- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on X-linked Thrombocytopenia
Total 3301 results
-
Jazz PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Spain, Italy, United Kingdom
-
Universitaire Ziekenhuizen KU LeuvenKU LeuvenCompletedCommunication | Parent-Child Relations | Behavior, ChildBelgium
-
Assistance Publique - Hôpitaux de ParisCompletedThrombotic Microangiopathies | Thrombotic Thrombocytopenic PurpuraFrance
-
Ovid Therapeutics Inc.Completed
-
Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
-
Children's Hospital Medical Center, CincinnatiNot yet recruitingAutism Spectrum Disorder | Fragile X Syndrome
-
bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
-
PfizerTerminatedHealthy | Polyradiculoneuropathy, Chronic Inflammatory Demyelinating | Primary Immune ThrombocytopeniaSpain, United States, Belgium, United Kingdom, New Zealand
-
Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - ItalyCompletedEpilepsy | Quality of Life | Dysbiosis | Rett SyndromeItaly
-
Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
-
University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCDKL5 | Rett Syndrome | MECP2 Duplication | FOXG1 DisordersUnited States
-
Mahidol UniversityRamathibodi HospitalCompletedChronic Idiopathic Thrombocytopenic Purpura | Helicobacter Pylori InfectionThailand
-
Grifols Therapeutics LLCCompletedPurpura, Thrombocytopenic, IdiopathicUnited States
-
Fundacion CRIS de Investigación para Vencer el...AmgenCompletedMyelodysplastic Syndromes | Immune ThrombocytopeniaSpain
-
Assistance Publique - Hôpitaux de ParisTakeda Pharmaceuticals International, Inc.WithdrawnImmune Thrombocytopenia | Warm Autoimmune Hemolytic AnemiaFrance
-
Henri Mondor University HospitalCompletedSystemic Lupus Erythematosus | Immune Thrombocytopenia
-
Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUnknownRett SyndromeUnited States
-
Sunshine Care FoundationMassachusetts General Hospital; Jose R. Reyes Memorial Medical CenterCompletedX-Linked Dystonia ParkinsonismPhilippines
-
University Hospital, BordeauxCompletedNational Prospective Cohort for Monitoring Children With Severe Autoimmune Cytopenia. (BIOCEREVANCE)Cytopenia | Autoimmune Haemolytic Anaemia | Thrombocytopenic Purpura, Immune
-
University of the Philippines Manila - Philippine...AvailableX-Linked Dystonia ParkinsonismPhilippines
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
-
Beijing Tiantan HospitalRecruiting
-
University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
-
Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
-
Peking University People's HospitalBeijing Friendship Hospital; Beijing Tongren Hospital; Beijing Hospital; Navy General...Not yet recruitingPurpura, Thrombocytopenic, IdiopathicChina
-
GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseFrance
-
University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedRett Syndrome | CDKL5 Disorder | MECP2 Duplication dIsorder | FOXG1 SyndromeUnited States
-
Rigshospitalet, DenmarkCompleted
-
University Hospital, BordeauxCompletedImmunotherapy | Immune Thrombocytopenic Purpura | Autoimmune Hemolytic Anemia | Evan Syndrome
-
Ultragenyx Pharmaceutical IncTerminatedCreatine Deficiency, X-linkedUnited States, Canada
-
Indiana UniversityCompletedFragile X Syndrome | Autism Spectrum DisordersUnited States
-
University of North Carolina, Chapel HillCompletedFragile X Syndrome | Psychosis | Autism Spectrum DisordersUnited States
-
University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome | MECP2 Duplication Disorder | Rett-related DisorderUnited States
-
Nova Mentis Life Science CorpKGK Science Inc.SuspendedCognitive Dysfunction | Fragile X Syndrome | BehaviorCanada
-
RespireRxFRAXA Research FoundationCompletedFragile X Syndrome | AutismUnited States
-
Ariel UniversityAssociazione Italiana Rett (AIRETT)Not yet recruitingRett SyndromeItaly
-
Hamilton Health Sciences CorporationHoffmann-La RocheCompletedPurpura, Thrombocytopenic, IdiopathicCanada
-
University of Alabama at BirminghamCompletedPurpura, Thrombocytopenic, IdiopathicUnited States
-
University Hospital, BordeauxMinistry for Health and Solidarity, FranceRecruitingImmune Thrombocytopenia | Autoimmune Hemolytic Anemia | Autoimmune NeutropeniaFrance
-
University Hospital, BordeauxCompletedRheumatoid Arthritis | Lupus Erythematosus | Autoimmune ThrombocytopeniaFrance
-
Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
-
Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
-
Shenzhen Geno-Immune Medical InstituteUnknown
-
NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
-
Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHypophosphatemic Rickets, X Linked DominantUnited States
-
GlaxoSmithKlineCompletedPurpura, Thrombocytopenic, IdiopathicUnited States
-
Shandong UniversityPeking Union Medical College Hospital; Cancer Institute and Hospital, Chinese... and other collaboratorsCompletedPurpura, Thrombocytopenic, IdiopathicChina
-
GlaxoSmithKlineCompletedHealthy Subjects | Purpura, Thrombocytopenic, IdiopathicUnited States
-
Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophySpain
-
Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States