- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Sialic Storage Disease in Brazil
Total 8448 results
-
JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IUnited States, Brazil, Japan
-
Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
-
Hospital de Clinicas de Porto AlegreThe Isaac FoundationActive, not recruitingMucopolysaccharidoses | Mucopolysaccharidosis VI | Morquio A Syndrome | Mucopolysaccharidosis IV A | MPS IV A | MPS VI | MPS - Mucopolysaccharidosis | Morquio Syndrome A | Morquio SyndromeBrazil
-
Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
-
Freeline TherapeuticsRecruitingGaucher Disease, Type 1Spain, Israel, United States, United Kingdom, Brazil, Germany, Paraguay
-
Passage Bio, Inc.SuspendedLeukodystrophy, Globoid CellUnited States, Brazil, Netherlands, United Kingdom, Canada, Israel
-
ShireCovance; PRA Health Sciences; PharmaNetCompletedMucopolysaccharidosis II | Hunter Syndrome | MPS IIBrazil, Poland, Taiwan
-
Federal University of São PauloUnknownPeritoneal Dialysis | Renal Failure, End StageBrazil
-
Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler's Syndrome | Hurler-Scheie SyndromeBrazil, Canada
-
Ultragenyx Pharmaceutical IncTerminatedWilson Disease | Ornithine Transcarbamylase Deficiency | Glycogen Storage Disease Type IASpain, United Kingdom, Canada, United States, Brazil
-
Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
-
Hospital de Clinicas de Porto AlegreCompletedKidney Diseases | Chronic Kidney Diseases | Renal Insufficiency, Chronic | Kidney Failure, Chronic | End-Stage Kidney Disease | Kidney Insufficiency, ChronicBrazil
-
Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
-
University of Sao Paulo General HospitalWithdrawnVitamin D Deficiency | Hyperparathyroidism, Secondary | Renal Disease, End Stage | Adynamic Bone Disease | Restless Leg Disorder | Renal Disease BoneBrazil
-
REGENXBIO Inc.Active, not recruitingHurler Syndrome | Hurler-Scheie Syndrome | Mucopolysaccharidosis Type I (MPS I)United States, Brazil, Israel
-
Federal University of São PauloFundação de Amparo à Pesquisa do Estado de São PauloUnknown
-
Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo Syndrome)Spain, Netherlands, United Kingdom, United States, Brazil
-
Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIIUnited States, Brazil, Mexico, Portugal
-
REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
-
Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
-
ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
-
Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, Poland, Netherlands, Canada, Argentina, United Kingdom, Norway, Brazil, Czech Republic
-
AstraZenecaHospital Israelita Albert EinsteinRecruitingHepatocellular Carcinoma | Hepatocellular Carcinoma by BCLC Stage | Hepatocellular Carcinoma Stage I | Hepatocellular Carcinoma Stage III | Hepatocellular Carcinoma Stage IIBrazil
-
BioMarin PharmaceuticalCompletedMPS VIUnited States, Australia, France, Brazil, Germany, Portugal, United Kingdom
-
Alexion PharmaceuticalsTerminatedMPS IIIB (Sanfilippo B Syndrome)Spain, United States, Brazil, United Kingdom, Portugal, Italy
-
Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
-
ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)Denmark, Germany, Japan, Australia, France, Brazil, Czechia
-
ANS PharmaAllergisa Pesquisa Dermato-Cosmetica LTDAUnknownSkin Care | Skin Diseases, MetabolicBrazil
-
ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
-
Federal University of Rio Grande do SulHospital de Clinicas de Porto AlegreCompletedBipolar Disorder | Attention Deficit Hyperactivity DisorderBrazil
-
Marilia Medicine SchoolCompleted
-
Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
-
Latin American Cooperative Oncology GroupAstraZenecaNot yet recruitingExtensive-stage Small-cell Lung CancerBrazil
-
Adapt Produtos Oftalmológicos Ltda.UnknownEye Infection/Inflammation OtherBrazil
-
ShireTerminatedMetabolic Diseases | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Demyelinating Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Lysosomal Storage Diseases | Lipid Metabolism Disorders | Sphingolipidoses | Hereditary Central Nervous System Demyelinating Diseases and other conditionsUnited States, Denmark, France, Argentina, Belgium, Brazil, Canada, Germany, Japan, Turkey
-
Azidus BrasilCompleted
-
Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
-
Genzyme, a Sanofi CompanyTerminatedFabry DiseaseAustria, Brazil, France, United States, Argentina, Belgium, Canada, Finland, Hungary, Norway, Poland, Spain, Taiwan, United Kingdom
-
Amicus TherapeuticsCompletedFabry DiseaseFrance, Austria, United States, Belgium, Japan, United Kingdom, Denmark, Brazil, Australia, Italy
-
Universidade Estadual de LondrinaNational Council for Scientific and Technological Development (CNPq) - BrazilUnknownPulmonary Disease, Chronic ObstructiveBrazil
-
REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
-
University of Sao Paulo General HospitalRecruitingChronic Obstructive Pulmonary DiseaseBrazil
-
University of the State of Santa CatarinaTerminatedPulmonary Disease, Chronic ObstructiveBrazil
-
Eduardo Foschini MirandaUnknownFatigue | Chronic Obstructive Pulmonary DiseaseBrazil
-
Universidade Federal de PernambucoUnknownChronic Obstructive Pulmonary DiseaseBrazil
-
Hospital Israelita Albert EinsteinRecruitingAssessment of Patients Undergoing Cardiac Surgery and Admitted to the Intensive Care Unit (BraSIS-2)Cardiac Disease | Cardiac Valve Disease | Cardiac IschemiaBrazil
-
Universidade Federal do Rio Grande do NorteCompletedObesity | Chronic Obstructive Pulmonary Disease ModerateBrazil
-
Federal University of São PauloCompletedPulmonary Disease, Chronic Obstructive | Pulmonary Emphysema | Chronic BronchitisBrazil
-
Universidade Federal de PernambucoCompletedParkinson's Disease.Brazil
-
Universidade Federal de PernambucoConselho Nacional de Desenvolvimento Científico e TecnológicoUnknownChronic Obstructive Pulmonary Disease (COPD)Brazil