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Clinical Trials on Severe Combined Immune Deficiency (SCID)
Total 6112 results
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NYU Langone HealthWithdrawnSevere Sleep Apnea | Severe Insomnia | Epileptiform ActivityUnited States
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Riga Stradins UniversityLatvian Institute of Organic Synthesis; Latvian Biomedical Research and Study... and other collaboratorsUnknownPregnancy | Iodine Deficiency | Selenium Deficiency | Thyroid Autoimmune DiseaseLatvia
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Ultragenyx Pharmaceutical IncActive, not recruitingOrnithine Transcarbamylase (OTC) DeficiencyCanada, United States, France, Spain, United Kingdom
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Prothya BiosolutionsCompletedInfections | IgG DeficiencyNetherlands
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London School of Hygiene and Tropical MedicineCompletedHiv | Ebola Virus Disease | EbolaKenya, Uganda
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Federal Research Institute of Pediatric Hematology...Not yet recruitingSevere Congenital Neutropenia | GATA2 DeficiencyRussian Federation
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...TerminatedGenetic Disorder | Severe Aplastic Anemia | Immunodeficiency SyndromeUnited States
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Postgraduate Institute of Medical Education and...CompletedSeptic Shock | Severe Sepsis | Immune ModulationIndia
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Hospices Civils de LyonUnknownLiver Post-transplant PatientsFrance
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BriovaRx Infusion ServicesTerminatedPrimary Immune Deficiency DisorderUnited States
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Orpha LabsCompletedLeukocyte Adhesion Deficiency, Type II
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PfizerCompletedHIV Infections | CryptosporidiosisUnited States
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RevimmuneWashington University School of Medicine; University Hospital, Limoges; George...TerminatedSepsis, SevereUnited States, France
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Technische Universität DresdenGWT-TUD GmbHCompletedPrimary Immunodeficiency (PID) | Secondary Immunodeficiency (SID) | Neurological Autoimmune DiseaseGermany
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National Institute of Allergy and Infectious Diseases...CompletedLeukocyte-Adhesion Deficiency SyndromeUnited States
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University of AarhusCompletedGrowth Hormone DeficiencyDenmark
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CSL BehringRecruiting
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University of California, Los AngelesCompleted
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Fondazione TelethonCompletedImmunologic Deficiency SyndromesItaly, Israel
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Children's Hospital of PhiladelphiaCompletedImmunodeficienciesUnited States
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Medical College of WisconsinBaxter Healthcare CorporationWithdrawn
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Federal Research Institute of Pediatric Hematology...CompletedLeukemia, Myeloid, Acute | Opportunistic Infections | Graft vs Host Disease | Precursor T-Cell Lymphoblastic Leukemia-Lymphoma | Bone Marrow Failure Syndromes | Immune Deficiency DiseaseRussian Federation
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Indonesia UniversityKementerian Riset dan Teknologi / Badan Riset dan Inovasi Nasional, IndonesiaCompletedCovid19 | Vitamin D Deficiency | Overweight and Obesity | Immune DeficiencyIndonesia
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Bio Products LaboratoryCompletedPrimary Antibody DeficiencyUnited Kingdom
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Cecile TremblayMerck Sharp & Dohme LLC; Dalhousie University; Université de Montréal; Coalition... and other collaboratorsActive, not recruiting
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer CenterCompletedMetabolism, Inborn Errors | Methionine Adenosyltransferase Deficiency
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Universitas PadjadjaranRadboud University Medical CenterCompletedVitamin D Deficiency | Blood Platelet DisordersIndonesia
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Charles University, Czech RepublicRecruitingSepsis | Immune Deficiency | Immunologic Paralysis | Immunologic SuppressionCzechia
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Indiana UniversityWithdrawnArthritis, Rheumatoid | Vitamin D DeficiencyUnited States
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Hospices Civils de LyonUnknownPatients Waiting for a Liver Transplant.France
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University Hospital, GrenobleNot yet recruitingSevere Anaphylactic Reaction, Self-administration, Adrenaline, Self-assessment
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Rockefeller UniversityTerminatedMetabolic Syndrome | Immune DeficiencyUnited States
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Columbia UniversityClínica de Familia La Romana, Dominican RepublicRecruitingHIV Infections | Sexually Transmitted Diseases, Viral | Acquired Immune Deficiency SyndromeUnited States, Dominican Republic
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Michele StatonNational Institute on Drug Abuse (NIDA)CompletedHepatitis C | Drug Abuse | Acquired Immune Deficiency Syndrome VirusUnited States
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Columbia UniversityNational Institutes of Health (NIH)CompletedTuberculosis | HIV (Human Immunodeficiency Virus) | AIDS (Acquired Immune Deficiency Syndrome) | Non-communicable Diseases (NCD)Kenya
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S.LAB (SOLOWAYS)Center of New Medical Technologies; Triangel ScientificCompletedHyperlipoproteinemias | HyperhomocysteinemiaRussian Federation
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Aeglea BiotherapeuticsTerminatedArginase I Deficiency | HyperargininemiaCanada
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde | Dehydrogenase Deficiency | DiseasesUnited States
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Beijing Chest HospitalNot yet recruitingMalnutrition | Lung Cancer | Amino Acid Deficiency
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National Human Genome Research Institute (NHGRI)TerminatedCitrullinemia | Argininosuccinic Aciduria | Hyperargininemia | Ornithine Carbamoyltransferase Deficiency | Carbamoyl-Phosphate Synthase I Deficiency | N-Acetylglutamate Synthase DeficiencyUnited States
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Ospedale Policlinico San MartinoGlaxoSmithKlineCompletedAcquired ImmunodeficiencyItaly
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Fundació Institut de Recerca de l'Hospital de la...Fondo de Investigacion SanitariaActive, not recruitingPneumonia | Frail Elderly Syndrome | Sarcopenia | Elderly Infection | Nutrition Disorders in Old Age | Age Associated Immune DeficiencySpain
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Medical University of ViennaCompletedHyperemesis Gravidarum | Nausea Gravidarum | Vitamin C DeficiencyAustria
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AUG TherapeuticsRecruitingLeukocyte Adhesion DeficiencyUnited States
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CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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Emory UniversityTerminatedHIV/AIDS | Vitamin D Deficiency | Smoker LungUnited States