- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on beta-Mannosidosis
Total 448 results
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityActive, not recruiting
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bluebird bioCompletedBeta-ThalassemiaUnited States, Germany, United Kingdom, France, Greece, Italy
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bluebird bioCompletedBeta-ThalassemiaFrance, United Kingdom, United States, Thailand, Italy, Germany
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IRCCS San RaffaeleTelethon Institute for Gene Therapy (OSR-TIGET)Active, not recruiting
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); Genzyme, a Sanofi Company; George Papanicolaou HospitalCompleted
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Boston UniversityCompletedBeta-ThalassemiaUnited States, United Kingdom
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Royal Brompton & Harefield NHS Foundation TrustCORDA, The Heart Charity; Apotex Inc.; The Cooley's Anemia Foundation,; The UK...UnknownBeta-ThalassemiaItaly
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Institute of Hematology & Blood Diseases HospitalR&D Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RecruitingTransfusion Dependent Beta-ThalassemiaChina
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EdiGene (GuangZhou) Inc.Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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Boston UniversityMahidol UniversityCompletedBeta Thalassemia IntermediaThailand
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Noordwest ZiekenhuisgroepKarolinska Institutet; Medical University of Graz; Fondazione Policlinico Universitario... and other collaboratorsRecruitingInvasive Group A Beta-Haemolytic Streptococcal DiseaseNetherlands
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Universidad Católica San Antonio de MurciaCompletedBeta Alanine SupplementationSpain
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Tampere University HospitalTurku University Hospital; University of TurkuActive, not recruitingInvasive Group A Beta-Haemolytic Streptococcal DiseaseFinland
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Università degli Studi di FerraraAzienda Ospedaliero, Universitaria Pisana; Rare Partners srl Impresa Sociale; Azienda Ospedaliero, Universitaria MeyerRecruitingBeta-ThalassemiaItaly
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National Institute of Blood and Marrow Transplant...Completed
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Vifor (International) Inc.Labcorp Drug Development IncWithdrawnBeta-ThalassemiaUnited States, Bulgaria, Israel
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Dr.Saqib Hussain AnsariUnknownThalassemia, BetaPakistan
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Xiaofang SunNanfang Hospital of Southern Medical University; Third Affiliated Hospital,... and other collaboratorsUnknownBeta-Thalassemia
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bluebird bioActive, not recruitingTransfusion-dependent Beta-ThalassemiaUnited States, France, United Kingdom, Australia, Thailand, Italy, Germany, Greece
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Sangamo TherapeuticsSanofiCompletedTransfusion Dependent Beta-thalassemiaUnited States
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Institute of Hematology & Blood Diseases Hospital...EdiGene Inc.; The Affiliated Hospital Of Guizhou Medical University; Zunyi Medical...Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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Novartis PharmaceuticalsCompletedBeta Thalassemia Transfusion DependentItaly
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Tehran University of Medical SciencesNovartisUnknownBone Marrow Transplantation | Beta-ThalassemiaIran, Islamic Republic of
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EmeraMedCompletedBeta Thalassemia MajorAlbania
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Nanfang Hospital of Southern Medical UniversityGuangdong Yike Gene Science and Technology CO.,LtdUnknownBeta Thalassemia MajorChina
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Ain Shams UniversityUnknownBeta Thalassemia MajorEgypt
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Boston UniversityHemaQuest Pharmaceuticals Inc.CompletedBeta Thalassemia IntermediaLebanon
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Assiut UniversityNot yet recruitingEKLF Mutations in Beta Thalassemia Patients
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National Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationSickle Cell Anemia | Sickle Beta Thalassemia | Sickle Cell Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Pain | Hbss | Hbsc | Sickle Cell Syndrome VariantUnited States
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Institute of Hematology & Blood Diseases Hospital...Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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Pharmacosmos A/SICON plcRecruitingBeta Thalassemia Major AnemiaDenmark
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Central Hospital, Nancy, FranceNot yet recruitingBeta Thalassemia Major Anemia
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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EdiGene (GuangZhou) Inc.PLA 923 HospitalActive, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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CelgeneAcceleron Pharma Inc. (a wholly owned subsidiary of Merck Sharp and Dohme...CompletedBeta-Thalassemia | Erythrocyte TransfusionUnited States, Israel, Australia, Turkey, Taiwan, Malaysia, United Kingdom, Canada, Thailand, France, Lebanon, Italy, Bulgaria, Greece, Tunisia
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Memorial Sloan Kettering Cancer CenterCompletedBeta Thalassemia Major | Congenital AnemiasUnited States
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Universidad Católica San Antonio de MurciaCompletedBeta Alanine SupplementationSpain
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Universidad Católica San Antonio de MurciaCompletedBeta Alanine SupplementationSpain
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University Hospital, GrenobleCompletedAdrenergic Beta-2 Agonist Effect | Albuterol EffectFrance
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Tanta UniversityUnknownNigella Sativa With Beta Thalassemia MajorEgypt
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Indonesia UniversityCompletedHemolysis | Oxidative Stress | Beta Thalassemia Major AnemiaIndonesia
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Vifor (International) Inc.Labcorp Corporation of America Holdings, IncCompletedBeta-Thalassemia | Non-transfusion-dependent ThalassemiaGreece, Israel, Italy, Lebanon, Thailand
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Ain Shams UniversityUnknownBeta-thalassemia | Serum Ferritin | Iron Chelation TherapyEgypt
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Ahram Canadian UniversityRecruiting
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Tanta UniversityRecruitingBeta Thalassemia With Increased Tricuspid Regurgitant Jet VelocityEgypt