- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Sanfilippo Disease Type A
Total 58197 results
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University of AbujaUniversity of CambridgeCompletedA Feasibility Study on Hypertensive Heart Failure TreatmentNigeria
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Fondation LenvalNot yet recruitingPediatric Triage in a Pediatric Emergency DepartmentFrance
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University College, LondonRecruiting
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University of British ColumbiaBiogenCompletedHemophilia A, Congenital | Hemophilia B, CongenitalCanada
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Eli Lilly and CompanyRecruitingElevated Lp(a) | Atherosclerotic Cardiovascular Disease (ASCVD)United States, Australia, Spain, Canada, Argentina, China, Italy, France, Japan, Taiwan, Korea, Republic of, Denmark, Germany, Hungary, Israel, Austria, Belgium, Netherlands, Brazil, Mexico, Romania, United Kingdom, Greece, Czechia, Poland and more
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Cliniques universitaires Saint-Luc- Université...CompletedHaemophilia A | Haemophilia BBelgium
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Stanford UniversityNational Cancer Institute (NCI)TerminatedRecurrent Hepatocellular Carcinoma | Child-Pugh Class A | Child-Pugh Class BUnited States, Japan
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Baxalta now part of ShireCompletedHemophilia A | Hemophilia B | Hemophilia A or B With InhibitorsPoland, United States, Bulgaria, Romania, Japan, Russian Federation, New Zealand, Croatia, Ukraine, Brazil
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GlaxoSmithKlineCompletedHepatitis BUnited States, Australia, Canada, New Zealand
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Jiangsu Province Centers for Disease Control and...Royal (Wuxi) Biological Co., LTDCompletedGroup A, C Polysaccharide Meningitis | Type b Haemophilus InfluenzaChina
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McGill University Health Centre/Research Institute...CHU de Quebec-Universite LavalUnknownType2 Diabetes | Islet Cell Transplantation | Type1 Diabetes MellitusCanada
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Association Clinique Thérapeutique Infantile du...RecruitingRisk Factors | Outcome, Fatal | Therapy | Severe Infection | Strain | Virulence Factors | Medical Care | Sepsis Due to Streptococcus, Group A | Medical ComplicationsFrance
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University of Missouri, Kansas CityCompletedA Multilevel, Tailored COVID-19 Testing Condition | A Nontailored COVID-19 Testing Control ConditionUnited States
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Novartis PharmaceuticalsCompletedPrevention of Acute Rejection in Paediatric Recipients of a Renal TransplantGermany, United Kingdom, France, Italy, United States, Hungary, Norway, Spain, Argentina, Brazil, Poland, Sweden, Turkey
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Fondation Ophtalmologique Adolphe de RothschildTerminatedOcclusion or Malformation of a Cerebral VesselFrance
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Cairo UniversityAbdelhamid, Bassant Mohamed, M.D.; Mohamed, Ahmed A., M.D.; Atef Kamel Salama; Nadia... and other collaboratorsCompletedNalbuphine as an Adjuvant to L. A in Peribulbar Block for Cataract SurgeryEgypt
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis IVA (Morquio A Syndrome)Australia
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Eline C. B. EskesRecruitingAsmd, Visceral TypeNetherlands
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NeuroDx DevelopmentBoston Children's HospitalUnknownCSF Flow Through the Shunt of a Hydrocephalus PatientUnited States
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National Institute of Allergy and Infectious Diseases...CompletedStreptococcus Group AMali
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Novartis PharmaceuticalsNot yet recruitingElevated Lp(a) and Established Atherosclerotic Cardiovascular Disease
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Novartis PharmaceuticalsActive, not recruitingLocally Advanced or Metastatic KRAS G12C-mutated NSCLC With a PD-L1 Expression <1% or a PD-L1 Expression ≥ 1% and an STK11 Co-mutationSpain, Italy, Austria, Netherlands, United Kingdom, Thailand, France, Belgium, China, Germany, Greece, Argentina, Turkey, Malaysia, Portugal, Brazil, United States, Hungary, India
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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Chulalongkorn UniversityRecruitingComparison of Outcomes Between Low Dose Emicizumab and Factor VIII in Clinically Severe Hemophilia AJoint Bleed | Severe Hemophilia A Without InhibitorThailand
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Novo Nordisk A/SActive, not recruitingHaemophilia A With Inhibitors | Haemophilia B With InhibitorsSpain, Korea, Republic of, India, Australia, United Kingdom, Russian Federation, Poland, Ukraine, Thailand, Mexico, United States, Turkey, Japan, South Africa, Serbia, France, Croatia, Denmark, Algeria, Bulgaria, Malaysia, Portugal, Slovaki... and more
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AryoGen Pharmed Co.CompletedHemophilia A With Inhibitor | Hemophilia B With InhibitorIran, Islamic Republic of
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.UnknownHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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rEVO BiologicsLaboratoire français de Fractionnement et de BiotechnologiesCompletedHemophilia A With Inhibitors | Hemophilia B With InhibitorsUnited States, Bulgaria, Poland, Russian Federation, Belarus, Georgia, Israel, Romania, Ukraine, United Kingdom
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BayerCompletedHemophilia A, Hemophilia BItaly, China, New Zealand, Russian Federation, Taiwan, Singapore, Bulgaria, United States, Denmark, Germany, Hungary, South Africa, United Kingdom, Romania, Colombia, Mexico, Turkey, France, India, Japan, Australia, Netherlands, Poland and more
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University of ChicagoAmerican College of Chest Physicians; The John A. Hartford Foundation; Association...CompletedTransfer to a Health Care Facility After Critical IllnessUnited States
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Shahid Beheshti University of Medical SciencesUnknownHorizontal Strabismus With High AC/A RatioIran, Islamic Republic of
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Vladikavkaz Scientific Center of the Russian Academy...RecruitingConditionally Healthy Persons | Persons With a High Body Mass IndexRussian Federation
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The University of Hong KongQueen Elizabeth Hospital, Hong Kong; Queen Mary Hospital, Hong Kong; Pamela Youde... and other collaboratorsCompleted
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Boris Gala LopezMcGill University Health Centre/Research Institute of the McGill University...WithdrawnLiver Failure as A Complication of Care | 30-day Mortality
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Boston UniversityCompletedVitamin D Deficiency | Vitamin E Deficiency | Hypovitaminosis AUnited States
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Sirtex MedicalBright Research PartnersRecruitingUnresectable Hepatocellular Carcinoma | BCLC Stage B Hepatocellular Carcinoma | BCLC Stage C Hepatocellular Carcinoma | BCLC Stage A Hepatocellular CarcinomaUnited States
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Centre Hospitalier Universitaire DijonCompletedUnresectable Non-metastatic Hepatocellular Carcinoma | Child A/B7 CirrhosisFrance
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Novo Nordisk A/SActive, not recruitingHaemophilia A Without Inhibitors | Haemophilia B Without InhibitorsSpain, United States, Korea, Republic of, United Kingdom, Australia, Lithuania, France, Turkey, India, Estonia, Russian Federation, Ukraine, Mexico, Japan, Serbia, Canada, Croatia, Algeria, Bosnia and Herzegovina, Bulgaria, Denmark and more
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Laboratoire français de Fractionnement et de BiotechnologiesLFB USA, Inc.CompletedA Phase III Study on the Safety, Pharmacokinetics and Efficacy of Coagulation Factor VIIa (PERSEPT2)Hemophilia A With Inhibitors | Hemophilia B With InhibitorsBulgaria, Ukraine, Czechia, United States, Georgia, South Africa
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Emory UniversityNational Cancer Institute (NCI)RecruitingHepatocellular Carcinoma | BCLC Stage B Hepatocellular Carcinoma | BCLC Stage C Hepatocellular Carcinoma | BCLC Stage A Hepatocellular CarcinomaUnited States
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Bleeding and Clotting Disorders Institute Peoria...Genentech, Inc.RecruitingVon Willebrand Disease, Type 3 | Concomitant VWD and HemophiliaUnited States
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Pr. Nicolas GIRERDRecruitingKidney Transplantation for More Than One Year | Patients With a Kidney Transplantation on CyclosporineFrance
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Hospital Clinic of BarcelonaAstraZenecaCompletedPatients Who Are Scheduled to Undergo a PCI (Percutaneous Coronary Intervention) for CTO (Chronic Total Occlusion)Spain
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Mandos LLCTerminatedNiemann-Pick Type C DiseaseUnited States
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ActelionCompleted
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LivaNovaCompletedPatients Implanted With a PacemakerKorea, Republic of, France, Spain, Germany, Japan, Portugal, Denmark, United States, Belgium, Canada, Italy
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University Hospital, LinkoepingRecruitingMRI | Liver Resection | Liver Failure as A Complication of CareSweden, Norway, Denmark, Finland
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Hospices Civils de LyonCompleted
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Assistance Publique - Hôpitaux de ParisMedian TechnologiesCompletedCT Scans Prior to Surgery With a Least 2 Years of Follow-upFrance