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Clinical Trials on X-linked Ichthyosis
Total 2425 results
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University Hospital, ToulouseAssociation for the development of research in DermatologyUnknown
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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University Hospital, MontpellierAssociation Xtraordinaire sub-group DDX3X; GenidaUnknownIntellectual Developmental Disorder | X-LINKEDFrance
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Beacon TherapeuticsRecruitingX-Linked Retinitis PigmentosaUnited States
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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Uskudar UniversityRecruitingLesch-Nyhan SyndromeTurkey
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ShireCompletedHunter SyndromeUnited States, Spain, Canada, United Kingdom, Mexico, Australia, France
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Green Cross CorporationCompleted
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Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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ShireCompleted
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Green Cross CorporationUnknownThe Long-term Safety Study of Idursulfase-beta in Hunter Syndrome(Mucopolysaccharidosis II) PatientsHunter SyndromeKorea, Republic of
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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Eunice Kennedy Shriver National Institute of Child...TerminatedFragile X Syndrome | Premature Ovarian Failure | Premature Menopause | FMR1 Premutation | Primary Ovairan InsufficiencyUnited States
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TakedaRecruiting
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TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
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TakedaCompletedMucopolysaccharidosis (MPS)Brazil
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Green Cross CorporationCompleted
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Duke UniversityRecruiting
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ShireCompletedHunter SyndromeUnited States, United Kingdom
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National Taiwan University HospitalUnknownRett Syndrome | Tourette Syndrome | Tic DisordersTaiwan
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University Hospital, MontpellierAgence de La BiomédecineActive, not recruitingFragile X Syndrome | Huntington Disease | Myotonic Dystrophy 1France
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Northwestern UniversityIcahn School of Medicine at Mount Sinai; Galderma R&DRecruiting
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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University of British ColumbiaVancouver General HospitalWithdrawn
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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Kyowa Kirin Pharmaceutical Development LtdRecruitingX-Linked HypophosphatemiaFrance, Netherlands, United Kingdom
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
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ShireCompleted
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis (MPS)United States, Argentina, Mexico, Spain, United Kingdom
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National Institute of Neurological Disorders and...CompletedMotor Neuron DiseaseUnited States
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Psyadon PharmaCompletedLesch-Nyhan DiseaseUnited States
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AB2 Bio Ltd.CompletedNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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AB2 Bio Ltd.Active, not recruitingNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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Medical University of GrazCompletedBipolar Affective DisorderAustria
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Canada
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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Center for Eye Research AustraliaCompleted
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St. James's Hospital, IrelandUniversity of Dublin, Trinity College; Science Foundation IrelandRecruitingAtopic Dermatitis | Psoriasis Vulgaris | Ichthyosis VulgarisIreland