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Clinical Trials on Urea Cycle Disorders, Inborn
Total 7042 results
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Organon and CoCompletedHypercholesterolemia | Heterozygous Familial Hypercholesterolemia
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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Travere Therapeutics, Inc.UnknownCerebrotendinous Xanthomatosis (CTX)United States
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Austrian Academic Institute for Clinical NutritionMedical University of ViennaCompletedHeterozygous Familial HypercholesterolemiaAustria
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Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
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Merck Sharp & Dohme LLCCompletedHeterozygous Familial Hypercholesterolemia (HeFH)
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Mayo ClinicCompletedHemochromatosisUnited States
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Merck Sharp & Dohme LLCTerminatedHypercholesterolemia | Mixed Hyperlipemia
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Cerenis Therapeutics, SACompleted
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National Center for Research Resources (NCRR)University of PennsylvaniaCompletedFamilial Hypercholesterolemia
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late-Infantile Neuronal Ceroid Lipfuscinosis
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The Hospital for Sick ChildrenTerminatedMetabolic Disease | Genetic Disorder | MalignancyCanada
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National Human Genome Research Institute (NHGRI)RecruitingCongenital Disorders of GlycosylationUnited States
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Russian Cardiology Research and Production CenterPfizer; AstraZeneca; AmgenRecruitingFamilial HypercholesterolemiaRussian Federation
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Amryt PharmaRecruitingHomozygous Familial HypercholesterolemiaItaly, United States, Argentina, Canada, France, Greece, Netherlands, United Kingdom
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LIB Therapeutics LLCMedpace, Inc.CompletedHeterozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey
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Innovent Biologics (Suzhou) Co. Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Australia, Austria, Netherlands, Taiwan, Ukraine
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Novartis PharmaceuticalsCompletedA Study of Inclisiran in Participants With Homozygous Familial Hypercholesterolemia (HoFH) (ORION-5)Homozygous Familial HypercholesterolemiaHong Kong, Israel, Russian Federation, Serbia, South Africa, Taiwan, Turkey, Ukraine
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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Organon and CoTerminatedLipid Metabolism, Inborn Errors | Hypercholesterolemia, Familial
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Korea United Pharm. Inc.Active, not recruiting
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Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedPediatric Heterozygous HypercholesterolemiaGreece, Norway, Canada
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AmgenCompletedHomozygous Familial Hypercholesterolemia HoFHIndia
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Regeneron PharmaceuticalsSanofiCompletedHypercholesterolemia | Heterozygous Familial HypercholesterolemiaUnited States, Canada
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Regeneron PharmaceuticalsSanofiCompletedHeterozygous Familial HypercholesterolemiaUnited States, Germany
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Laval UniversityAmgenCompleted
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.WithdrawnHomozygous Familial HypercholesterolemiaCanada
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AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
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Aegerion Pharmaceuticals, Inc.CompletedFamilial Hypercholesterolemia - HomozygousJapan
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Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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PfizerCompletedHeterozygous Familial HypercholesterolemiaCanada, Netherlands, United Kingdom, United States, Spain, Poland, Finland, Norway, South Africa, Italy, Bulgaria
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Laval UniversityCompletedHomozygous Familial HypercholesterolemiaCanada
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Regeneron PharmaceuticalsSanofiCompletedHeterozygous Familial HypercholesterolemiaUnited Kingdom, Netherlands, Czech Republic, Norway
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Cerenis Therapeutics, SACompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Netherlands, United Kingdom
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Aegerion Pharmaceuticals, Inc.University of Pennsylvania; Doris Duke Charitable FoundationCompletedHomozygous Familial HypercholesterolemiaUnited States
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The University of Western AustraliaNational Health and Medical Research Council, AustraliaUnknownFamilial Hypercholesterolaemia | HypertriglyceridaemiaAustralia
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The Hospital for Sick ChildrenBioMarin PharmaceuticalCompletedPhenylketonuria | Mild HyperphenylalaninemiaCanada
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Novartis PharmaceuticalsRecruitingHypercholesterolaemia | Familial HypercholesterolaemiaJapan
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Imperial College LondonRecruitingFamilial HypercholesterolemiaUnited Kingdom
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University Hospital, LinkoepingRecruitingHypercholesterolemia, Familial | Clinical Decision SupportSweden
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Shanghai Junshi Bioscience Co., Ltd.CompletedHeterozygous Familial HypercholesterolemiaChina
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Brigham and Women's HospitalActive, not recruitingASCVD | Hyperlipemia, MixedUnited States
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Daniel GaudetUltragenyx Pharmaceutical IncActive, not recruitingSafety and Effectiveness of Evinacumab for the Treatment of Homozygous Familial HypercholesterolemiaHomozygous Familial HypercholesterolemiaCanada
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Innovent Biologics (Suzhou) Co. Ltd.Completed
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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Amryt PharmaActive, not recruitingHomozygous Familial Hypercholesterolaemia (HoFH)Germany, Israel, Italy, Saudi Arabia, Spain, Tunisia