- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: AAV9 BBP-812
Total 3301 results
-
Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
-
Cryonove PharmaCEISO; Dermatech; INNOVSOLUTIONCompleted
-
NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
-
Adrenas Therapeutics IncRecruitingCongenital Adrenal HyperplasiaUnited States
-
Benjamin GreenbergActive, not recruiting
-
Kyuzi KamoiNot yet recruiting
-
uniQure France SASRecruitingMesial Temporal Lobe EpilepsyUnited States
-
Nagaoka Red Cross HospitalUnknownType 2 Diabetes Mellitus | Blood PressureJapan
-
Nagaoka Red Cross HospitalCompletedHypertension | Type 2 Diabetes
-
REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
-
Mackay Memorial HospitalOBI Pharma, IncUnknown
-
MeiraGTx, LLCRecruitingGrade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Parotid GlandsUnited States, Canada
-
ML Bio Solutions, Inc.Active, not recruiting
-
Opus Genetics, IncRecruiting
-
Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
-
Abeona Therapeutics, IncTerminatedMucopolysaccharidosis Type 3 BUnited States, Germany, France, Spain
-
Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
-
Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
-
CSL BehringCompletedHemophilia BGermany, Denmark, Netherlands
-
Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
-
eyeDNA TherapeuticsRecruitingRetinitis PigmentosaFrance
-
BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
-
Supernus Pharmaceuticals, Inc.CompletedAttention-Deficit/Hyperactivity Disorder (ADHD)United States
-
Cantero Therapeutics, a BridgeBio companyCelerionCompleted
-
University of FloridaUniversity of Miami; University of Massachusetts, WorcesterNo longer available
-
MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
-
Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
-
Genzyme, a Sanofi CompanyCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Gene Therapy | Age-Related Maculopathies | Age-Related Maculopathy | Retinal Neovascularization | Maculopathies, Age-Related | Maculopathy, Age-Related | Therapy, GeneUnited States
-
MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaActive, not recruitingAchromatopsiaUnited Kingdom, United States
-
Celladon CorporationCompletedHeart Failure | Cardiomyopathies | Ischemic Cardiomyopathy | Non-ischemic CardiomyopathyUnited States, United Kingdom, Belgium, Germany, Poland, Israel, Netherlands, Hungary, Denmark, Sweden
-
Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
-
ViGeneron GmbHRecruiting
-
Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
-
Sangamo TherapeuticsCeregeneCompletedParkinson's DiseaseUnited States
-
CoA Therapeutics, Inc., a BridgeBio companyTerminatedHealthy Volunteers | Propionic Acidemia | Methylmalonic Acidemia | Organic AcidemiaUnited States
-
CSL BehringActive, not recruiting
-
BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
-
Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
-
Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
-
Spark TherapeuticsCompleted
-
National Institute of Neurological Disorders and...Completed
-
Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
-
BiogenCompletedChoroideremiaUnited States, Germany, France
-
Supernus Pharmaceuticals, Inc.Completed
-
Supernus Pharmaceuticals, Inc.Completed
-
Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)SuspendedMethylmalonic Acidemia (MMA)United States
-
UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
-
Supernus Pharmaceuticals, Inc.Completed
-
Supernus Pharmaceuticals, Inc.Completed