- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Dose 6 of BMN 331
Total 7811 results
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BioMarin PharmaceuticalRecruitingHereditary Angioedema | HAEUnited States, Spain, Australia
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, United Kingdom
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyNetherlands, Belgium, Italy, Sweden
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Cellectar Biosciences, Inc.RecruitingMultiple Myeloma | Waldenstrom Macroglobulinemia | Mantle Cell Lymphoma | Marginal Zone Lymphoma | Chronic Lymphocytic Leukemia | Lymphoplasmacytic Lymphoma | Diffuse Large B Cell Lymphoma | Small Lymphocytic Lymphoma | Central Nervous System LymphomaUnited States, Australia, Czechia, Greece, Israel, Brazil, Finland, France, Spain, Turkey, United Kingdom
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis IVA (Morquio A Syndrome)Australia
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Medical College of WisconsinMiltenyi Biomedicine GmbHActive, not recruitingB-cell Chronic Lymphocytic Leukemia | B-cell Non Hodgkin LymphomaUnited States
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Stealth BioTherapeutics Inc.CompletedMitochondrial MyopathyUnited States
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVATaiwan, United States, Italy, United Kingdom
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Lumen Bioscience, Inc.Completed
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Mashhad University of Medical SciencesUnknownGraves' DiseaseIran, Islamic Republic of
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ViGenCell Inc.Not yet recruiting
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Pennington Biomedical Research CenterNational Center for Complementary and Integrative Health (NCCIH); Office of...CompletedDiabetes PreventionUnited States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited Kingdom, United States, Germany
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Novo Nordisk A/SCompletedType 2 Diabetes | Healthy VolunteersUnited States, Canada
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Ottawa Heart Institute Research CorporationHeart and Stroke Foundation of OntarioCompleted
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Pulmongene Ltd.CompletedIdiopathic Pulmonary FibrosisAustralia
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Bial - Portela C S.A.Completed
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Boehringer IngelheimCompleted
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Federal Budgetary Research Institution State Research...CompletedSmallpox | Monkeypox | Cowpox | Vaccinia Virus InfectionRussian Federation
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Brown UniversityCompleted
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J2H BiotechCompletedNon-alcoholic SteatohepatitisKorea, Republic of
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CohBar, Inc.CompletedNonalcoholic Fatty Liver DiseaseUnited States
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Weill Medical College of Cornell UniversityNational Cancer Institute (NCI); Merck Sharp & Dohme LLC; University of Sao Paulo and other collaboratorsActive, not recruitingHPV Infection | HIV-1-infection | HPV Positive Oropharyngeal Squamous Cell CarcinomaBrazil, Mexico, Puerto Rico
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, Japan, United Kingdom
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QurAlis CorporationRecruitingAmyotrophic Lateral SclerosisCanada, Germany, Netherlands, Ireland, United Kingdom, Belgium
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Bristol-Myers SquibbWithdrawn
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Boehringer IngelheimCompleted
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BiocadCompleted
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Bristol-Myers SquibbCompletedHealthy ParticipantsGermany
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University Hospital, GhentCompleted
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University of MinnesotaRecruitingSolid Organ TransplantUnited States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, United Kingdom, Canada, Germany
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Kilimanjaro Clinical Research InstituteLondon School of Hygiene and Tropical Medicine; Ifakara Health InstituteUnknownMalaria TransmissionTanzania
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MediciNovaCompletedChronic Obstructive Pulmonary DiseaseUnited States
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Beijing Health Guard Biotechnology, IncNational Institutes for Food and Drug Control, China; Yunnan Center for Disease... and other collaboratorsActive, not recruitingHuman Papillomavirus InfectionChina
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Janssen Research & Development, LLCCompleted
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PfizerCompleted
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Bristol-Myers SquibbCardioxyl Pharmaceuticals, IncCompleted
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The First Affiliated Hospital of Soochow UniversityFundamenta Therapeutics, Ltd.RecruitingB Cell Lymphoma | CAR | Relapsed Non-Hodgkin LymphomaChina
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Shanghai Bovax Biotechnology Co., Ltd.Chongqing Bovax Biopharmaceutical Co., Ltd.CompletedCervical Cancer | Vulvar Cancer | Vaginal Cancer | CIN1 | CIN2 | CIN3 | VaIN1 | VaIN2 | VaIN3 | Genital Wart | VIN 1 | VIN 2 | VIN 3 | AIS | HPV InfectionsChina
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J2H BiotechCompletedNon-alcoholic SteatohepatitisKorea, Republic of
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Acorda TherapeuticsCompletedIdiopathic Parkinson's DiseaseUnited States, Canada, Czechia, Poland, Spain
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Lidian ChenPeking University Third HospitalNot yet recruiting
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Bristol-Myers SquibbCompletedActive Psoriatic ArthritisSpain, United States, Hungary, Germany, Poland, United Kingdom, Russian Federation, Italy, Czechia
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Vanderbilt University Medical CenterAmerican Heart AssociationNot yet recruitingLong COVID | Autonomic Dysfunction | POTS - Postural Orthostatic Tachycardia Syndrome
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Baylor College of MedicineThe Methodist Hospital Research InstituteRecruitingEBV-Related Hodgkin Lymphoma | EBV Related Non-Hodgkin's Lymphoma | EBV-Related Lymphoproliferative DisorderUnited States