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Clinical Trials on X-linked Hypophosphatemic Rickets/Osteomalacia
Total 1579 results
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationCompleted
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National Taiwan University HospitalUnknown
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Maastricht University Medical CenterCompleted
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineCompletedRett Syndrome
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineCompleted
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University Hospital, Basel, SwitzerlandNovartisCompletedRett's SyndromeSwitzerland
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Hubert Serve, Prof., MDUnknown
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University Hospital, ToursCompletedHealthy Volunteers | Autism | Fragile-X Syndrome (FXS)France
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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Ovid Therapeutics Inc.Completed
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama... and other collaboratorsRecruiting
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National Taiwan University HospitalCompletedNeurologic Disorder | Rett Syndrome
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Jazz PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Spain, Italy, United Kingdom
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Universitaire Ziekenhuizen KU LeuvenKU LeuvenCompletedCommunication | Parent-Child Relations | Behavior, ChildBelgium
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RecruitingRett Syndrome | Rett Syndrome, Atypical | RTTUnited States
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUnknownRett SyndromeUnited States
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Sunshine Care FoundationMassachusetts General Hospital; Jose R. Reyes Memorial Medical CenterCompletedX-Linked Dystonia ParkinsonismPhilippines
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Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
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University of the Philippines Manila - Philippine...AvailableX-Linked Dystonia ParkinsonismPhilippines
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Ultragenyx Pharmaceutical IncTerminatedCreatine Deficiency, X-linkedUnited States, Canada
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Children's Hospital Medical Center, CincinnatiNot yet recruitingAutism Spectrum Disorder | Fragile X Syndrome
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Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - ItalyCompletedEpilepsy | Quality of Life | Dysbiosis | Rett SyndromeItaly
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCDKL5 | Rett Syndrome | MECP2 Duplication | FOXG1 DisordersUnited States
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Indiana UniversityCompletedFragile X Syndrome | Autism Spectrum DisordersUnited States
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University of North Carolina, Chapel HillCompletedFragile X Syndrome | Psychosis | Autism Spectrum DisordersUnited States
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome | MECP2 Duplication Disorder | Rett-related DisorderUnited States
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Beijing Tiantan HospitalRecruiting
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University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
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Nova Mentis Life Science CorpKGK Science Inc.SuspendedCognitive Dysfunction | Fragile X Syndrome | BehaviorCanada
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RespireRxFRAXA Research FoundationCompletedFragile X Syndrome | AutismUnited States
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Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Ariel UniversityAssociazione Italiana Rett (AIRETT)Not yet recruitingRett SyndromeItaly
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseFrance
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedRett Syndrome | CDKL5 Disorder | MECP2 Duplication dIsorder | FOXG1 SyndromeUnited States
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Rigshospitalet, DenmarkCompleted
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseUnited Kingdom
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Zimmer BiometCompletedOsteoporosis | Osteomalacia | Rotator Cuff Tear Arthropathy | Joint; Destruction, SacroiliacKorea, Republic of
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophySpain
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States
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IRCCS Fondazione Stella MarisRecruitingCreatine Deficiency, X-linked | Creatine Deficiency Syndrome Due to Gamt DeficiencyItaly
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National Institute of Diabetes and Digestive and...CompletedHypocalcemia | Rickets | Osteomalacia | Pseudohypoparathyroidism | PseudopseudohpoparathyroidismUnited States