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Clinical Trials on mTOR Pathway Abberation
Total 2059 results
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University Hospital, Basel, SwitzerlandEnrolling by invitationSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIISwitzerland
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National Institutes of Health Clinical Center (CC)CompletedDepression | HIV Infections | HIV-Associated Cognitive Motor ComplexUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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Association pour le Développement et l'Organisation...Association Française du Syndrome d'Ondine; Fonds de Recherche en Santé RespiratoireCompletedHealthy | Amyotrophic Lateral Sclerosis | Ondine SyndromeFrance
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Flex Pharma, Inc.TerminatedCharcot-Marie-Tooth DiseaseUnited States
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Ramathibodi HospitalAstraZenecaCompletedSpinobulbar Muscular Atrophy | Kennedy's DiseaseThailand
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Radboud University Medical CenterCompletedAnterior Cutaneous Nerve Entrapment Syndrome (ACNES)Netherlands
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Wayne State UniversityMuscular Dystrophy Association; Charcot-Marie-Tooth AssociationCompleted
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Holdsworth House Medical PracticeCompletedHIV-1-Associated Cognitive Motor Complex
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University of GenovaUnknownCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease Type 1AItaly
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National Institute of Neurological Disorders and...CompletedSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIIUnited States
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Atara BiotherapeuticsRecruitingHigh-grade B-cell Lymphoma | MCL | Diffuse Large B-cell Lymphoma (DLBCL) | Relapsed/Refractory B-cell Non-Hodgkin Lymphoma | DLBCL/High-grade B-cell Lymphoma With MYC and BCL2 Rearrangements | Anaplastic Lymphoma Kinase-Positive Large B-Cell Lymphoma | LBCL With IRF4 Rearrangement | High-grade B-cell... and other conditionsUnited States
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University of UtahRecruitingClinical Characteristics and Temporal Properties of Individual Tics in Persistent Tic Disorder (PTD)Tourette Syndrome | Tic Disorders | Tics | Tourette Syndrome in Children | Tourette Syndrome in Adolescence | Vocal Tic | Motor Tic | Tics/TremorUnited States
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Samsung Medical CenterNot yet recruitingCharcot-Marie-Tooth Disease, Type 1
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Synaptrix Labs Inc.Not yet recruitingParalysis | Amyotrophic Lateral Sclerosis | Spinal Cord Injuries | Neurologic Disorder | Cervical Spinal Cord Injury | Paralysis; Stroke | Tetraplegic; Paralysis | Quadriplegia/TetraplegiaUnited States
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Bahçeşehir UniversityNot yet recruitingDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Healthy Individuals
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University Hospital, Strasbourg, FranceRecruitingBardet-Biedl Syndrome | Alström SyndromeFrance
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University of IowaJohns Hopkins University; University of Colorado, Denver; King's College Hospital... and other collaboratorsRecruitingCharcot-Marie-Tooth Disease, Type Ia (Disorder) | HMSNUnited States, Italy, United Kingdom, Australia
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2 | Anti-myostatinUnited States, Germany, Belgium, Spain, United Kingdom, Netherlands, France, Italy, Poland
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Wave Life Sciences Ltd.TerminatedALS | FTDCanada, Belgium, New Zealand, Netherlands, Australia, Sweden, United Kingdom, Ireland
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Wake Forest University Health SciencesCompletedCovid19 | Amyotrophic Lateral SclerosisUnited States
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Nationwide Children's HospitalNovartisActive, not recruitingSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IUnited States
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Karolinska InstitutetUppsala University; Region StockholmCompletedTourette's Disorder | Persistent (Chronic) Motor or Vocal Tic DisorderSweden
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Assistance Publique - Hôpitaux de ParisCompletedInfantile Spinal Muscular Atrophy of Type 2 or 3France
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National Institute of Mental Health (NIMH)TerminatedHIV-Associated Cognitive Motor ComplexUnited States
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University of RochesterCompletedCharcot Marie Tooth DiseaseUnited States
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University of AlbertaCompletedCarpal Tunnel Syndrome | Compression NeuropathyCanada
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Ivan Segura DuranCompletedCarpal Tunnel Syndrome | Entrapment Neuropathy
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China Medical University HospitalUnknownParkinson's Disease | Amyotrophic Lateral Sclerosis | Alzheimer Disease
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National Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Recurrent Childhood Medulloblastoma | Recurrent Childhood Ependymoma | Recurrent Melanoma | Recurrent Neuroblastoma | Recurrent Osteosarcoma | Recurrent Childhood Rhabdomyosarcoma | Recurrent Colon Cancer | Recurrent Wilms Tumor and Other Childhood... and other conditionsUnited States
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophies | Inherited Neuromuscular Conditions | Inherited Neuropathies | Muscle Myopathies | Hereditary Spastic ParaplegiasUnited States
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National Institute of Neurological Disorders and...CompletedAmyotrophic Lateral Sclerosis | Frontotemporal Lobar DegenerationUnited States
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Pinar YasarCompletedStroke | Urinary Incontinence | Motor Skills DisordersTurkey
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Pharnext S.C.A.Premier Research Group plc; Eurofins Optimed; Synteract HCR (Syneos Health); Gr... and other collaboratorsActive, not recruitingCharcot-Marie-Tooth Disease, Type IAUnited States, Belgium, Canada, France, Netherlands, Spain, United Kingdom
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University of MinnesotaCompletedTourette Syndrome | Tic Disorders | Tics | Tourette Syndrome in Children | Tourette Syndrome in Adolescence | Tic Disorder, Childhood | Tic, MotorUnited States
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Wave Life Sciences Ltd.TerminatedALS | FTDNetherlands, United Kingdom
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Transposon Therapeutics, Inc.Active, not recruitingAmyotrophic Lateral Sclerosis | Frontotemporal DementiaSpain, United States, Belgium, France, Germany
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University of Missouri-ColumbiaNational Institute on Deafness and Other Communication Disorders (NIDCD)CompletedParkinson Disease | Amyotrophic Lateral SclerosisUnited States
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Yuzuncu Yıl UniversityCompleted
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Pharnext SACompletedPhase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) (PLEO-CMT)Charcot-Marie-Tooth Disease Type 1AUnited States, United Kingdom, Belgium, Canada, France, Netherlands, Spain, Germany
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Hill-RomCompletedMotor Neuron Disease | Cystic Fibrosis | Airway Clearance ImpairmentUnited States
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Tehran University of Medical SciencesUnknownInfantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]Iran, Islamic Republic of
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Guy Hains ChiropractorCompletedCompression Neuropathy, Carpal TunnelCanada
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Assistance Publique - Hôpitaux de ParisTerminatedAmyotrophic Lateral Sclerosis | Frontotemporal DementiaFrance
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Istanbul University - Cerrahpasa (IUC)Not yet recruitingCarpal Tunnel Syndrome | Entrapment Neuropathy | Median Nerve EntrapmentTurkey
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Johns Hopkins UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingAmyotrophic Lateral Sclerosis | Tetraplegia | Locked-in Syndrome | Brainstem StrokeUnited States
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Assistance Publique Hopitaux De MarseilleRecruitingCharcot-Marie-Tooth Disease Type 1AFrance