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Clinical Trials on Spinal Muscular Atrophy (SMA)
Total 2764 results
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TakedaAstraZenecaRecruitingMultiple System AtrophySpain, Germany, United States, Italy, United Kingdom, Austria, Denmark, France, Japan, Portugal
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Mayo ClinicRecruiting
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Alterity TherapeuticsRecruitingMultiple System AtrophyUnited States, Australia, New Zealand, United Kingdom, Italy, France, Austria
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Corestem, Inc.CompletedMultiple System AtrophyKorea, Republic of
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University Hospital, BordeauxCompletedMultiple System AtrophyFrance
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Affiris AGInstitut National de la Santé Et de la Recherche Médicale, France; University... and other collaboratorsCompletedNeurodegenerative Diseases | Multiple System AtrophyFrance
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University of Massachusetts, WorcesterCompletedMultiple System AtrophyUnited States
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Phillip LowNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt... and other collaboratorsTerminated
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University Hospital, ToulouseFondation de FranceCompletedMultiple System Atrophy | Pain ThresholdFrance
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Quark PharmaceuticalsCompletedOptic Atrophy | Non-arteritic Anterior Ischemic Optic NeuropathyUnited States, Israel
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Korea University Ansan HospitalRecruitingSepsis | Shock | Trauma | Cardiac Arrest | Acute Respiratory Failure | Patients Who Visit Emergency DepartmentKorea, Republic of
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TheratechnologiesTerminatedChronic Obstructive Pulmonary Disease (COPD)
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University of California, Los AngelesActive, not recruitingSpinocerebellar Ataxias | Spinocerebellar Ataxia 3 | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | MSA-CUnited States
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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Muhammad Haroon AnwarPakistan Institute of Medical SciencesRecruitingHypotension | Spinal Anesthetics Causing Adverse Effects in Therapeutic Use | Hypotension on InductionPakistan
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...CompletedBody Weight Changes | Sarcopenia | Prader Labhart Willi SyndromeTaiwan
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Changhua Christian HospitalCompletedStroke | Cancer | Chronic Kidney Diseases | OsteoporosisTaiwan
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Medical University InnsbruckRecruiting
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University Hospital, BordeauxInstitut National de Recherche en Informatique et en AutomatiqueRecruitingParkinson Disease | Multiple System AtrophyFrance
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University Hospital, ToulouseCompletedMultiple System AtrophyFrance
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Universidad de AlmeriaCompletedNeurologic Disorder | Pediatric Disorder | Duchenne | Sensorimotor Disorder NosSpain
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Hacettepe UniversitySuleyman Demirel UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Posture Disorders in Children | Ambulation Disorder, NeurologicTurkey
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McMaster UniversityNot yet recruiting
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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Fondazione Serena Onlus - Centro Clinico NeMO MilanoAzienda Ospedaliera Città della Salute e della Scienza di Torino; Fondazione... and other collaboratorsActive, not recruiting
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Centre Hospitalier Universitaire de NiceWithdrawn
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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AMO Pharma LimitedCompletedMyotonic Dystrophy 1United Kingdom
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State University of New York at BuffaloSuspendedCognitive Impairment | Cardiovascular Abnormalities | Spinal Cord Injuries | Cerebrovascular Disease; SequelaeUnited States
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Wake Forest University Health SciencesCompletedHeart Diseases | Spinal Cord InjuriesUnited States
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Rigshospitalet, DenmarkRecruitingCerebral Palsy | Muscular DystrophiesDenmark
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Ophthalmos Research and Education InstituteCompletedStargardt Disease 1 | Dry AMDFrance, Germany, Italy
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Lupin Ltd.Recruiting
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Lupin Ltd.Active, not recruitingMyotonic DystrophyFrance, Germany, United Kingdom
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University of NancyCentral Hospital, Nancy, FranceCompleted
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University of VersaillesAssistance Publique - Hôpitaux de Paris; Association Française contre les Myopathies...Completed
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisCompletedMuscular Dystrophy, OculopharyngealFrance
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Hillel Yaffe Medical CenterUnknown
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...RecruitingMetabolic Syndrome | Sarcopenia | Prader-Willi SyndromeTaiwan
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Institut Català d'OncologiaDepartment of Health, Generalitat de CatalunyaRecruitingSarcopenia | Head and Neck Small Cell CarcinomaSpain
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University Hospital, Clermont-FerrandM2iSH laboratory; Benoit ChassaingUnknownColorectal Neoplasms | Metabolic Syndrome | Sarcopenia | Microbiota | PrognosisFrance
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University Hospital, BordeauxRecruitingMultiple System AtrophyFrance
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Peter NovakCompletedParkinson Disease | Multiple System AtrophyUnited States
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China Medical University HospitalMinistry of Science and Technology, TaiwanUnknownParkinson's Disease | Multiple System AtrophyTaiwan
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ARTHEx Biotech S.L.Recruiting
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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Istituto Auxologico ItalianoFondazione Serena Onlus - Centro Clinico NeMO MilanoCompletedMyotonic Dystrophy 1Italy
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Poitiers University HospitalTerminated
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy (HIBM)United States
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National Institute of Nursing Research (NINR)CompletedCerebral Palsy | Neuromuscular DiseaseUnited States