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Clinical Trials on Sialic Storage Disease
Total 381619 results
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University of FloridaDiabetes SentryTerminatedClinical Evaluation of a Non-Invasive Hypoglycemia Detector in a Glycogen Storage Disease PopulationGlycogen Storage DiseaseUnited States
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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University Hospital Center of MartiniqueRecruiting
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University of California, IrvineCompletedMuscle Weakness | Pompe DiseaseUnited States
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Rambam Health Care CampusUnknown
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Azienda Ospedaliera Città della Salute e della...San Salvatore Hospital of L'AquilaUnknownPeripheral Artery Occlusive Disease | Popliteal Sciatic Nerve Block
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University of California, San FranciscoDuke UniversityRecruitingWolman Disease | MPS IVA | Pompe Disease Infantile-Onset | Gaucher Disease, Type 2 | MPS VI | MPS I | Gaucher Disease, Type 3 | MPS II | Mps VIIUnited States
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Rigshospitalet, DenmarkCompleted
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Centre Hospitalier Universitaire de NiceCompletedPompe's DiseaseFrance
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Istanbul UniversityBiruni UniversityNot yet recruitingLipid Storage DiseaseTurkey
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Taipei Medical University HospitalRecruiting
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University Hospital, CaenWithdrawn
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Ultragenyx Pharmaceutical IncTerminatedGlycogen Storage Disease Type IIIUnited States, Spain, Italy
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Nantes University HospitalCompleted
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Ostfold Hospital TrustVestre Viken Hospital Trust; Oslo University Hospital; Helse Stavanger HF; Sykehuset...Completed
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BiogenCompleted
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Johns Hopkins UniversityWalter Reed Army Medical CenterCompleted
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GAAD Medical Research Institute Inc.Unknown
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National Institute of Dental and Craniofacial Research...Completed
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China Academy of Chinese Medical SciencesWangjing Hospital, China Academy of Chinese Medical SciencesUnknown
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Nantes University HospitalCompleted
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Saint Bernard Mission UniversityUnknown
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Regeneron PharmaceuticalsSanofiCompleted
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The Back Research Center, DenmarkCompleted
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Prince Sattam Bin Abdulaziz UniversityCompleted
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Medtronic Spinal and BiologicsCompletedBack Pain | SciaticaSwitzerland, Belgium, Czech Republic, Germany, Italy, Poland, Spain, United Kingdom
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SanofiCompletedPompe Disease | Mucopolysaccharidosis Type I (MPS I)Italy
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Rigshospitalet, DenmarkUniversity College, LondonCompletedMcArdle DiseaseDenmark, United Kingdom
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Reneo Pharma LtdCompletedMcArdle DiseaseSpain, United Kingdom
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IRCCS Eugenio MedeaUniversity of Pisa; University of MessinaCompleted
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Rigshospitalet, DenmarkCompleted
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Nicoline LøkkenCompleted
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University College, LondonCompleted
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Eunice Kennedy Shriver National Institute of Child...RecruitingLysosomal Storage Disease | Cholesterol MetabolismUnited States
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Fondazione Don Carlo Gnocchi OnlusAssociazione Italiana Glicogenosi (AIG); Associazione Riabilitatori Insufficienza... and other collaboratorsRecruitingGlycogen Storage Disease Type II | Pompe Disease (Late-onset)Italy
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Joanne Kurtzberg, MDAldagenWithdrawnLysosomal Storage Diseases | Inborn Errors of MetabolismUnited States
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Rigshospitalet, DenmarkUltragenyx Pharmaceutical IncCompletedTarui Disease | Debrancher Deficiency | GYG1 DEFICIENCYDenmark
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Turkish Society of Pediatric Gastroenterology,...CompletedDuchenne Muscular Dystrophy | Pompe Disease (Late-onset)Turkey
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Brigham and Women's HospitalCompletedSciatica | RadiculopathyUnited States
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Johns Hopkins UniversityMilton S. Hershey Medical Center; United States Naval Medical Center, San Diego and other collaboratorsCompleted
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Rigshospitalet, DenmarkCompleted
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Institut National de la Santé Et de la Recherche...Rigshospitalet, DenmarkUnknownGlycogen Storage Disease Type V
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Massachusetts General HospitalCompleted
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National Institute of Dental and Craniofacial Research...Completed
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National Human Genome Research Institute (NHGRI)Enrolling by invitationParkinson Disease | Gaucher Disease | Lysosomal Storage DisordersUnited States
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University Hospital, GenevaCompleted
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Cairo UniversityKafrelsheikh UniversityCompleted
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University Hospital, GrenobleCompleted
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Kaiser PermanenteNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Completed