- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Urea Cycle Disorders, Inborn
Total 7042 results
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Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedFamilial HypercholesterolemiaUnited States, Spain, Turkey, Canada, Belgium, Germany, Greece, Hungary, Italy, Norway, Poland, Puerto Rico, Russian Federation, Slovakia, Switzerland
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University of PennsylvaniaCompletedHypercholesterolemia, FamilialUnited States
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University of NottinghamUniversity College, London; Newcastle University; University of ManchesterUnknownFamilial HypercholesterolemiaUnited Kingdom
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ShionogiIntegriumCompletedCombined HyperlipidemiaUnited States
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China Cardiovascular AssociationAmgenUnknownFamilial HypercholesterolemiaChina
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Isfahan University of Medical SciencesUnknownFamilial HypercholesterolemiaIran, Islamic Republic of
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Emory UniversityKaneka Medical America LLCCompletedFamilial HypercholesterolemiaUnited States
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TakedaTerminatedHypercholesterolemiaFrance, United Kingdom, United States, Israel, Poland, Canada
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AstraZenecaCompletedFamilial HypercholesterolemiaUnited States, Spain, Netherlands, Norway, Canada
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AstraZenecaCompleted
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Medical University of ViennaUnknown
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University of TehranCompletedHypercholesterolemia, FamilialIran, Islamic Republic of
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Medical Research Laboratories InternationalTerminatedFamilial HypercholesterolemiaIsrael, Netherlands, United States, Canada, Norway
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Isfahan University of Medical SciencesCompletedTangier Disease | Body Mass Index Quantitative Trait Locus 7 DisorderIran, Islamic Republic of
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Neurogene Inc.RecruitingCeroid Lipofuscinosis, Neuronal 5United States
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University of Wisconsin, MadisonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Stanford...Recruiting
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaCzechia, France, Denmark, Netherlands, Austria, Mexico, Spain, United States, Argentina, Brazil, Bulgaria, Canada, Finland, Hungary, Italy, Lebanon, Norway, Poland, Russian Federation, Slovenia, South Africa, Sweden, Taiwan, Turkey
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University of Texas Southwestern Medical CenterCompletedHypertriglyceridemia | Hyperlipoproteinemia Type IUnited States
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedHypertriglyceridemia | Familial HypercholesterolemiaCanada
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NeuroBo Pharmaceuticals Inc.CompletedHypercholesteremiaUnited States, Canada, Israel
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNorway, Russian Federation, Sweden, South Africa, Czechia, United States, Canada, France, Netherlands, Spain
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNetherlands, United States, Canada, Russian Federation, South Africa
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University of OsloOslo University Hospital; Mills DACompletedHealthy | Familial HypercholesterolemiaNorway
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Cortria CorporationMontreal Heart InstituteCompletedHypertriglyceridemia | Mixed HyperlipidemiaCanada
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Federico II UniversityCompletedDyslipidemia | Familial Hypercholesterolemia
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LipomedCompletedHemochromatosisEgypt, Turkey
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University of IoanninaUnknown
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National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde | Dehydrogenase Deficiency | DiseasesUnited States
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National Human Genome Research Institute (NHGRI)CompletedUndiagnosed Disease | Healthy Volunteer (Adult With Typically Developing Child) | Inherited Neurodegenerative Disorders | Inherited Metabolic Disorders (Inborn Errors of Metabolism) | Alzheimer's Disease and Related DementiasUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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University of ZurichCompletedFabry DiseaseSwitzerland
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Pamlab, Inc.Clionsky Neuro Systems Inc.UnknownMild Cognitive ImpairmentUnited States
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Aevi Genomic Medicine, LLC, a Cerecor companyCompletedAttention Deficit Disorder With HyperactivityUnited States
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AmgenCompletedHyperlipidemiaCanada, France, Netherlands, United Kingdom, New Zealand, South Africa, Spain, United States, Australia, Germany, Sweden, Hong Kong, Switzerland, Norway
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UniQure Biopharma B.V.Chiesi Farmaceutici S.p.A.Withdrawn
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialUnited States, Canada, South Africa, Czech Republic, Italy, Finland, Netherlands, France
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Dr. Reddy's Laboratories LimitedPharmaNetCompletedType II HyperlipidemiaUkraine, Poland, Italy
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LipomedCompleted
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Akros Pharma Inc.CompletedType II HyperlipidemiaNetherlands
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialAustralia, Canada, United States, France, South Africa, Sweden, Norway, Denmark, Iceland
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In His ImageKos PharmaceuticalsCompletedDyslipidemia | Hyperlipidemia | Mixed HyperlipidemiaUnited States
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Emily de los ReyesRecruitingBatten Disease | CLN6United States
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StemCells, Inc.WithdrawnNeuronal Ceroid LipofuscinosisUnited States
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Canada, Brazil, Taiwan, Singapore, South Africa, United Kingdom
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Taiwan, Brazil, Canada, South Africa, United Kingdom, Singapore
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Region StockholmKarolinska InstitutetRecruitingBipolar Disorder | Bipolar Depression | Bipolar I Disorder | Bipolar II Disorder | Bipolar Affective Disorder; Remission in | Bipolar Affective Disorder, Currently Depressed, ModerateSweden
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States
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Isfahan University of Medical SciencesCompletedTangier Disease | Body Mass Index Quantitative Trait Locus 5 DisorderIran, Islamic Republic of
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IRCCS Fondazione Stella MarisCompletedNeuronal Ceroid-LipofuscinosesItaly
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TRPHARMKlinar CRO; Düzen Laboratories GroupTerminatedCTX - Cerebrotendinous XanthomatosisTurkey