- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on X-linked Lymphoproliferative Disease
Total 14257 results
-
Eunice Kennedy Shriver National Institute of Child...RecruitingAutism Spectrum Disorder | Fragile X Syndrome | Developmental Delay | Genetic Disorder | Asperger DisorderUnited States
-
Shanghai Children's Medical CenterUnknown
-
Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxAvailableMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States
-
Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...CompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Hemophagocytic Lymphohistiocytosis (HLH) | Non Hodgkins Lymphoma | Familial Hemophagocytic Lymphohistiocytosis (FLH) | Viral-associated Hemophagocytic Syndrome (VAHS) | X-linked Lymphoproliferative...United States
-
Rocket Pharmaceuticals Inc.Recruiting
-
University of California, San DiegoRocket Pharmaceuticals Inc.Recruiting
-
Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRecruitingMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States, United Kingdom, Netherlands
-
Universitair Ziekenhuis BrusselMarguerite - Marie Delacroix FoundationNot yet recruitingClassical Lissencephalies and Subcortical Band HeterotopiasBelgium
-
University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome, Preserved Speech Variant | Mecp2 Duplication Syndrome | Rett-related DisordersUnited States
-
InnoVec Biotherapeutics Inc.Peking Union Medical College HospitalNot yet recruitingEye Diseases | Retinal Degeneration | Retinal Disease | RetinoschisisChina
-
University Hospital ErlangenPervormance GmbHCompletedShort Term Effects and Risks of Physical Exercise in Subjects With Hypohidrotic Ectodermal DysplasiaX-Linked Hypohidrotic Ectodermal Dysplasia | Exercise-induced Rise of Body TemperatureGermany
-
BiogenCompletedChoroideremiaUnited States, Germany, France
-
Duke UniversityFoundation Fighting BlindnessWithdrawnChoroideremiaUnited States
-
University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... and other collaboratorsCompleted
-
University of AlbertaTerminated
-
TakedaRecruitingSpinal and Bulbar Muscular AtrophyJapan
-
Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
-
Rush University Medical CenterEmory UniversityEnrolling by invitationTuberous Sclerosis | Fragile X Syndrome | Rett Syndrome | Hamartoma Syndrome, Multiple | Angelman Syndrome | Creatine Deficiency, X-linked | Telomeric 22Q13 Monosomy Syndrome | Chromosome 15Q, Partial DeletionUnited States
-
University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Enrolling by invitationIntellectual Disability | Down Syndrome | Attention Deficit Hyperactivity Disorder | Fragile X SyndromeUnited States
-
4D Molecular TherapeuticsActive, not recruitingChoroideremiaUnited States
-
4D Molecular TherapeuticsTerminated
-
University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation TrustCompleted
-
STZ eyetrialUniversity Hospital TuebingenCompleted
-
Rocket Pharmaceuticals Inc.Completed
-
National Institute of Allergy and Infectious Diseases...TerminatedChronic Granulomatous DiseaseUnited States
-
Shenzhen Geno-Immune Medical InstituteUnknown
-
Federal Research Institute of Pediatric Hematology...UnknownChronic Granulomatous DiseaseRussian Federation
-
National Institute of Allergy and Infectious Diseases...Terminated
-
University Hospital, GrenobleTerminatedChronic Granulomatous DiseaseFrance
-
National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous DiseaseUnited States
-
University Hospital, BrestUnknownDysautonomia | Masculinity | MECP2-Related Severe Neonatal EncephalopathyFrance
-
University of Colorado, DenverCompletedChronic Granulomatous DiseaseUnited States
-
Radboud University Medical CenterCompletedChronic Granulomatous DiseaseNetherlands
-
Federal Research Institute of Pediatric Hematology...CompletedChronic Granulomatous DiseaseRussian Federation
-
University of ZurichGoethe UniversityCompletedChronic Granulomatous DiseaseSwitzerland
-
BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
-
AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
-
Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
-
Ramathibodi HospitalAstraZenecaCompletedSpinobulbar Muscular Atrophy | Kennedy's DiseaseThailand
-
Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly
-
Assistance Publique - Hôpitaux de ParisCompleted
-
National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous DiseaseUnited States
-
National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous DiseaseUnited States
-
Children's Hospital of Fudan UniversityTerminated
-
Helixmith Co., Ltd.UnknownChronic Granulomatous DiseaseKorea, Republic of
-
Baylor College of MedicineCompletedChronic Granulomatous DiseaseUnited States
-
Seoul National University HospitalUnknownChronic Granulomatous DiseaseKorea, Republic of
-
National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous DiseaseUnited States