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Clinical Trials on Rett Syndrome, Atypical
Total 34399 results
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RecruitingRett Syndrome | Rett Syndrome, Atypical | RTTUnited States
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome, Preserved Speech Variant | Mecp2 Duplication Syndrome | Rett-related DisordersUnited States
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama... and other collaboratorsRecruiting
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Jazz PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Spain, Italy, United Kingdom
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Northwestern UniversityCompletedAtypical Facial Pain | Typical Facial PainUnited States
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Memorial Sloan Kettering Cancer CenterActive, not recruitingChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Myeloproliferative Neoplasms | Atypical Chronic Myeloid Leukemia | Myelodysplastic/Myeloproliferative Overlapping SyndromeUnited States
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National Cancer Institute (NCI)TerminatedChronic Myelomonocytic Leukemia | Previously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | Atypical Chronic Myeloid Leukemia, BCR-ABL1 Negative | Myelodysplastic/Myeloproliferative Neoplasm, Unclassifiable | de Novo Myelodysplastic SyndromesUnited States
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University Hospital, ToursHospices Civils de Lyon; University Hospital, Strasbourg, France; University... and other collaboratorsActive, not recruitingHemolytic-Uremic Syndrome, AtypicalFrance
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AlexionCompletedAtypical Hemolytic-Uremic SyndromeUnited Kingdom, United States, France, Italy, Germany, Spain, Belgium
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Alexion PharmaceuticalsCompletedAtypical Hemolytic-Uremic SyndromeUnited Kingdom, Belgium, United States, Germany, Italy, France, Netherlands, Australia, Canada
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AlexionSyneos HealthRecruitingAtypical Hemolytic-Uremic SyndromeFrance, Germany, Israel, Italy, United Kingdom, Canada, United States, Australia, Belgium, Denmark, Korea, Republic of, Poland, Russian Federation, Spain, Taiwan
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome | MECP2 Duplication Disorder | Rett-related DisorderUnited States
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Alexion PharmaceuticalsCompletedAtypical Hemolytic Uremic Syndrome (aHUS)Japan
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Alexion PharmaceuticalsCompletedATYPICAL HEMOLYTIC UREMIC SYNDROME (AHUS)Japan
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University Hospital, GhentCompletedAtypical Hemolytic Uraemic SyndromeBelgium
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St. Petersburg State Pavlov Medical UniversityTerminatedMyelodysplastic Syndromes | Leukemia, Chronic Myeloid | Leukemia, Myeloid, Chronic, Atypical, BCR-ABL NegativeRussian Federation
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Queen's UniversityCompletedChest Pain Atypical SyndromeCanada
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Washington University School of MedicineCTI BioPharmaWithdrawnMyelodysplastic Syndromes | Myelofibrosis | Chronic Myelomonocytic Leukemia | Juvenile Myelomonocytic Leukemia | Myeloproliferative Neoplasm | Atypical Chronic Myeloid Leukemia
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Maastricht University Medical CenterRecruitingThrombotic Microangiopathies | Hemolytic-Uremic Syndrome | Hemolytic Uremic Syndrome, AtypicalNetherlands
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Assistance Publique - Hôpitaux de ParisCompleted
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University of Colorado, DenverNational Institute on Aging (NIA)CompletedSuspected Typical Alzheimer's Disease (AD) | Suspected Atypical Alzheimer's Disease (AD)United States
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AstraZenecaRecruitingAtypical Hemolytic Uremic Syndrome(aHUS)China
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Alexion Pharmaceuticals, Inc.CompletedAtypical Hemolytic Uremic Syndrome (aHUS)United States, France, Spain, Taiwan, United Kingdom, Australia, Belgium, Germany, Italy, Japan, Korea, Republic of, Russian Federation, Austria, Canada
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AlexionCompletedAtypical Hemolytic Uremic Syndrome (aHUS)United States, France, Germany, Spain, Switzerland, Netherlands, Canada, Austria
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NovelMed TherapeuticsNot yet recruitingaHUS - Atypical Hemolytic Uremic Syndrome
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Alexion Pharmaceuticals, Inc.CompletedAtypical Hemolytic Uremic Syndrome (aHUS)Italy, United States, Korea, Republic of, Spain, Germany, Belgium, United Kingdom
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Alexion Pharmaceuticals, Inc.AstraZenecaRecruitingAtypical Hemolytic UremicChina
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Roswell Park Cancer InstituteNeuroEndocrine Tumor Research Foundation (NETRF)RecruitingLung Atypical Carcinoid Tumor | Metastatic Pancreatic Neuroendocrine Tumor | Lung Typical Carcinoid TumorUnited States
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Omar AljitawiRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Myelofibrosis | Chronic Myelomonocytic Leukemia | Myelodysplastic/Myeloproliferative Neoplasm | Atypical Chronic Myeloid Leukemia | Chronic Monocytic LeukemiaUnited States
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University Hospital, Basel, SwitzerlandNovartisCompletedRett's SyndromeSwitzerland
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge Syndrome | Complete Atypical DiGeorge Anomaly | Complete Atypical DiGeorge SyndromeUnited States
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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ACADIA Pharmaceuticals Inc.Completed
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IRCCS Eugenio MedeaAssociazione Italiana Rett (AIRett) O.n.l.u.s.Completed
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Rett Syndrome Research TrustDuke UniversityCompletedRett SyndromeUnited States
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgCompleted
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Montefiore Medical CenterRett Syndrome Research TrustCompleted
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Montefiore Medical CenterRett Syndrome Research TrustCompletedRett SyndromeUnited States
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Assistance Publique Hopitaux De MarseilleCompleted
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Medical University of ViennaCompleted
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Immunovia, Inc.CompletedPancreatic Ductal Adenocarcinoma | Familial Pancreatic Cancer | FAMMM - Familial Atypical Mole Malignant Melanoma SyndromeUnited States, Sweden, Canada, Spain, United Kingdom
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedRett Syndrome | CDKL5 Disorder | MECP2 Duplication dIsorder | FOXG1 SyndromeUnited States
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Claremont Graduate UniversityGruter InstituteCompleted
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National Cancer Institute (NCI)TerminatedRecurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13;q22) | Adult Acute Myeloid Leukemia With t(8;21)(q22;q22) | Secondary Acute Myeloid Leukemia and other conditionsCanada
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University of North Carolina, Chapel HillCompletedTypical DevelopmentUnited States
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The University of Texas Medical Branch, GalvestonCompleted
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PapiVax Biotech, Inc.ParexelRecruitingASC-US | LSIL | ASC-H Atypical Squamous Cells, Cannot Rule Out High-Grade Squamous Intra-Epithelial LesionUnited States
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Mario Negri Institute for Pharmacological ResearchAlnylam PharmaceuticalsWithdrawn