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Clinical Trials on Sickle Cell-Beta0-Thalassemia in United Kingdom
Total 744 results
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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Imara, Inc.Active, not recruitingSickle Cell DiseaseUnited States, United Kingdom
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Imperial College Healthcare NHS TrustImperial College LondonCompletedSickle Cell DiseaseUnited Kingdom
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Global Blood TherapeuticsCompleted
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Guy's and St Thomas' NHS Foundation TrustCompleted
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University College, LondonGuy's and St Thomas' NHS Foundation Trust; The Whittington Hospital NHS TrustUnknownSickle Cell DiseaseUnited Kingdom
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bluebird bioCompletedβ-thalassemia MajorUnited States, Australia, Thailand
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Memorial Sloan Kettering Cancer CenterActive, not recruitingConfirmed Diagnosis of ß-thalassemia MajorUnited States
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SangartWithdrawnSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | Hemoglobin SC Disease | Sickle Cell Disorders | Sickle Cell Hemoglobin C DiseaseFrance, United Kingdom, Netherlands, Turkey, Bahrain, Belgium, Brazil, Lebanon, Qatar
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Global Blood TherapeuticsCompletedSickle Cell Disease | Healthy SubjectsUnited Kingdom
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NHS Blood and TransplantUniversity of York; British Medical Research CouncilTerminatedSickle Cell DiseaseUnited Kingdom
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Ann & Robert H Lurie Children's Hospital of ChicagoUnknown
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Weill Medical College of Cornell UniversityUnknownThalassemia MajorUnited States
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St. Jude Children's Research HospitalCompletedSickle Cell Disease | Thalassemia | Marrow AplasiaUnited States
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King's College Hospital NHS TrustKing's College London; University College London Hospitals; University of Sheffield and other collaboratorsRecruitingSickle Cell DiseaseUnited Kingdom
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PfizerTerminatedSickle Cell DiseaseUnited Kingdom
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Baxalta now part of ShireTerminatedSickle Cell DiseaseUnited Kingdom
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DisperSol Technologies, LLCCompletedThalassemia MajorThailand, United States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedThalassemiaUnited States, Canada
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University of California, San FranciscoCalifornia Institute for Regenerative Medicine (CIRM)Enrolling by invitationHemoglobinopathies | Alpha Thalassemia Major | Thalassemia Major | Fetal Hydrops | Hemoglobinopathy; With Thalassemia | Fetal Anemia | Alpha; Thalassemia | Thalassemia Alpha | A-ThalassemiaUnited States
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Dana-Farber Cancer InstituteTehran University of Medical SciencesCompletedThalassemia MajorUnited States, Iran, Islamic Republic of
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States, United Kingdom, Germany
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Children's Hospital Los AngelesNational Heart, Lung, and Blood Institute (NHLBI); Vanderbilt University Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Healthy ControlsUnited States
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload in β-thalassemiaUnited States, Greece, Argentina, Germany, Belgium, Italy, United Kingdom, France, Tunisia, Canada, Turkey, Brazil
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London North West Healthcare NHS TrustMedical Research Council CTUTerminatedSickle Cell DiseaseUnited Kingdom
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedHematologic Diseases | Iron Overload | Hypertension, Pulmonary | Osteoporosis | Thalassemia | Beta-Thalassemia | Anemia, Cooley'sUnited States, Canada
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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Vanderbilt-Ingram Cancer CenterActive, not recruitingSickle Cell Disease | HemoglobinopathiesUnited States, United Kingdom, France
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National Heart, Lung, and Blood Institute (NHLBI)Terminated
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Forma Therapeutics, Inc.Novo Nordisk A/SRecruitingSickle Cell DiseaseLebanon, Canada, Kenya, United Kingdom
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Guy's and St Thomas' NHS Foundation TrustLondon School of Hygiene and Tropical Medicine; King's College London; King's... and other collaboratorsUnknownPregnancy, High Risk | Sickle Cell Disease | Blood Transfusion ComplicationUnited Kingdom
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PfizerCompletedPhase 1 Sickle CellUnited States, United Kingdom, Belgium, Netherlands, Italy
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Novartis PharmaceuticalsCompletedAnemia | HemosiderosisUnited States, Germany, Belgium, United Kingdom, Italy, Canada, France
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UCSF Benioff Children's Hospital OaklandNovartis PharmaceuticalsCompletedTHALASSEMIA MAJORUnited States
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Phoenix Children's HospitalCompletedMyelodysplastic Syndromes | Vitamin D Deficiency | Pediatric Cancer | Aplastic Anemia | Stem Cell Transplant Complications | Sickle Cell Anemia in Children | Thalassemia in Children | Blood Disorder | Pediatric Acute Myeloid Leukemia | Pediatric Acute Lymphoid LeukemiaUnited States
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Stanford UniversityUniversity of Alabama at Birmingham; University of MinnesotaCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States
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Children's Hospital of PhiladelphiaAnn & Robert H Lurie Children's Hospital of Chicago; The Cooley's Anemia Foundation...CompletedThalassemia Major With Severe Transfusional Iron OverloadUnited States
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AstraZenecaCompletedInvestigation of Platelet Aggregation in Paediatric Patients With Sickle Cell DiseaseUnited States, Canada, United Kingdom, South Africa, Lebanon, Kenya
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Academisch Medisch Centrum - Universiteit van Amsterdam...University Medical Center Groningen; Erasmus Medical Center; Guy's and St Thomas... and other collaboratorsCompletedSickle Cell DiseaseBelgium, Netherlands, United Kingdom
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Children's Hospital of PhiladelphiaNational Heart, Lung, and Blood Institute (NHLBI); New York Blood CenterRecruiting
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UCSF Benioff Children's Hospital OaklandFood and Drug Administration (FDA)CompletedSickle Cell Disease | Pulmonary Hypertension | ThalassemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingObservational Study to Deeply Phenotype Major Organs in Sickle Cell Disease After Curative TherapiesMortality in Sickle Cell | Sickle Cell Cardiopulmonary Complications | Sickle Cell Organ Damage | Sickle Cell Life Expectancy and Risk Factors for Early Death | Sickle Cell Lung Disease and Sudden DeathUnited States
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AstraZenecaCompletedSickle Cell DiseaseBelgium, United Kingdom, Italy, Spain, Kenya, Lebanon
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National Institute of Diabetes and Digestive and...RecruitingSickle Cell Disease | Sickle Cell Anemia | Sickle Cell TraitUnited States
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Axcella Health, IncCompletedSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | To Assess the Safety and Tolerabiltiy of an Amino Acid Composition in Subjects With Sickle Cell Disease | Sickle Cell DisordersUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingSickle Cell Disease | Hemoglobinopathies | Hematological Diseases | Hydroxyurea Failure | Hydroxyurea IntoleranceUnited States, Italy, United Kingdom, Germany
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Novartis PharmaceuticalsCompletedSickle Cell AnemiaTurkey, United States, Germany, Canada, United Kingdom, Israel, South Africa
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle Cell TraitUnited States
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Boston Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)Completed
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell AnemiaUnited States