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Clinical Trials on Trientine Treatment for Wilson's Disease in Argentina
Total 277 results
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Latin American Cooperative Oncology GroupGlaxoSmithKlineCompletedBRMS1 | Performance Status Zero to Two for Beginning the Study | Patient With a Maximum of One Chemotherapy | Patient With Progression After TaxanesArgentina, Brazil, Peru
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The Foundation for Orthopaedics and Regenerative...RecruitingGlaucoma | Eye Diseases | Macular Degeneration | Diabetic Retinopathy | Retinitis Pigmentosa | Optic Atrophy | Traumatic Optic NeuropathyAntigua and Barbuda, Argentina, Mexico
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Tulane University School of Public Health and Tropical...University of Zambia; Kinshasa School of Public Health; Instituto de Efectividad...CompletedCongenital SyphilisUnited States, Congo, The Democratic Republic of the, Argentina, Zambia
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CENTOGENE GmbH RostockCompletedFabry Disease | Anderson-Fabry Disease | Fabry´s DiseaseArgentina, Belgium, Croatia, Czechia, Denmark, France, Germany, United Kingdom
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Pontificia Universidad Catolica de ChileUnknownRespiratory Distress SyndromeArgentina, Chile, Paraguay, Peru, Uruguay
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Janssen Research & Development, LLCTerminatedDermatitis, AtopicUnited States, Argentina
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IpsenActive, not recruitingFibrodysplasia Ossificans Progressiva (FOP)United States, France, Australia, Argentina, Italy, Canada, Sweden, United Kingdom, Brazil, Spain
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PfizerCompletedFamilial Amyloid Polyneuropathy | ATTR-PNSweden, Brazil, Germany, Argentina, France, Portugal
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Bordeaux Colorectal Institute AcademyRecruitingColorectal Surgery | Benign or Malignant Rectal or Colon TumorsFrance, Switzerland, Argentina, Belgium, Germany, Italy, Netherlands, Spain, United Kingdom
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PharmaxisCompleted
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Windtree TherapeuticsCompletedCOVID-19 | Acute Lung Injury/Acute Respiratory Distress Syndrome (ARDS)United States, Argentina
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Baxalta now part of ShireCompletedHemophilia BColombia, Bulgaria, Chile, Poland, Romania, Argentina, Czechia, Russian Federation, Ukraine, United Kingdom
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IgenomixRecruitingInfertility | Aneuploidy | Chromosome AbnormalityFrance, Argentina, Spain, United States, Brazil, Italy
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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ShireCompletedSanfilippo SyndromeUnited States, Spain, United Kingdom, Argentina, France, Germany, Italy, Netherlands
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis (MPS)United States, Argentina, Mexico, Spain, United Kingdom
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Novartis PharmaceuticalsTerminatedGouty ArthritisChina, Poland, Singapore, Argentina
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Debiopharm International SARecruitingBone or Joint InfectionUnited States, Ukraine, Argentina, South Africa, Georgia
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IgenomixCompletedInfertility | Aneuploidy | Chromosome AbnormalityMexico, Turkey, United States, Argentina, Spain, Brazil, Italy, Peru
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Baxalta now part of ShireCompletedHemophilia BColombia, Bulgaria, Chile, Poland, Romania, Argentina, Brazil, Czechia, Russian Federation, Ukraine
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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Insmed IncorporatedCompletedLaron Syndrome | Growth Hormone Insensitivity Syndrome (GHIS)United States, Argentina, Australia, Brazil, China, Egypt, Germany, Israel, Italy, Norway, Peru, Slovakia, Turkey, United Kingdom
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Allievex CorporationActive, not recruitingMucopolysaccharidosis Type IIIBUnited States, Germany, Spain, Argentina, Australia, Brazil, Colombia, Taiwan, Turkey
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IV A | Mucopolysaccharidosis IVAFrance, United Kingdom, Taiwan, United States, Argentina, Netherlands, Canada, Brazil, Germany, Italy
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Enzyvant Therapeutics GmBHCompletedFarber Disease | Farber's Disease | Farber Lipogranulomatosis | Acid Ceramidase Deficiency | Ceramidase Deficiency | N-Laurylsphingosine Deacylase Deficiency | ASAH1 MutationUnited States, Egypt, Canada, Italy, Turkey, Argentina, Germany, India, Sweden
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Hoffmann-La RocheCompletedDown SyndromeUnited States, France, Italy, Canada, United Kingdom, Argentina, Spain
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Turner SyndromeArgentina, Australia, Austria, Canada, France, Germany, Italy, Norway, Russian Federation, Singapore, Spain, Sweden, United Kingdom
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Christian Medical College, Vellore, IndiaUnknownHemophiliaIndia, Argentina, Brazil, Egypt, Iran, Islamic Republic of, Singapore, South Africa, Thailand, Venezuela
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Philip MoonsCompletedHeart Defects, CongenitalNorway, Taiwan, Belgium, Netherlands, United States, Sweden, Switzerland, Canada, Argentina, Australia, France, India, Italy, Japan, Malta
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SanofiRecruitingGaucher's Disease Type IIIUnited States, Germany, Hungary, France, China, Japan, Canada, Argentina, Italy, Turkey
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, Poland, Netherlands, Canada, Argentina, United Kingdom, Norway, Brazil, Czech Republic
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Hoffmann-La RocheCompletedJuvenile Idiopathic ArthritisCanada, Mexico, United States, Argentina, Germany, Israel, Italy, Russian Federation, Spain, United Kingdom
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Noonan Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Adult Growth Hormone Deficiency | Genetic Disorder | Foetal Growth Problem | Small for Gestational AgeIsrael, Saudi Arabia, Spain, Argentina, Russian Federation, Germany, Netherlands, Italy, Belgium, United Kingdom, Slovenia, Ireland, Sweden, Denmark, Hungary, Finland, Norway, France, Czechia, Lithuania, Luxembourg, Serbia, Switzerland
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ShireTerminatedMetabolic Diseases | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Demyelinating Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Lysosomal Storage Diseases | Lipid Metabolism Disorders | Sphingolipidoses | Hereditary Central Nervous System Demyelinating Diseases and other conditionsUnited States, Denmark, France, Argentina, Belgium, Brazil, Canada, Germany, Japan, Turkey
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Incyte CorporationRecruitingFibrodysplasia Ossificans Progressiva (FOP)United States, France, Korea, Republic of, Spain, Italy, United Kingdom, Russian Federation, China, Australia, Brazil, Mexico, New Zealand, Argentina, Canada, Netherlands, Turkey, Chile, Germany, South Africa, Portugal
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Baxalta now part of ShireCompletedHemophilia BPoland, United Kingdom, Spain, Bulgaria, Romania, Japan, Russian Federation, Brazil, Chile, Sweden, Colombia, Ukraine, Argentina, Czechia
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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NYU Langone HealthWithdrawnSarcoma | Brain and Central Nervous System Tumors | Neuroblastoma | RetinoblastomaUnited States, Canada, Argentina
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Spain, Canada, New Zealand, Argentina, Mexico, Singapore
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Unity Health TorontoCanadian Institutes of Health Research (CIHR); University of Toronto; Applied...RecruitingARDSFrance, Canada, Chile, Italy, Argentina, Spain, United States
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SanofiActive, not recruitingGaucher's Disease Type III | Gaucher's Disease Type ICanada, Argentina, France, Italy, Japan, Russian Federation, Spain, Sweden, Turkey, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A | Haemophilia BBelgium, Germany, France, United Kingdom, Italy, Hungary, Austria, Sweden, Iran, Islamic Republic of, Argentina, Ireland, Poland, Portugal, Slovakia
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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PfizerCompletedFamilial Amyloid PolyneuropathyUnited Kingdom, Spain, United States, Argentina, Brazil, France, Germany, Portugal, Sweden
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsSlovakia, Spain, Argentina, Germany, Croatia, Italy, Canada, United Kingdom, Ireland, Sweden, France, United States, Czech Republic, Switzerland