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Clinical Trials on Woodhouse Sakati Syndrome
Total 34214 results
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LMU KlinikumSeventh Framework Programme; NBIA AllianceRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA) | Pantothenate Kinase-associated Neurodegeneration (PKAN) | Aceruloplasminemia | Beta-Propeller Protein-Associated Neurodegeneration (BPAN) | Mitochondrial Membrane Protein Associated Neurodegeneration (MPAN) | Fatty Acid Hydroxylase-associated... and other conditionsCanada, Czechia, Germany, Italy, Netherlands, Poland, Serbia, Spain
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Institut de Recherches Internationales ServierServier Bio-Innovation LLCNot yet recruitingMyelodysplastic Syndromes (MDS) | Hypomethylating Agent (HMA) Naive Myelodysplastic Syndromes (MDS)
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TJ Biopharma Co., Ltd.Recruiting
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI)RecruitingMyelodysplastic Syndromes (MDS)United States, Israel
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndromes (MDS)United States, Australia, Canada, France, Germany, Italy, United Kingdom
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AbbVieCelgene; Genentech, Inc.CompletedMyelodysplastic Syndromes (MDS)United States, Australia, Germany
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The First Affiliated Hospital with Nanjing Medical...UnknownMyelodysplastic Syndromes (MDS)China
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SCRI Development Innovations, LLCNovartis PharmaceuticalsTerminated
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PersImmune, IncUniversity of California, San DiegoUnknown
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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National Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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Benjamin TomlinsonRecruitingMyelodysplastic Syndromes | MDS/MPN Crossover SyndromesUnited States
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Ministry of Public Health, Democratic Republic...National Institutes of Health (NIH); Oregon Health and Science University; National... and other collaboratorsCompletedNeurotoxicity Syndrome, Cassava | Neurotoxicity Syndrome, Cyanate | Neurotoxicity Syndrome, Cyanide | Neurotoxicity Syndrome, ThiocyanateCongo, The Democratic Republic of the
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Dana-Farber Cancer InstituteCompletedMyelodysplastic Syndromes (MDS)United States
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Radboud University Medical CenterRecruitingMyelodysplastic Syndromes (MDS)Denmark, Switzerland, Serbia, Austria, Croatia, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Romania, Spain, Sweden, United Kingdom
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TakedaWithdrawn
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Prof. Janet DunnKing's College Hospital NHS Trust; University of Manchester; University of Birmingham and other collaboratorsRecruitingMyelodysplastic Syndromes (MDS)United Kingdom
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Aston UniversityNot yet recruitingDry Eye Syndromes | Computer Vision Syndrome
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AkesoRecruitingHigher-risk Myelodysplastic SyndromesUnited States, China
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Nuwacell Biotechnologies Co., Ltd.The First Affiliated Hospital of University of Science and Technology of...Not yet recruitingRelapsed / Refractory Myelodysplastic Syndromes
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
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The University of QueenslandRoyal Brisbane and Women's HospitalUnknown
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Navy General Hospital, BeijingNot yet recruitingHigher-risk Myelodysplastic SyndromesChina
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University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
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ALX Oncology Inc.Active, not recruitingHigher Risk Myelodysplastic SyndromesKorea, Republic of, United States, Spain
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Rigel PharmaceuticalsRecruitingLow Risk Myelodysplastic SyndromesUnited States
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Bristol-Myers SquibbActive, not recruitingLower-risk Myelodysplastic SyndromesJapan
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The University of Texas Health Science Center,...RecruitingNeuropsychiatric SyndromesUnited States
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Sumitomo Pharma America, Inc.TerminatedAnemia in Myelodysplastic SyndromesUnited States
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Groupe Francophone des MyelodysplasiesUnknownAnemia in Myelodysplastic SyndromesFrance
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Brian JonasNational Cancer Institute (NCI); Celgene; Pharmacyclics LLC.CompletedPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Therapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | Refractory High Risk Myelodysplastic SyndromeUnited States
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argenxNot yet recruiting
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argenxRecruitingCongenital Myasthenic SyndromeSpain, Italy, France, United Kingdom, United States, Canada
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Catalyst Pharmaceuticals, Inc.CompletedMyasthenic Syndromes, CongenitalUnited States
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The Champ FoundationChildren's Hospital of Philadelphia; The Cleveland ClinicRecruitingPearson Syndrome | Single Large Scale Mitochondrial DNA Deletion Syndromes (SLSMDS)United States
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Peking University Third HospitalCompletedParaneoplastic Neurological SyndromeChina
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Erasme University HospitalBrussel Medical Device Center (BMDC)RecruitingBlind Loop Syndrome Postoperative | Candy Cane SyndromeBelgium
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Mayo ClinicCompletedCongenital Myasthenic SyndromeUnited States
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Institut de Myologie, FranceAssistance Publique - Hôpitaux de ParisCompletedCongenital Myasthenic Syndrome
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Rockefeller UniversityCompleted
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Dafne BalemansGrünenthal GmbHCompleted
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Guang'anmen Hospital of China Academy of Chinese...Cancer Institute and Hospital, Chinese Academy of Medical Sciences; China Food...CompletedQi Stagnation and Blood Stasis SyndromeChina
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Jinling Hospital, ChinaCompletedShort Bowel Syndrome | Nonthyroidal Illness Syndrome
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Radboud University Medical CenterUnknown
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Universitaire Ziekenhuizen KU LeuvenCompletedPostoperative Dumping SyndromeBelgium
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Assistance Publique - Hôpitaux de ParisCompletedParaneoplastic Neurological SyndromesFrance
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National Pediatric Neuroinflammation Organization...CompletedOpsoclonus-myoclonus SyndromeUnited States
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Universitaire Ziekenhuizen KU LeuvenIpsenCompleted
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Novartis PharmaceuticalsCompletedDumping SyndromeBelgium, Netherlands, Germany, France, United States
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Technological Educational Institute of ThessalyRecruiting