Clinical Trials on Wiskott-Aldrich Syndrome

Total 34064 results

Stoke Therapeutics, Inc

Completed

An Open-Label Study to Investigate the Safety of Single and Multiple Ascending Doses in Children and Adolescents With Dravet Syndrome

Dravet Syndrome

United States
Fondazione Policlinico Universitario Agostino Gemelli...
IRCCS San Raffaele

Enrolling by invitation

EXploring novEl Molecular Determinants of DRAvet Syndrome Phenotype Heterogeneity (EXEDRA)

Dravet Syndrome

Italy
ORA, Inc.
Topivert Pharma Ltd

Completed

Safety and Efficacy of TOP1630 for Dry Eye Syndrome

Dry Eye Syndrome

United States
Zealand Pharma

Enrolling by invitation

Evaluation of Long Term Safety and Efficacy of Glepaglutide in Treatment of SBS - Extension Trial (EASE SBS 3)

Short Bowel Syndrome

Germany, United States, Belgium, Denmark, France, United Kingdom, Netherlands, Poland
Zogenix International Limited, Inc., a subsidiary...

Completed

An Open-Label Extension Trial to Assess the Long-Term Safety of ZX008 (Fenfluramine Hydrochloride HCl) Oral Solution in Children and Young Adults With Dravet Syndrome

Dravet Syndrome

United States, United Kingdom, Spain, Belgium, Italy, Australia, Denmark, Germany, Canada, Japan, Netherlands, France
Takeda

Completed

A Study With Teduglutide (Revestive®) in Adults With Short Bowl Syndrome (T-Rex)

Short Bowel Syndrome

Spain
University of Nebraska

Withdrawn

Pharmacokinetics of Citalopram in Patients With Short Bowel Syndrome

Short Bowel Syndrome

United States
Eastern Cooperative Oncology Group
National Cancer Institute (NCI)

Completed

Erythropoietin (EPO)+/- Filgrastim (G-CSF) vs. Supportive Therapy Alone for Patients With Myelodysplastic Syndromes

Myelodysplastic Syndromes | Anemia

United States
Shiraz University of Medical Sciences

Completed

Probiotic in Dry Eye Syndromes

Dry Eye Syndrome

Iran, Islamic Republic of
Takeda
Takeda

Completed

An Extension Study of Teduglutide in Japanese Participants With Short Bowel Syndrome Who Completed 24 Weeks of Treatment in SHP633-306 or TED-C14-004

Short Bowel Syndrome

Japan
SIFI SpA

Completed

A Non-inferiority Study of Eyestil® Plus Multidose Versus Vismed Multi® (047/SI)

Dry Eye Syndromes

France, Spain
9 Meters Biopharma, Inc.

Terminated

VIBRANT Study of Vurolenatide in Adult Patients With Short Bowel Syndrome.

Short Bowel Syndrome

United States
Aprea Therapeutics

Terminated

APR-548 in Combination With Azacitidine for the Treatment of TP53 Myelodysplastic Syndromes (MDS)

Myelodysplastic Syndromes | MDS

United States
Shire
Takeda

Completed

A Study in Japanese Children With Short Bowel Syndrome Who Completed SHP633-302

Short Bowel Syndrome

Japan
Celgene
Acceleron Pharma Inc. (a wholly owned subsidiary of Merck Sharp and Dohme...

Completed

A Study of Luspatercept (ACE-536) to Treat Anemia Due to Very Low, Low, or Intermediate Risk Myelodysplastic Syndromes (MEDALIST)

Myelodysplastic Syndromes

Canada, United States, Germany, Belgium, France, United Kingdom, Turkey, Spain, Italy, Netherlands, Sweden
Aurinia Pharmaceuticals Inc.

Completed

Dose Ranging Study to Assess the Efficacy and Safety of Voclosporin Ophthalmic Solution in Subjects With Dry Eye Syndrome (AUDREY)

Keratoconjunctivitis Sicca | Dry Eye Syndrome

United States
Kukje Pharma
Samil Pharmaceutical Co., Ltd.

Completed

[KSR-001-P02] Phase 2b/3 Study, Evaluate the Efficacy and Safety of KSR-001 in Patients With Dry Eye Syndrome

Dry Eye Syndromes

Korea, Republic of
Shire

Completed

Long-term Study of Teduglutide in Pediatric Subjects With Short Bowel Syndrome Who Completed the TED-C13-003 Study

Short Bowel Syndrome

United States, United Kingdom
Shire

Completed

A One-Year, Open-Label Study With Teduglutide for Subjects Who Completed Study CL0600-021 (STEPS3)

Short Bowel Syndrome

United States
Shire

Completed

Short Bowel Syndrome Research Study for Children Up To 17 Years of Age on Parenteral Nutrition

Short Bowel Syndrome

United States, Canada, Finland, Belgium, Italy, United Kingdom, Germany
Shire
Nycomed

Completed

Study of Teduglutide Effectiveness in Parenteral Nutrition (PN)-Dependent Short Bowel Syndrome (SBS) Subjects (STEPS)

Short Bowel Syndrome

United States, Spain, France, Canada, Netherlands, Denmark, Germany, Italy, Poland, United Kingdom
Shire

Completed

Safety, Efficacy and Pharmacokinetic Study of Teduglutide in Infants 4 to 12 Months of Age With Short Bowel Syndrome

Short Bowel Syndrome

Finland, Italy, United Kingdom, France
Medical University of Vienna

Completed

Teduglutide in Short Bowel Syndrome Patients

Short Bowel Syndrome
Gillette Children's Specialty Healthcare
Mayo Clinic; Dartmouth-Hitchcock Medical Center; Ann & Robert H Lurie Children...

Completed

Verapamil as Therapy for Children and Young Adults With Dravet Syndrome

Dravet Syndrome

United States
Qatar University
Hamad Medical Corporation; Weill Cornell Medical College in Qatar

Completed

Impact of a Pharmacist-delivered Discharge and Follow-up Intervention for Patients With Acute Coronary Syndromes in Qatar

Acute Coronary Syndromes

Qatar
Eleos, Inc.
H. Lee Moffitt Cancer Center and Research Institute

Terminated

A Study of Aezea® (Cenersen) in Transfusion Dependent Anemia Associated With Myelodysplastic Syndrome (MDS)

Myelodysplastic Syndromes

United States
Andalusian Initiative for Advanced Therapies -...

Unknown

Safety and Efficacy of Ticagrelor vs Clopidogrel in Patients With Acute Coronary Syndrome

Acute Coronary Syndromes

Spain
Shire

Completed

Study of Teduglutide in Japanese Participants With Short Bowel Syndrome

Short Bowel Syndrome

Japan
Jonsson Comprehensive Cancer Center
Celgene Corporation; CTI BioPharma

Terminated

Azacitidine and Arsenic Trioxide in Treating Patients With Myelodysplastic Syndromes

Myelodysplastic Syndromes | Leukemia

United States
University of California, Los Angeles

Available

Treatment of Dravet Syndrome With Fenfluramine (Expanded Access Protocol) (Dravet)

Dravet Syndrome

United States
Huons Co., Ltd.

Completed

HU007 Eye Drops in Patients With Dry Eye Syndrome

Dry Eye Syndromes

Korea, Republic of
Children's Hospital of Philadelphia
AbbVie

Completed

Use of Pancreatic Enzymes in Short Bowel Syndrome (SBS)

Short Bowel Syndrome

United States
Christopher Duggan

Completed

Measurement of Body Composition by Air Displacement Plethysmography in Pediatric Intestinal Failure Patients

Short Bowel Syndrome

United States
ReGenTree, LLC

Completed

Assessment of the Safety and Efficacy of RGN-259 Ophthalmic Solutions for Dry Eye Syndrome: ARISE-1

Dry Eye Syndrome

United States
Topivert Pharma Ltd

Completed

Study of TOP1630 for Dry Eye Syndrome (THEIA-1)

Dry Eye Syndrome

United States
Avizorex Pharma, S.L.

Unknown

Assessing the Safety and Efficacy of AVX-012 in Subjects With Mild-to-moderate Dry Eye Syndrome (AVX012CT001)

Dry Eye Syndrome

Spain
Seref istek
Usak State Hospital

Completed

The Comparison of 50% AS Versus PFAT+ 0.05 % COE in Severe Dry Eye Syndrome

Dry Eye Syndrome
J&M Shuler

Completed

Ability of Near Infrared Spectroscopy to Isolate Compartments of the Extremity

Acute Compartment Syndrome

United States
University of Texas Southwestern Medical Center
Advanced Vision Research

Completed

A Placebo Controlled Double Masked Clinical Assessment Study of Essential Fatty Acid Supplement and Its Effect on Patients With Apparent Aqueous Deficient Dry Eye Syndrome

Dry Eye Syndrome

United States
Yungjin Pharm. Co., Ltd.

Completed

Phase 2 Study to Evaluation the Safety and Efficacy of Orally Administered KL7016 in Patients With Dry Eye Syndrome

Dry Eye Syndrome

Korea, Republic of
Azienda Ospedaliero-Universitaria di Parma

Terminated

Pharmacogenetics of Clopidogrel in Acute Coronary Syndromes (PHARMCLO)

Acute Coronary Syndromes

Italy
Laboratoires Thea

Completed

Efficacy and Safety of T2762 and Vismed® in Dry Eye Syndrome

Dry Eye Syndrome

France
Laboratoires Thea

Terminated

Comparison of the Efficacy and Safety of T2762 Versus Optive® in the Treatment of Moderate to Severe Dry Eye Syndrome

Dry Eye Syndrome

France
Jinling Hospital, China
National Natural Science Foundation of China

Completed

The Preventative and Therapeutical Effect of Ursodeoxycholic Acid(UDCA) to Short Bowel Syndrome Patients

Short Bowel Syndrome

China
Mayo Clinic

Completed

Comparison of Different Oral Rehydration Solutions (ORS)

Short Bowel Syndrome

United States
DH Bio Co., Ltd.
BTO Pharm. Co., Ltd.

Completed

Efficacy and Safety Study of Haporine-S for Treatment of Moderate to Severe Dry Eye Syndromes

Dry Eye Syndromes

Korea, Republic of
Taejoon Pharmaceutical Co., Ltd.

Completed

Efficacy and Safety Study of TJCS for Treatment of Moderate to Severe Dry Eye Syndromes

Dry Eye Syndromes

Korea, Republic of
San Filippo Neri General Hospital
Associazione Nazionale Medici Cardiologi Ospedalieri

Unknown

Registry of Acute Coronary Syndromes in the Lazio Region of Italy (NET-SCA)

Acute Coronary Syndromes

Italy
M.D. Anderson Cancer Center
Novartis

Completed

Phase I Study of Gimatecan in Patients With Myelodysplastic Syndromes

Myelodysplastic Syndromes | MDS

United States
Children's Hospital of Michigan
Merck Sharp & Dohme LLC; Boston Children's Hospital; William Beaumont Hospitals

Completed

Safety and Immunogenicity of Rotavirus Vaccine (RotaTeq(R)) in Infants With Short Bowel Syndrome

Short Bowel Syndrome

United States

Clinical Trials on Wiskott-Aldrich Syndrome

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