisk A/SActive, not recruitingTransthyretin Amyloid Cardiomyopathy (ATTR CM)United States, Netherlands, Spain, Portugal, Canada, Czechia, France, Germany, Italy, Japan
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University Hospital, ToulouseMSDAVENIRActive, not recruitingFrail ElderlyFrance
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Ionis Pharmaceuticals, Inc.AstraZenecaRecruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)United States, Austria, Belgium, Canada, France, Germany, Israel, Italy, Portugal, Spain, Sweden, United Kingdom, Australia, Greece
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Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated Amyloidosis | ATTR AmyloidosisIsrael, Italy, Netherlands, Spain, United States, France, Denmark, Germany, Portugal, Brazil, Taiwan
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Central Hospital, Nancy, FranceRecruiting
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Ionis Pharmaceuticals, Inc.Active, not recruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)United States, Australia, Spain, Canada, Germany, Japan, Italy, Israel, Argentina, France, Portugal, Austria, Brazil, Greece, United Kingdom, Czechia, Sweden, Belgium, Denmark, Poland, Puerto Rico
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Zhejiang UniversityRecruitingTransthyroxin Amyloidosis CardiomyopathyChina
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Alnylam PharmaceuticalsCompletedTransthyretin-mediated Amyloidosis (ATTR Amyloidosis)United Kingdom
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Eidos Therapeutics, a BridgeBio companyCompletedHeart Diseases | Amyloidosis | Cardiomyopathies | Transthyretin Amyloidosis | Amyloid CardiomyopathyUnited States, Netherlands, Ireland, Canada, Italy, Spain, Belgium, New Zealand, Israel, Australia, Portugal, Brazil, Poland, Czechia, Denmark, Greece, Korea, Republic of, United Kingdom
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Assistance Publique - Hôpitaux de ParisCompletedDiagnosis | Polyneuropathy | Idiopathic Progressive NeuropathyFrance
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Steen Hvitfeldt PoulsenRecruitingTransthyretin Amyloidosis | Transthyretin Cardiac Amyloidosis | Wild-Type Transthyretin-Related (ATTR)AmyloidosisDenmark
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Ionis Pharmaceuticals, Inc.Approved for marketingAmyloidosis, Hereditary
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Algalarrondo VincentBichat Hospital; BioquantisRecruitingTransthyretin Cardiac Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Amyloid CardiomyopathyFrance