- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Single-Gene Defects in United States
Total 3350 results
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Lindner Center of HOPEUniversity of CincinnatiCompleted
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New York Glaucoma Research InstituteUnknownChronic Angle-closure GlaucomaUnited States
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Alcon ResearchCompleted
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HemoSonics LLCCompleted
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle Cell TraitUnited States
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Boston Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)Completed
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City of Hope Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Active, not recruitingSickle Cell Disease | Anemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Sickle Cell DisorderUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell AnemiaUnited States
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St. Jude Children's Research HospitalCompleted
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Encore Medical Inc.Bright Research Partners; Yale Cardiovascular Research GroupRecruitingPatent Foramen Ovale | Cryptogenic StrokeUnited States
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Northeastern State UniversityActive, not recruitingOcular Hypertension | Primary Open-Angle Glaucoma, Unspecified EyeUnited States
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Robert ShannonUniversity of California, Los Angeles; House Clinic, Inc.; Med-El CorporationUnknown
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University of California, DavisRecruiting
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Alcon ResearchCompletedAngle-closure GlaucomaUnited States
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Michael WagnerEdgewood Oncology Inc.Not yet recruitingLiposarcoma | MDM2 Gene Amplification | Metastatic Liposarcoma | Unresectable Liposarcoma | Recurrent LiposarcomaUnited States
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Shirish M GadgeelAstraZeneca; Henry Ford Health SystemWithdrawnLung Cancer | Non-small Cell Lung Cancer | PD-L1 Gene Mutation | KRAS Activating MutationUnited States
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AllerganCompletedOcular Hypertension | Open-Angle GlaucomaUnited States
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Alcon ResearchCompletedOcular Hypertension | Open-angle GlaucomaUnited States
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Alcon ResearchCompletedOpen-Angle GlaucomaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingSickle Cell Disease | Sickle Cell Disorders | Hb-SS Disease | Hemoglobin S | Disease Sickle Cell Anemia | Hemoglobin Beta Thalassemia DiseaseUnited States
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Albert Einstein College of MedicineCompleted
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UConn HealthActive, not recruitingSickle Cell Disease | Sickle Cell TraitUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...National Cancer Institute (NCI)TerminatedSickle Cell DiseaseUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell AnemiaUnited States
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Dana-Farber Cancer InstituteMerck Sharp & Dohme LLC; Boston Children's Hospital; Brigham and Women's HospitalTerminatedSickle Cell Disease | Sickle Cell AnemiaUnited States
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Abbott Medical DevicesRecruitingStroke | Patent Foramen OvaleUnited States, Germany, Canada, Switzerland, Italy, Portugal, United Kingdom
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Shetty-Kim Research FoundationUnknownArticular Cartilage DefectUnited Kingdom
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Center for International Blood and Marrow Transplant...RecruitingSolid Tumors | Gene Therapy | Allogeneic Stem Cell Transplantation | Autologous Stem Cell Transplantation | Blood Cancers | Non-malignant Disease | CAR-TUnited States
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Glaukos CorporationCompletedPrimary Open-angle GlaucomaUnited States
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Bp Consulting, IncCompleted
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Johns Hopkins UniversityNational Institute on Drug Abuse (NIDA)Completed
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Alcon ResearchCompletedOcular Hypertension | Open-angle GlaucomaUnited States
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Alcon ResearchTerminatedOcular Hypertension | Open-Angle GlaucomaUnited States
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Alcon ResearchCompletedOcular Hypertension | Open-Angle GlaucomaUnited States
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Baylor College of MedicinePfizerCompletedSickle Cell Disease | Sickle Cell Anemia | Hemoglobin DisorderUnited States
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Valley Anesthesiology ConsultantsPhoenix Children's HospitalTerminatedSickle Cell Disease | Sickle Cell Crisis | Vaso-Occlusive CrisesUnited States
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Alessandra BiffiCompletedSickle Cell Disease Without CrisisUnited States
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Brigham and Women's HospitalActive, not recruiting
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Boston Children's HospitalNational Institute on Alcohol Abuse and Alcoholism (NIAAA)CompletedPrevention Harmful EffectsUnited States
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University of FloridaNational Human Genome Research Institute (NHGRI)RecruitingSickle Cell Disease | Sickle Cell TraitUnited States
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Children's Hospital of PhiladelphiaNational Heart, Lung, and Blood Institute (NHLBI); New York Blood CenterRecruiting
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University of PittsburghRecruitingSickle Cell DiseaseUnited States
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Children's Hospital Medical Center, CincinnatiUniversity of Colorado, Denver; Children's Hospital of Philadelphia; Duke University and other collaboratorsRecruitingSickle Cell Disease | Sickle Cell AnemiaUnited States
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Case Comprehensive Cancer CenterCompletedSickle Cell Disease | Sickle Cell Anemia | SCDUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Disease | Sickle Cell AnemiaUnited States
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BloodworksUniversity of WashingtonCompletedSickle Cell Disease | Sickle Cell AnemiaUnited States
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Icahn School of Medicine at Mount SinaiMassachusetts General Hospital; National Institute of Neurological Disorders...RecruitingParkinson Disease | GBA Gene Mutation | LRRK2United States
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Medipost Co Ltd.CompletedDegeneration Articular Cartilage KneeUnited States
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ShireCompletedOcular Hypertension | Primary Open-angle Glaucoma (POAG)United States
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John P. Hussman Institute for Human GenomicsUniversity of MiamiUnknown