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Clinical Trials on Still Disease, Juvenile Onset
Total 1260 results
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Ankara UniversityCompletedVery Low Birth Weight Infants | Necrotising Enterocolitis | Late Onset Neonatal SepsisTurkey
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Emma Marie Caroline SlackUniversity of Zurich; University Children's Hospital, ZurichCompletedLate-Onset Neonatal Sepsis | Necrotising EnterocolitisSwitzerland
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Groupe Francophone des MyelodysplasiesAstex Pharmaceuticals, Inc.Completed
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University of UtahGenzyme, a Sanofi CompanyTerminatedCancer | Chronic Myelomonocytic LeukemiaUnited States
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Rigshospitalet, DenmarkOdense University Hospital; University of Copenhagen; Imperial College London; University... and other collaboratorsActive, not recruitingMyelodysplastic Syndromes | Cytopenia | Chronic Myelomonocytic Leukemia-1Denmark, United States
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H. Lee Moffitt Cancer Center and Research InstitutePfizerCompletedChronic Myelomonocytic Leukemia (CMML) | Myelodysplastic Syndrome (MDS)United States
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GeneCradle IncRecruitingPompe Disease (Late-onset)China
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GeneCradle IncRecruitingPompe Disease Infantile-OnsetChina
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRecruiting
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknownPompe Disease | Late Onset Pompe DiseaseSpain
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Groupe Francophone des MyelodysplasiesAbbVieRecruitingChronic Myeloid LeukemiaFrance
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Kirby InstituteCelgeneCompletedAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic LeukemiaAustralia
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PfizerCompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Myelodysplastic SyndromeSpain, Canada, Austria, Czechia, France, Hungary, Italy, Japan, Mexico, Poland, United Kingdom
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Sensei Biotherapeutics, Inc.WithdrawnMyelodysplastic Syndromes | Chronic Myelomonocytic Leukemia (CMML)
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Sidney Kimmel Comprehensive Cancer Center at Johns...Genzyme, a Sanofi CompanyTerminatedAcute Myeloid Leukemia | Myeloproliferative Disorders | Myelofibrosis | Chronic Myelomonocytic Leukemia | Juvenile Myelomonocytic Leukemia | Acute Leukemia | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Promyelocytic Leukemia | Chronic Myelogenous LeukemiaUnited States, Canada
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Treadwell Therapeutics, IncRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | AML | MDS | CMMLHong Kong, United States, Canada
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AbbVie (prior sponsor, Abbott)CompletedEnthesitis Related Arthritis (ERA)
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Stemline Therapeutics, Inc.CompletedMyelofibrosis | Chronic Myelomonocytic LeukemiaUnited States, Canada
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University College DublinWellcome Trust; Health Research Board, Ireland; National Maternity Hospital,... and other collaboratorsRecruitingLate-Onset Neonatal Sepsis | Necrotising Enterocolitis | Culture Negative Neonatal SepsisIreland
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M.D. Anderson Cancer CenterGenentech, Inc.; Astex Pharmaceuticals, Inc.RecruitingChronic Myelomonocytic Leukemia | Myelodysplastic SyndromeUnited States
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National Cancer Institute (NCI)Active, not recruitingAnemia | Chronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | de Novo Myelodysplastic SyndromeUnited States
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Heinrich-Heine University, DuesseldorfKoordinierungszentrum für Klinische Studien - DuesseldorfRecruitingMyelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | Secondary Acute Myeloid LeukemiaGermany
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Mayo ClinicRecruitingRecurrent Chronic Myelomonocytic Leukemia | Refractory Chronic Myelomonocytic LeukemiaUnited States
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Astex Pharmaceuticals, Inc.Enrolling by invitationAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic LeukemiaUnited States, Spain, Canada, Austria, Slovakia, Bulgaria, Hungary
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Arbeitsgemeinschaft medikamentoese TumortherapieCompletedAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic LeukemiaAustria, Croatia
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PfizerCompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Myelodysplastic SyndromeUnited States, United Kingdom, Belgium, Canada, Germany, France
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Heinrich-Heine University, DuesseldorfCelgene Corporation; Koordinierungszentrum für Klinische Studien DüsseldorfActive, not recruitingMyelodysplastic Syndromes | Leukemia, Myeloid, Acute | Chronic Myelomonocytic Leukemia | IDH2 Gene Mutation | IDH2 R172 | IDH2 R140Germany
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Duke UniversityCompleted
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom, Germany, France, Italy, Portugal, Belgium, Netherlands
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Seagen Inc.CompletedAcute Myeloid Leukemia | Myeloproliferative Disorders | Chronic Myelomonocytic Leukemia | Myelodysplastic SyndromeUnited States
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Huashan HospitalNot yet recruitingPompe Disease (Late-onset)China
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Rambam Health Care CampusRecruitingPompe Disease Infantile-OnsetIsrael
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Duke UniversityGenzyme, a Sanofi CompanyActive, not recruitingPompe Disease (Late-onset) | Pompe Disease | GAA DeficiencyUnited States
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Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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Odense University HospitalUnknownAdult Onset Growth Hormone DeficiencyDenmark
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Yanbing LiNot yet recruitingEfficacy and Safety of Chiglitazar Sodium in the Treatment of T2DM Patients | Metformin Combined With Insulin Glargine in the Treatment of Type 2 Diabetes Patients Who Still Have Poor Hypoglycemic Effect | 128 Patients Were Randomly Assigned 1:1 | Metformin and Insulin Glargine Combined... and other conditionsChina
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Karen Ballen, MDRecruitingAcute Myeloid Leukemia | Myelofibrosis | Chronic Myelomonocytic LeukemiaUnited States
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University Hospital, LilleCompletedLewy Body Disease | Frontotemporal Lobar Degeneration | Alzheimer Disease, Early OnsetFrance
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Otsuka Australia Pharmaceutical Pty LtdRecruitingMyelodysplastic Syndromes | Leukemia, Myeloid, Acute | Leukemia, Myelomonocytic, Chronic | Patient PreferenceNew Zealand, Australia
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Clinical Hub for Interventional Research (CHOIR)The University of New South Wales; Australian National UniversityRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic LeukemiaAustralia
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Ascentage Pharma Group Inc.RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic Leukemia | AML | MDS | CMML | High-risk Myelodysplastic SyndromeUnited States